DNL343 and Disease Progression in Amyotrophic Lateral Sclerosis

Sabrina Paganoni, Lori B. Chibnik, Melanie Quintana, Eric A. Macklin, Michelle A. Detry, Matteo Vestrucci, Giorgio Paulon, Anna McGlothlin, Jianing Wang, David Walk, Lauren Elman, Marianne Chase, Lindsay Heyd, Brittney Harkey, Alexander V. Sherman, Jeremy Shefner, James D. Berry, Erica Scirocco, Elisa Giacomelli, Hong Yu, Gale Kittle, Meaghan Hall, Doreen Ho, Omar Jawdat, Shafeeq Ladha, Eduardo Locatelli, Michael Rivner, Kevin Felice, Jonathan Katz, Senda Ajroud-Driss, Dominic Fee, Timothy Miller, Laura Rosow, Adam Quick, Daragh Heitzman, Laura A. Foster, Nicholas J. Maragakis, Stephen A. Goutman, Jeffrey Rosenfeld, Michael Benatar, Andrea Swenson, Robert Dedick Connors, Sheetal Shroff, Richard Bedlack, Courtney E. McIlduff, I-Hweii Amy Chen, Joseph Americo M. Fernandes, Alison Walsh, Amanda Peltier, Hristelina Ilieva, Frank Diaz, Hani Kushlaf, Said R. Beydoun, Bennett Myers, Ximena Arcila-Londono, Terry Heiman-Patterson, Michael Elliott, Jackie Whitesell, Tawfiq Al-Lahham, Matthew Elliott, Nicholas Olney, Michael Baer, Carlayne Jackson, Eufrosina Young, Jim Caress, Michael D. Weiss, Rebecca Kuenzler, Shakti Nayar, Edward J. Kasarskis, Zachary Simmons, Summer Gibson, Margaret Ayo Owegi, Namita A. Goyal, James P. Wymer, Kelly G. Gwathmey, Amber Erickson, Nurcan Gursoy, Gustavo Alameda, Cynthia Bodkin, Abel Wu, Jennifer Martinez-Thompson, Paul T. Twydell, Jinsy Andrews, Elham Bayat, Kourosh Rezania, Uzma Usman, Leo McCluskey, Sukanthi Kovvuru, Danna Jennings, Annette Garza-Meilandt, Romeo Maciuca, Isaac V. Cohen, Deepika Tamuly, Erden Eren, Merit E. Cudkowicz, Suma Babu, Unknown, Rachel A. Donahue, Hao-Wun Chen, Amy Kantor, Julia Caporaletti, Alexandra McCaffrey, Jennifer Scalia, Jeffrey A. Cohen, Jaimin Shah, Ghazala Hayat, Gary L. Pattee, Vinay Chaudhry, Lindsay Zilliox, Stephen Johnson, Constantine Farmakidis, Jourdan Milliard, Robert Bowser, Gabriela Lopes, Benjamin Barnes, Liberty Jenkins, Robert Sufit, April Szymanski, David Shrilla, Amber Malcolm, Catherine Lomen-Hoerth, Jill Goslinga, Min Kang, Madina Tugizova, Paul Sampognaro, Stephen Kolb, Sarah Heintzman, Alan Martin, Lora L. Clawson, Alpa Uchil, Kristen Riley, Jinae Arneklev, Eva L. Feldman, Savannah Quigley, Jasdeep Kaur, Nathan Carberry, Christopher Nance, Florian P Thomas, Xiaoyan Li, Seward Rutkove, Jerrica Farias, Tuan Vu, Kathleen Murray, Claudia Guerra Hernandez, Ezequiel Piccione, Pariwat Thaisetthawatkul, Alissa Romano, Diana L. Davis, Piera Pasinelli, Richard Lewis, Jacqueline Janecek, Leila Darki, Rodrigo Rodrigue, Luisa Rojas, Kara Steijlen, Iram Zaman, Anahita Deboo, David Ivanick, Brittany Guthrie, David Lacomis, Sarah Jones, Michael Hadler, Lauren Brown, Tracy Bazan, Colin Quinn, Sam Maiser, Ratna