Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy

Michela Guglieri, Kate Bushby, Michael P. McDermott, Kimberly A. Hart, Rabi Tawil, William B. Martens, Barbara E. Herr, Elaine McColl, Chris Speed, Jennifer Wilkinson, Janbernd Kirschner, Wendy M. King, Michelle Eagle, Mary W. Brown, Tracey Willis, Robert C. Griggs, Unknown, Volker Straub, Henriette van Ruiten, Anne-Marie Childs, Emma Ciafaloni, Perry B. Shieh, Stefan Spinty, Lorenzo Maggi, Giovanni Baranello, Russell J. Butterfield, I. A. Horrocks, Helen Roper, Zoya Alhaswani, Kevin M. Flanigan, Nancy L. Kuntz, Adnan Manzur, Basil T. Darras, Peter B. Kang, Leslie Morrison, Monika Krzesniak-Swinarska, Jean K. Mah, Tiziana E. Mongini, Federica Ricci, Maja von der Hagen, Richard S. Finkel, Kathleen O’Reardon, Matthew Wicklund, Ashutosh Kumar, Craig M. McDonald, Jay J. Han, Nanette Joyce, Erik K. Henricson, Ulrike Schara-Schmidt, Andrea Gangfuss, Ekkehard Wilichowski, Richard J. Barohn, Jeffrey M. Statland, Craig Campbell, Giuseppe Vita, Gian Luca Vita, James F. Howard, Imelda Hughes, Hugh J. McMillan, Elena Pegoraro, Luca Bello, W. Bryan Burnette, Mathula Thangarajh, Taeun Chang

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DOI
10.1001/jama.2022.4315
Published
2022-04-19
Container
JAMA
Publisher
American Medical Association (AMA)
Open access
unknown

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BibTeX

@article{allodium:10.1001/jama.2022.4315,
  title = {Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy},
  author = {Michela Guglieri and Kate Bushby and Michael P. McDermott and Kimberly A. Hart and Rabi Tawil and William B. Martens and Barbara E. Herr and Elaine McColl and Chris Speed and Jennifer Wilkinson and Janbernd Kirschner and Wendy M. King and Michelle Eagle and Mary W. Brown and Tracey Willis and Robert C. Griggs and Unknown and Volker Straub and Henriette van Ruiten and Anne-Marie Childs and Emma Ciafaloni and Perry B. Shieh and Stefan Spinty and Lorenzo Maggi and Giovanni Baranello and Russell J. Butterfield and I. A. Horrocks and Helen Roper and Zoya Alhaswani and Kevin M. Flanigan and Nancy L. Kuntz and Adnan Manzur and Basil T. Darras and Peter B. Kang and Leslie Morrison and Monika Krzesniak-Swinarska and Jean K. Mah and Tiziana E. Mongini and Federica Ricci and Maja von der Hagen and Richard S. Finkel and Kathleen O’Reardon and Matthew Wicklund and Ashutosh Kumar and Craig M. McDonald and Jay J. Han and Nanette Joyce and Erik K. Henricson and Ulrike Schara-Schmidt and Andrea Gangfuss and Ekkehard Wilichowski and Richard J. Barohn and Jeffrey M. Statland and Craig Campbell and Giuseppe Vita and Gian Luca Vita and James F. Howard and Imelda Hughes and Hugh J. McMillan and Elena Pegoraro and Luca Bello and W. Bryan Burnette and Mathula Thangarajh and Taeun Chang},
  year = {2022},
  journal = {JAMA},
  doi = {10.1001/jama.2022.4315},
  url = {https://doi.org/10.1001/jama.2022.4315}
}

RIS

TY  - JOUR
TI  - Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy
AU  - Michela Guglieri
AU  - Kate Bushby
AU  - Michael P. McDermott
AU  - Kimberly A. Hart
AU  - Rabi Tawil
AU  - William B. Martens
AU  - Barbara E. Herr
AU  - Elaine McColl
AU  - Chris Speed
AU  - Jennifer Wilkinson
AU  - Janbernd Kirschner
AU  - Wendy M. King
AU  - Michelle Eagle
AU  - Mary W. Brown
AU  - Tracey Willis
AU  - Robert C. Griggs
AU  - Unknown
AU  - Volker Straub
AU  - Henriette van Ruiten
AU  - Anne-Marie Childs
AU  - Emma Ciafaloni
AU  - Perry B. Shieh
AU  - Stefan Spinty
AU  - Lorenzo Maggi
AU  - Giovanni Baranello
AU  - Russell J. Butterfield
AU  - I. A. Horrocks
AU  - Helen Roper
AU  - Zoya Alhaswani
AU  - Kevin M. Flanigan
AU  - Nancy L. Kuntz
AU  - Adnan Manzur
AU  - Basil T. Darras
AU  - Peter B. Kang
AU  - Leslie Morrison
AU  - Monika Krzesniak-Swinarska
AU  - Jean K. Mah
AU  - Tiziana E. Mongini
AU  - Federica Ricci
AU  - Maja von der Hagen
AU  - Richard S. Finkel
AU  - Kathleen O’Reardon
AU  - Matthew Wicklund
AU  - Ashutosh Kumar
AU  - Craig M. McDonald
AU  - Jay J. Han
AU  - Nanette Joyce
AU  - Erik K. Henricson
AU  - Ulrike Schara-Schmidt
AU  - Andrea Gangfuss
AU  - Ekkehard Wilichowski
AU  - Richard J. Barohn
AU  - Jeffrey M. Statland
AU  - Craig Campbell
AU  - Giuseppe Vita
AU  - Gian Luca Vita
AU  - James F. Howard
AU  - Imelda Hughes
AU  - Hugh J. McMillan
AU  - Elena Pegoraro
AU  - Luca Bello
AU  - W. Bryan Burnette
AU  - Mathula Thangarajh
AU  - Taeun Chang
PY  - 2022
JO  - JAMA
DO  - 10.1001/jama.2022.4315
UR  - https://doi.org/10.1001/jama.2022.4315
ER  - 

APA

Guglieri, M., Bushby, K., McDermott, M. P., Hart, K. A., Tawil, R., Martens, W. B., Herr, B. E., McColl, E., Speed, C., Wilkinson, J., Kirschner, J., King, W. M., Eagle, M., Brown, M. W., Willis, T., Griggs, R. C., Unknown, Straub, V., Ruiten, H. V., Childs, A., Ciafaloni, E., Shieh, P. B., Spinty, S., Maggi, L., Baranello, G., Butterfield, R. J., Horrocks, I. A., Roper, H., Alhaswani, Z., Flanigan, K. M., Kuntz, N. L., Manzur, A., Darras, B. T., Kang, P. B., Morrison, L., Krzesniak-Swinarska, M., Mah, J. K., Mongini, T. E., Ricci, F., Hagen, M. V. D., Finkel, R. S., O’Reardon, K., Wicklund, M., Kumar, A., McDonald, C. M., Han, J. J., Joyce, N., Henricson, E. K., Schara-Schmidt, U., Gangfuss, A., Wilichowski, E., Barohn, R. J., Statland, J. M., Campbell, C., Vita, G., Vita, G. L., Howard, J. F., Hughes, I., McMillan, H. J., Pegoraro, E., Bello, L., Burnette, W. B., Thangarajh, M., & Chang, T. (2022). Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy. JAMA. https://doi.org/10.1001/jama.2022.4315

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