DNL343 and Disease Progression in Amyotrophic Lateral Sclerosis
- DOI
- 10.1001/jamanetworkopen.2026.34809
- Published
- 2026-09-22
- Container
- JAMA Network Open
- Publisher
- American Medical Association (AMA)
- Open access
- unknown
Credibility signals
uncertain Score 64/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.
Show all credibility signals
- supportingDOI registered: A matching record was returned by Crossref.
- supportingDOI resolves: A matching record was returned by Crossref.
- not scoredDirectory of Open Access Journals: No matching DOAJ record was present in this response. No allow-list match; this is not evidence of low credibility.
- not scoredMEDLINE indexed: Not checked or no result supplied; no credibility inference made.
- not scoredOpenAlex core source: Not checked or no result supplied; no credibility inference made.
- not scoredKnown publisher allow-list: Not checked or no result supplied; no credibility inference made.
- not scoredROR affiliation: Not checked or no result supplied; no credibility inference made.
- not scoredRetraction Watch retraction: No retraction notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch expression of concern: No expression of concern notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch correction: No correction notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch reinstatement: No reinstatement notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredOpen access status: Not checked or no result supplied; no credibility inference made.
- not scoredPublication license: Not checked or no result supplied; no credibility inference made.
- not scoredPublication version: A publication version was supplied but is not scored.
- supportingMetadata completeness: All 6 scored descriptive metadata groups are present.
Cite this work
BibTeX
@article{allodium:10.1001/jamanetworkopen.2026.34809,
title = {DNL343 and Disease Progression in Amyotrophic Lateral Sclerosis},
author = {Sabrina Paganoni and Lori B. Chibnik and Melanie Quintana and Eric A. Macklin and Michelle A. Detry and Matteo Vestrucci and Giorgio Paulon and Anna McGlothlin and Jianing Wang and David Walk and Lauren Elman and Marianne Chase and Lindsay Heyd and Brittney Harkey and Alexander V. Sherman and Jeremy Shefner and James D. Berry and Erica Scirocco and Elisa Giacomelli and Hong Yu and Gale Kittle and Meaghan Hall and Doreen Ho and Omar Jawdat and Shafeeq Ladha and Eduardo Locatelli and Michael Rivner and Kevin Felice and Jonathan Katz and Senda Ajroud-Driss and Dominic Fee and Timothy Miller and Laura Rosow and Adam Quick and Daragh Heitzman and Laura A. Foster and Nicholas J. Maragakis and Stephen A. Goutman and Jeffrey Rosenfeld and Michael Benatar and Andrea Swenson and Robert Dedick Connors and Sheetal Shroff and Richard Bedlack and Courtney E. McIlduff and I-Hweii Amy Chen and Joseph Americo M. Fernandes and Alison Walsh and Amanda Peltier and Hristelina Ilieva and Frank Diaz and Hani Kushlaf and Said R. Beydoun and Bennett Myers and Ximena Arcila-Londono and Terry Heiman-Patterson and Michael Elliott and Jackie Whitesell and Tawfiq Al-Lahham and Matthew Elliott and Nicholas Olney and Michael Baer and Carlayne Jackson and Eufrosina Young and Jim Caress and Michael D. Weiss and Rebecca Kuenzler and Shakti Nayar and Edward J. Kasarskis and Zachary Simmons and Summer Gibson and Margaret Ayo Owegi and Namita A. Goyal and James P. Wymer and Kelly G. Gwathmey and Amber Erickson and Nurcan Gursoy and Gustavo Alameda and Cynthia Bodkin and Abel Wu and Jennifer Martinez-Thompson and Paul T. Twydell and Jinsy Andrews and Elham Bayat and Kourosh Rezania and Uzma Usman and Leo McCluskey and Sukanthi Kovvuru and Danna Jennings and Annette Garza-Meilandt and Romeo Maciuca and Isaac V. Cohen and Deepika Tamuly and Erden Eren and Merit E. Cudkowicz and Suma Babu and Unknown and Rachel A. Donahue and Hao-Wun Chen and Amy Kantor and Julia Caporaletti and Alexandra McCaffrey and Jennifer Scalia and Jeffrey A. Cohen and Jaimin Shah and Ghazala Hayat and Gary