Bhavaraju-Sanka, Jenny A. Meyer, Michael S. Cartwright, Nassim Rad, Nimish Thakore, Zabeen Mahuwala, Vishakhadatta (Vish) Mathur Kumaraswamy, James Grogan, Xiaowei Su, Mansoureh Mamarabadi, Mark Bromberg, Robert H. Brown Jr., Kate Daniello, Jeffery Mullen, Whitney McNeely, Qihua Fan, Simona Treidler, Nathan P. Staff, Julia Yasek, Raymond Roos, Erika Renkl, Bjorn Oskarsson, Montserrat Diaz-Abad, Luisa Arroyave, Victoria Barlow, Genevive Changkuon, Melissa Cirino, Madison Coleman, Derek Dagostino, Christina Deignan, Emma Deirmendjian, Annette De Mattos, Sofia DiStefano, Kristin Drake, Michaela Estes, Precious Figueroa-Szostek, Abaigeal M. Ford, Tessa Garozzo, Meredith Hasenoehrl, Jennifer Henrique, Natalie Henrique, Samuel Hurwitz, Courtney Igne, Liam Irwin, Katie Jentoft, Boglarka Jordan, Igor Katsovskiy, Olga Kharakozova, Taylor Kolvek, Alexander Korin, Thuong La, Haining Li, Lida Mazina, Joe Ostrow, Jaclyn Pagliaro, Jack Palillo, Payal Patel, Janae Patterson, Minh Phan, Najla Popel, Jesse Rosenthal, Anil Sanjana, Catherine Small, Taylor Stimpson, Lia M. Tamburello, Natalia Tarasenko, Mirna Thomas, Eric Tustison, Emem Udo, Prasha Vigneswaran, Yusra Wahab, Anat Weiss Sadan, Isaac Whitworth, Kathy Wong, Spencer Wright, Mariah Connolly, Adrian Felix, Karly Garrett, Ashley Stepler, Abigail De La Rosa Garcia, Kamran Khan, Ivy McGlaughlin, Grace Ghali, Oyinkansola Lawal, Linda Nelson, Marissa Pabon, Diana Rede, Heather Sporn, Victor Bill, Kirsten Clark, Cornelia Kamp, Julie Kennedy, Eileen Fannon, Christopher Mark, Arian Horbovetz, Andrew McGarry, Margherita Torti

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DOI
10.1001/jamanetworkopen.2026.34809
Published
2026-09-22
Container
JAMA Network Open
Publisher
American Medical Association (AMA)
Open access
unknown

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BibTeX

@article{allodium:10.1001/jamanetworkopen.2026.34809,
  title = {DNL343 and Disease Progression in Amyotrophic Lateral Sclerosis},
  author = {Sabrina Paganoni and Lori B. Chibnik and Melanie Quintana and Eric A. Macklin and Michelle A. Detry and Matteo Vestrucci and Giorgio Paulon and Anna McGlothlin and Jianing Wang and David Walk and Lauren Elman and Marianne Chase and Lindsay Heyd and Brittney Harkey and Alexander V. Sherman and Jeremy Shefner and James D. Berry and Erica Scirocco and Elisa Giacomelli and Hong Yu and Gale Kittle and Meaghan Hall and Doreen Ho and Omar Jawdat and Shafeeq Ladha and Eduardo Locatelli and Michael Rivner and Kevin Felice and Jonathan Katz and Senda Ajroud-Driss and Dominic Fee and Timothy Miller and Laura Rosow and Adam Quick and Daragh Heitzman and Laura A. Foster and Nicholas J. Maragakis and Stephen A. Goutman and Jeffrey Rosenfeld and Michael Benatar and Andrea Swenson and Robert Dedick Connors and Sheetal Shroff and Richard Bedlack and Courtney E. McIlduff and I-Hweii Amy Chen and Joseph Americo M. Fernandes and Alison Walsh and Amanda Peltier and Hristelina Ilieva and Frank Diaz and Hani Kushlaf and Said R. Beydoun and Bennett Myers and Ximena Arcila-Londono and Terry Heiman-Patterson and Michael Elliott and Jackie Whitesell and Tawfiq Al-Lahham and Matthew Elliott and Nicholas Olney and Michael Baer and Carlayne Jackson and Eufrosina Young and Jim Caress and Michael D. Weiss and Rebecca Kuenzler and Shakti Nayar and Edward J. Kasarskis and Zachary Simmons and Summer Gibson and Margaret Ayo Owegi and Namita A. Goyal and James P. Wymer and Kelly G. Gwathmey and Amber Erickson and Nurcan Gursoy and Gustavo Alameda and Cynthia Bodkin and Abel Wu and Jennifer Martinez-Thompson and Paul T. Twydell and Jinsy Andrews and Elham Bayat and Kourosh Rezania and Uzma Usman and Leo McCluskey and Sukanthi Kovvuru and Danna Jennings and Annette Garza-Meilandt and Romeo Maciuca and Isaac V. Cohen and Deepika Tamuly and Erden Eren and Merit E. Cudkowicz and Suma Babu and Unknown and Rachel A. Donahue and Hao-Wun Chen and Amy Kantor and Julia Caporaletti and Alexandra McCaffrey and Jennifer Scalia and Jeffrey A. Cohen and Jaimin Shah and Ghazala Hayat and Gary L. Pattee and Vinay Chaudhry and Lindsay Zilliox and Stephen Johnson and Constantine Farmakidis and Jourdan Milliard and Robert Bowser and Gabriela Lopes and Benjamin Barnes and Liberty Jenkins and Robert Sufit and April Szymanski and David Shrilla and Amber Malcolm and Catherine Lomen-Hoerth and Jill Goslinga and Min Kang and Madina Tugizova and Paul Sampognaro and Stephen Kolb and Sarah Heintzman and Alan Martin and Lora L. Clawson and Alpa Uchil and Kristen Riley and Jinae Arneklev and Eva L. Feldman and Savannah Quigley and Jasdeep Kaur and Nathan Carberry and Christopher Nance and Florian P Thomas and Xiaoyan Li and Seward Rutkove and Jerrica Farias and Tuan Vu and Kathleen Murray and Claudia Guerra Hernandez and Ezequiel Piccione and Pariwat Thaisetthawatkul and Alissa Romano and Diana L. Davis and Piera Pasinelli and Richard Lewis and Jacqueline Janecek and Leila Darki and Rodrigo Rodrigue and Luisa Rojas and Kara Steijlen and Iram Zaman and Anahita Deboo and David Ivanick and Brittany Guthrie and David Lacomis and Sarah Jones and Michael Hadler and Lauren Brown and Tracy Bazan and Colin Quinn and Sam Maiser and Ratna Bhavaraju-Sanka and Jenny A. Meyer and Michael S. Cartwright and Nassim Rad and Nimish Thakore and Zabeen Mahuwala and Vishakhadatta (Vish) Mathur Kumaraswamy and James Grogan and Xiaowei Su and Mansoureh Mamarabadi and Mark Bromberg and Robert H. Brown Jr. and Kate Daniello and Jeffery Mullen and Whitney McNeely and Qihua Fan and Simona Treidler and Nathan P. Staff and Julia Yasek and Raymond Roos and Erika Renkl and Bjorn Oskarsson and Montserrat Diaz-Abad and Luisa Arroyave and Victoria Barlow and Genevive Changkuon and Melissa Cirino and Madison Coleman and Derek Dagostino and Christina Deignan and Emma Deirmendjian and Annette De Mattos and Sofia DiStefano and Kristin Drake and Michaela Estes and Precious Figueroa-Szostek and Abaigeal M. Ford and Tessa Garozzo and Meredith Hasenoehrl and Jennifer Henrique and Natalie Henrique and Samuel Hurwitz and Courtney Igne and Liam Irwin and Katie Jentoft and Boglarka Jordan and Igor Katsovskiy and Olga Kharakozova and Taylor Kolvek and Alexander Korin and Thuong La and Haining Li and Lida Mazina and Joe Ostrow and Jaclyn Pagliaro and Jack Palillo and Payal Patel and Janae Patterson and Minh Phan and Najla Popel and Jesse Rosenthal and Anil Sanjana and Catherine Small and Taylor Stimpson and Lia M. Tamburello and Natalia Tarasenko and Mirna Thomas and Eric Tustison and Emem Udo and Prasha Vigneswaran and Yusra Wahab and Anat Weiss Sadan and Isaac Whitworth and Kathy Wong and Spencer Wright and Mariah Connolly and Adrian Felix and Karly Garrett and Ashley Stepler and Abigail De La Rosa Garcia and Kamran Khan and Ivy McGlaughlin and Grace Ghali and Oyinkansola Lawal and Linda Nelson and Marissa Pabon and Diana Rede and Heather Sporn and Victor Bill and Kirsten Clark and Cornelia Kamp and Julie Kennedy and Eileen Fannon and Christopher Mark and Arian Horbovetz and Andrew McGarry and Margherita Torti},
  year = {2026},
  journal = {JAMA Network Open},
  doi = {10.1001/jamanetworkopen.2026.34809},
  url = {https://doi.org/10.1001/jamanetworkopen.2026.34809}
}

RIS

TY  - JOUR
TI  - DNL343 and Disease Progression in Amyotrophic Lateral Sclerosis
AU  - Sabrina Paganoni
AU  - Lori B. Chibnik
AU  - Melanie Quintana
AU  - Eric A. Macklin
AU  - Michelle A. Detry
AU  - Matteo Vestrucci
AU  - Giorgio Paulon
AU  - Anna McGlothlin
AU  - Jianing Wang
AU  - David Walk
AU  - Lauren Elman
AU  - Marianne Chase
AU  - Lindsay Heyd
AU  - Brittney Harkey
AU  - Alexander V. Sherman
AU  - Jeremy Shefner
AU  - James D. Berry
AU  - Erica Scirocco
AU  - Elisa Giacomelli
AU  - Hong Yu
AU  - Gale Kittle
AU  - Meaghan Hall
AU  - Doreen Ho
AU  - Omar Jawdat
AU  - Shafeeq Ladha
AU  - Eduardo Locatelli
AU  - Michael Rivner
AU  - Kevin Felice
AU  - Jonathan Katz
AU  - Senda Ajroud-Driss
AU  - Dominic Fee
AU  - Timothy Miller
AU  - Laura Rosow
AU  - Adam Quick
AU  - Daragh Heitzman
AU  - Laura A. Foster
AU  - Nicholas J. Maragakis
AU  - Stephen A. Goutman
AU  - Jeffrey Rosenfeld
AU  - Michael Benatar
AU  - Andrea Swenson
AU  - Robert Dedick Connors
AU  - Sheetal Shroff
AU  - Richard Bedlack
AU  - Courtney E. McIlduff
AU  - I-Hweii Amy Chen
AU  - Joseph Americo M. Fernandes
AU  - Alison Walsh
AU  - Amanda Peltier
AU  - Hristelina Ilieva
AU  - Frank Diaz
AU  - Hani Kushlaf
AU  - Said R. Beydoun
AU  - Bennett Myers
AU  - Ximena Arcila-Londono
AU  - Terry Heiman-Patterson
AU  - Michael Elliott
AU  - Jackie Whitesell
AU  - Tawfiq Al-Lahham
AU  - Matthew Elliott
AU  - Nicholas Olney
AU  - Michael Baer
AU  - Carlayne Jackson
AU  - Eufrosina Young
AU  - Jim Caress
AU  - Michael D. Weiss
AU  - Rebecca Kuenzler
AU  - Shakti Nayar
AU  - Edward J. Kasarskis
AU  - Zachary Simmons
AU  - Summer Gibson
AU  - Margaret Ayo Owegi
AU  - Namita A. Goyal
AU  - James P. Wymer
AU  - Kelly G. Gwathmey
AU  - Amber Erickson
AU  - Nurcan Gursoy
AU  - Gustavo Alameda
AU  - Cynthia Bodkin
AU  - Abel Wu
AU  - Jennifer Martinez-Thompson
AU  - Paul T. Twydell
AU  - Jinsy Andrews
AU  - Elham Bayat
AU  - Kourosh Rezania
AU  - Uzma Usman
AU  - Leo McCluskey
AU  - Sukanthi Kovvuru
AU  - Danna Jennings
AU  - Annette Garza-Meilandt
AU  - Romeo Maciuca
AU  - Isaac V. Cohen
AU  - Deepika Tamuly
AU  - Erden Eren
AU  - Merit E. Cudkowicz
AU  - Suma Babu
AU  - Unknown
AU  - Rachel A. Donahue
AU  - Hao-Wun Chen
AU  - Amy Kantor
AU  - Julia Caporaletti
AU  - Alexandra McCaffrey
AU  - Jennifer Scalia
AU  - Jeffrey A. Cohen
AU  - Jaimin Shah
AU  - Ghazala Hayat
AU  - Gary L. Pattee
AU  - Vinay Chaudhry
AU  - Lindsay Zilliox
AU  - Stephen Johnson
AU  - Constantine Farmakidis
AU  - Jourdan Milliard
AU  - Robert Bowser
AU  - Gabriela Lopes
AU  - Benjamin Barnes
AU  - Liberty Jenkins
AU  - Robert Sufit
AU  - April Szymanski
AU  - David Shrilla
AU  - Amber Malcolm
AU  - Catherine Lomen-Hoerth
AU  - Jill Goslinga
AU  - Min Kang
AU  - Madina Tugizova
AU  - Paul Sampognaro
AU  - Stephen Kolb
AU  - Sarah Heintzman
AU  - Alan Martin
AU  - Lora L. Clawson
AU  - Alpa Uchil
AU  - Kristen Riley
AU  - Jinae Arneklev
AU  - Eva L. Feldman
AU  - Savannah Quigley
AU  - Jasdeep Kaur
AU  - Nathan Carberry
AU  - Christopher Nance
AU  - Florian P Thomas
AU  - Xiaoyan Li
AU  - Seward Rutkove
AU  - Jerrica Farias
AU  - Tuan Vu
AU  - Kathleen Murray
AU  - Claudia Guerra Hernandez
AU  - Ezequiel Piccione
AU  - Pariwat Thaisetthawatkul
AU  - Alissa Romano
AU  - Diana L. Davis
AU  - Piera Pasinelli
AU  - Richard Lewis
AU  - Jacqueline Janecek
AU  - Leila Darki
AU  - Rodrigo Rodrigue
AU  - Luisa Rojas
AU  - Kara Steijlen
AU  - Iram Zaman
AU  - Anahita Deboo
AU  - David Ivanick
AU  - Brittany Guthrie
AU  - David Lacomis
AU  - Sarah Jones
AU  - Michael Hadler
AU  - Lauren Brown
AU  - Tracy Bazan
AU  - Colin Quinn
AU  - Sam Maiser
AU  - Ratna Bhavaraju-Sanka
AU  - Jenny A. Meyer
AU  - Michael S. Cartwright
AU  - Nassim Rad
AU  - Nimish Thakore
AU  - Zabeen Mahuwala
AU  - Vishakhadatta (Vish) Mathur Kumaraswamy
AU  - James Grogan
AU  - Xiaowei Su
AU  - Mansoureh Mamarabadi
AU  - Mark Bromberg
AU  - Robert H. Brown Jr.
AU  - Kate Daniello
AU  - Jeffery Mullen
AU  - Whitney McNeely
AU  - Qihua Fan
AU  - Simona Treidler
AU  - Nathan P. Staff
AU  - Julia Yasek
AU  - Raymond Roos
AU  - Erika Renkl
AU  - Bjorn Oskarsson
AU  - Montserrat Diaz-Abad
AU  - Luisa Arroyave
AU  - Victoria Barlow
AU  - Genevive Changkuon
AU  - Melissa Cirino
AU  - Madison Coleman
AU  - Derek Dagostino
AU  - Christina Deignan
AU  - Emma Deirmendjian
AU  - Annette De Mattos
AU  - Sofia DiStefano
AU  - Kristin Drake
AU  - Michaela Estes
AU  - Precious Figueroa-Szostek
AU  - Abaigeal M. Ford
AU  - Tessa Garozzo
AU  - Meredith Hasenoehrl
AU  - Jennifer Henrique
AU  - Natalie Henrique
AU  - Samuel Hurwitz
AU  - Courtney Igne
AU  - Liam Irwin
AU  - Katie Jentoft
AU  - Boglarka Jordan
AU  - Igor Katsovskiy
AU  - Olga Kharakozova
AU  - Taylor Kolvek
AU  - Alexander Korin
AU  - Thuong La
AU  - Haining Li
AU  - Lida Mazina
AU  - Joe Ostrow
AU  - Jaclyn Pagliaro
AU  - Jack Palillo
AU  - Payal Patel
AU  - Janae Patterson
AU  - Minh Phan
AU  - Najla Popel
AU  - Jesse Rosenthal
AU  - Anil Sanjana
AU  - Catherine Small
AU  - Taylor Stimpson
AU  - Lia M. Tamburello
AU  - Natalia Tarasenko
AU  - Mirna Thomas
AU  - Eric Tustison
AU  - Emem Udo
AU  - Prasha Vigneswaran
AU  - Yusra Wahab
AU  - Anat Weiss Sadan
AU  - Isaac Whitworth
AU  - Kathy Wong
AU  - Spencer Wright
AU  - Mariah Connolly
AU  - Adrian Felix
AU  - Karly Garrett
AU  - Ashley Stepler
AU  - Abigail De La Rosa Garcia
AU  - Kamran Khan
AU  - Ivy McGlaughlin
AU  - Grace Ghali
AU  - Oyinkansola Lawal
AU  - Linda Nelson
AU  - Marissa Pabon
AU  - Diana Rede
AU  - Heather Sporn
AU  - Victor Bill
AU  - Kirsten Clark
AU  - Cornelia Kamp
AU  - Julie Kennedy
AU  - Eileen Fannon
AU  - Christopher Mark
AU  - Arian Horbovetz
AU  - Andrew McGarry
AU  - Margherita Torti
PY  - 2026
JO  - JAMA Network Open
DO  - 10.1001/jamanetworkopen.2026.34809
UR  - https://doi.org/10.1001/jamanetworkopen.2026.34809
ER  - 

APA

Paganoni, S., Chibnik, L. B., Quintana, M., Macklin, E. A., Detry, M. A., Vestrucci, M., Paulon, G., McGlothlin, A., Wang, J., Walk, D., Elman, L., Chase, M., Heyd, L., Harkey, B., Sherman, A. V., Shefner, J., Berry, J. D., Scirocco, E., Giacomelli, E., Yu, H., Kittle, G., Hall, M., Ho, D., Jawdat, O., Ladha, S., Locatelli, E., Rivner, M., Felice, K., Katz, J., Ajroud-Driss, S., Fee, D., Miller, T., Rosow, L., Quick, A., Heitzman, D., Foster, L. A., Maragakis, N. J., Goutman, S. A., Rosenfeld, J., Benatar, M., Swenson, A., Connors, R. D., Shroff, S., Bedlack, R., McIlduff, C. E., Chen, I. A., Fernandes, J. A. M., Walsh, A., Peltier, A., Ilieva, H., Diaz, F., Kushlaf, H., Beydoun, S. R., Myers, B., Arcila-Londono, X., Heiman-Patterson, T., Elliott, M., Whitesell, J., Al-Lahham, T., Elliott, M., Olney, N., Baer, M., Jackson, C., Young, E., Caress, J., Weiss, M. D., Kuenzler, R., Nayar, S., Kasarskis, E. J., Simmons, Z., Gibson, S., Owegi, M. A., Goyal, N. A., Wymer, J. P., Gwathmey, K. G., Erickson, A., Gursoy, N., Alameda, G., Bodkin, C., Wu, A., Martinez-Thompson, J., Twydell, P. T., Andrews, J., Bayat, E., Rezania, K., Usman, U., McCluskey, L., Kovvuru, S., Jennings, D., Garza-Meilandt, A., Maciuca, R., Cohen, I. V., Tamuly, D., Eren, E., Cudkowicz, M. E., Babu, S., Unknown, Donahue, R. A., Chen, H., Kantor, A., Caporaletti, J., McCaffrey, A., Scalia, J., Cohen, J. A., Shah, J., Hayat, G., Pattee, G. L., Chaudhry, V., Zilliox, L., Johnson, S., Farmakidis, C., Milliard, J., Bowser, R., Lopes, G., Barnes, B., Jenkins, L., Sufit, R., Szymanski, A., Shrilla, D., Malcolm, A., Lomen-Hoerth, C., Goslinga, J., Kang, M., Tugizova, M., Sampognaro, P., Kolb, S., Heintzman, S., Martin, A., Clawson, L. L., Uchil, A., Riley, K., Arneklev, J., Feldman, E. L., Quigley, S., Kaur, J., Carberry, N., Nance, C., Thomas, F. P., Li, X., Rutkove, S., Farias, J., Vu, T., Murray, K., Hernandez, C. G., Piccione, E., Thaisetthawatkul, P., Romano, A., Davis, D. L., Pasinelli, P., Lewis, R., Janecek, J., Darki, L., Rodrigue, R., Rojas, L., Steijlen, K., Zaman, I., Deboo, A., Ivanick, D., Guthrie, B., Lacomis, D., Jones, S., Hadler, M., Brown, L., Bazan, T., Quinn, C., Maiser, S., Bhavaraju-Sanka, R., Meyer, J. A., Cartwright, M. S., Rad, N., Thakore, N., Mahuwala, Z., Kumaraswamy, V. (. M., Grogan, J., Su, X., Mamarabadi, M., Bromberg, M., Jr., R. H. B., Daniello, K., Mullen, J., McNeely, W., Fan, Q., Treidler, S., Staff, N. P., Yasek, J., Roos, R., Renkl, E., Oskarsson, B., Diaz-Abad, M., Arroyave, L., Barlow, V., Changkuon, G., Cirino, M., Coleman, M., Dagostino, D., Deignan, C., Deirmendjian, E., Mattos, A. D., DiStefano, S., Drake, K., Estes, M., Figueroa-Szostek, P., Ford, A. M., Garozzo, T., Hasenoehrl, M., Henrique, J., Henrique, N., Hurwitz, S., Igne, C., Irwin, L., Jentoft, K., Jordan, B., Katsovskiy, I., Kharakozova, O., Kolvek, T., Korin, A., La, T., Li, H., Mazina, L., Ostrow, J., Pagliaro, J., Palillo, J., Patel, P., Patterson, J., Phan, M., Popel, N., Rosenthal, J., Sanjana, A., Small, C., Stimpson, T., Tamburello, L. M., Tarasenko, N., Thomas, M., Tustison, E., Udo, E., Vigneswaran, P., Wahab, Y., Sadan, A. W., Whitworth, I., Wong, K., Wright, S., Connolly, M., Felix, A., Garrett, K., Stepler, A., Garcia, A. D. L. R., Khan, K., McGlaughlin, I., Ghali, G., Lawal, O., Nelson, L., Pabon, M., Rede, D., Sporn, H., Bill, V., Clark, K., Kamp, C., Kennedy, J., Fannon, E., Mark, C., Horbovetz, A., McGarry, A., & Torti, M. (2026). DNL343 and Disease Progression in Amyotrophic Lateral Sclerosis. JAMA Network Open. https://doi.org/10.1001/jamanetworkopen.2026.34809

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