L. Pattee and Vinay Chaudhry and Lindsay Zilliox and Stephen Johnson and Constantine Farmakidis and Jourdan Milliard and Robert Bowser and Gabriela Lopes and Benjamin Barnes and Liberty Jenkins and Robert Sufit and April Szymanski and David Shrilla and Amber Malcolm and Catherine Lomen-Hoerth and Jill Goslinga and Min Kang and Madina Tugizova and Paul Sampognaro and Stephen Kolb and Sarah Heintzman and Alan Martin and Lora L. Clawson and Alpa Uchil and Kristen Riley and Jinae Arneklev and Eva L. Feldman and Savannah Quigley and Jasdeep Kaur and Nathan Carberry and Christopher Nance and Florian P Thomas and Xiaoyan Li and Seward Rutkove and Jerrica Farias and Tuan Vu and Kathleen Murray and Claudia Guerra Hernandez and Ezequiel Piccione and Pariwat Thaisetthawatkul and Alissa Romano and Diana L. Davis and Piera Pasinelli and Richard Lewis and Jacqueline Janecek and Leila Darki and Rodrigo Rodrigue and Luisa Rojas and Kara Steijlen and Iram Zaman and Anahita Deboo and David Ivanick and Brittany Guthrie and David Lacomis and Sarah Jones and Michael Hadler and Lauren Brown and Tracy Bazan and Colin Quinn and Sam Maiser and Ratna Bhavaraju-Sanka and Jenny A. Meyer and Michael S. Cartwright and Nassim Rad and Nimish Thakore and Zabeen Mahuwala and Vishakhadatta (Vish) Mathur Kumaraswamy and James Grogan and Xiaowei Su and Mansoureh Mamarabadi and Mark Bromberg and Robert H. Brown Jr. and Kate Daniello and Jeffery Mullen and Whitney McNeely and Qihua Fan and Simona Treidler and Nathan P. Staff and Julia Yasek and Raymond Roos and Erika Renkl and Bjorn Oskarsson and Montserrat Diaz-Abad and Luisa Arroyave and Victoria Barlow and Genevive Changkuon and Melissa Cirino and Madison Coleman and Derek Dagostino and Christina Deignan and Emma Deirmendjian and Annette De Mattos and Sofia DiStefano and Kristin Drake and Michaela Estes and Precious Figueroa-Szostek and Abaigeal M. Ford and Tessa Garozzo and Meredith Hasenoehrl and Jennifer Henrique and Natalie Henrique and Samuel Hurwitz and Courtney Igne and Liam Irwin and Katie Jentoft and Boglarka Jordan and Igor Katsovskiy and Olga Kharakozova and Taylor Kolvek and Alexander Korin and Thuong La and Haining Li and Lida Mazina and Joe Ostrow and Jaclyn Pagliaro and Jack Palillo and Payal Patel and Janae Patterson and Minh Phan and Najla Popel and Jesse Rosenthal and Anil Sanjana and Catherine Small and Taylor Stimpson and Lia M. Tamburello and Natalia Tarasenko and Mirna Thomas and Eric Tustison and Emem Udo and Prasha Vigneswaran and Yusra Wahab and Anat Weiss Sadan and Isaac Whitworth and Kathy Wong and Spencer Wright and Mariah Connolly and Adrian Felix and Karly Garrett and Ashley Stepler and Abigail De La Rosa Garcia and Kamran Khan and Ivy McGlaughlin and Grace Ghali and Oyinkansola Lawal and Linda Nelson and Marissa Pabon and Diana Rede and Heather Sporn and Victor Bill and Kirsten Clark and Cornelia Kamp and Julie Kennedy and Eileen Fannon and Christopher Mark and Arian Horbovetz and Andrew McGarry and Margherita Torti},
year = {2026},
journal = {JAMA Network Open},
doi = {10.1001/jamanetworkopen.2026.34809},
url = {https://doi.org/10.1001/jamanetworkopen.2026.34809}
}RIS
TY - JOUR TI - DNL343 and Disease Progression in Amyotrophic Lateral Sclerosis AU - Sabrina Paganoni AU - Lori B. Chibnik AU - Melanie Quintana AU - Eric A. Macklin AU - Michelle A. Detry AU - Matteo Vestrucci AU - Giorgio Paulon AU - Anna McGlothlin AU - Jianing Wang AU - David Walk AU - Lauren Elman AU - Marianne Chase AU - Lindsay Heyd AU - Brittney Harkey AU - Alexander V. Sherman AU - Jeremy Shefner AU - James D. Berry AU - Erica Scirocco AU - Elisa Giacomelli AU - Hong Yu AU - Gale Kittle AU - Meaghan Hall AU - Doreen Ho AU - Omar Jawdat AU - Shafeeq Ladha AU - Eduardo Locatelli AU - Michael Rivner AU - Kevin Felice AU - Jonathan Katz AU - Senda Ajroud-Driss AU - Dominic Fee AU - Timothy Miller AU - Laura Rosow AU - Adam Quick AU - Daragh Heitzman AU - Laura A. Foster AU - Nicholas J. Maragakis AU - Stephen A. Goutman AU - Jeffrey Rosenfeld AU - Michael Benatar AU - Andrea Swenson AU - Robert Dedick Connors AU - Sheetal Shroff AU - Richard Bedlack AU - Courtney E. McIlduff AU - I-Hweii Amy Chen AU - Joseph Americo M. Fernandes AU - Alison Walsh AU - Amanda Peltier AU - Hristelina Ilieva AU - Frank Diaz AU - Hani Kushlaf AU - Said R. Beydoun AU - Bennett Myers AU - Ximena Arcila-Londono AU - Terry Heiman-Patterson AU - Michael Elliott AU - Jackie Whitesell AU - Tawfiq Al-Lahham AU - Matthew Elliott AU - Nicholas Olney AU - Michael Baer AU - Carlayne Jackson AU - Eufrosina Young AU - Jim Caress AU - Michael D. Weiss AU - Rebecca Kuenzler AU - Shakti Nayar AU - Edward J. Kasarskis AU - Zachary Simmons AU - Summer Gibson AU - Margaret Ayo Owegi AU - Namita A. Goyal AU - James P. Wymer AU - Kelly G. Gwathmey AU - Amber Erickson AU - Nurcan Gursoy AU - Gustavo Alameda AU - Cynthia Bodkin AU - Abel Wu AU - Jennifer Martinez-Thompson AU - Paul T. Twydell AU - Jinsy Andrews AU - Elham Bayat AU - Kourosh Rezania AU - Uzma Usman AU - Leo McCluskey AU - Sukanthi Kovvuru AU - Danna Jennings AU - Annette Garza-Meilandt AU - Romeo Maciuca AU - Isaac V. Cohen AU - Deepika Tamuly AU - Erden Eren AU - Merit E. Cudkowicz AU - Suma Babu AU - Unknown AU - Rachel A. Donahue AU - Hao-Wun Chen AU - Amy Kantor AU - Julia Caporaletti AU - Alexandra McCaffrey AU - Jennifer Scalia AU - Jeffrey A. Cohen AU - Jaimin Shah AU - Ghazala Hayat AU - Gary L. Pattee AU - Vinay Chaudhry AU - Lindsay Zilliox AU - Stephen Johnson AU - Constantine Farmakidis AU - Jourdan Milliard AU - Robert Bowser AU - Gabriela Lopes AU - Benjamin Barnes AU - Liberty Jenkins AU - Robert Sufit AU - April Szymanski AU - David Shrilla AU - Amber Malcolm AU - Catherine Lomen-Hoerth AU - Jill Goslinga AU - Min Kang AU - Madina Tugizova AU - Paul Sampognaro AU - Stephen Kolb AU - Sarah Heintzman AU - Alan Martin AU - Lora L. Clawson AU - Alpa Uchil AU - Kristen Riley AU - Jinae Arneklev AU - Eva L. Feldman AU - Savannah Quigley AU - Jasdeep Kaur AU - Nathan Carberry AU - Christopher Nance AU - Florian P Thomas AU - Xiaoyan Li AU - Seward Rutkove AU - Jerrica Farias AU - Tuan Vu AU - Kathleen Murray AU - Claudia Guerra Hernandez AU - Ezequiel Piccione AU - Pariwat Thaisetthawatkul AU - Alissa Romano AU - Diana L. Davis AU - Piera Pasinelli AU - Richard Lewis AU - Jacqueline Janecek AU - Leila Darki AU - Rodrigo Rodrigue AU - Luisa Rojas AU - Kara Steijlen AU - Iram Zaman AU - Anahita Deboo AU - David Ivanick AU - Brittany Guthrie AU - David Lacomis AU - Sarah Jones AU - Michael Hadler AU - Lauren Brown AU - Tracy Bazan AU - Colin Quinn AU - Sam Maiser AU - Ratna Bhavaraju-Sanka AU - Jenny A. Meyer AU - Michael S. Cartwright AU - Nassim Rad AU - Nimish Thakore AU - Zabeen Mahuwala AU - Vishakhadatta (Vish) Mathur Kumaraswamy AU - James Grogan AU - Xiaowei Su AU - Mansoureh Mamarabadi AU - Mark Bromberg AU - Robert H. Brown Jr. AU - Kate Daniello AU - Jeffery Mullen AU - Whitney McNeely AU - Qihua Fan AU - Simona Treidler AU - Nathan P. Staff AU - Julia Yasek AU - Raymond Roos AU - Erika Renkl AU - Bjorn Oskarsson AU - Montserrat Diaz-Abad AU - Luisa Arroyave AU - Victoria Barlow AU - Genevive Changkuon AU - Melissa Cirino AU - Madison Coleman AU - Derek Dagostino AU - Christina Deignan AU - Emma Deirmendjian AU - Annette De Mattos AU - Sofia DiStefano AU - Kristin Drake AU - Michaela Estes AU - Precious Figueroa-Szostek AU - Abaigeal M. Ford AU - Tessa Garozzo AU - Meredith Hasenoehrl AU - Jennifer Henrique AU - Natalie Henrique AU - Samuel Hurwitz AU - Courtney Igne AU - Liam Irwin AU - Katie Jentoft AU - Boglarka Jordan AU - Igor Katsovskiy AU - Olga Kharakozova AU - Taylor Kolvek AU - Alexander Korin AU - Thuong La AU - Haining Li AU - Lida Mazina AU - Joe Ostrow AU - Jaclyn Pagliaro AU - Jack Palillo AU - Payal Patel AU - Janae Patterson AU - Minh Phan AU - Najla Popel AU - Jesse Rosenthal AU - Anil Sanjana AU - Catherine Small AU - Taylor Stimpson AU - Lia M. Tamburello AU - Natalia Tarasenko AU - Mirna Thomas AU - Eric Tustison AU - Emem Udo AU - Prasha Vigneswaran AU - Yusra Wahab AU - Anat Weiss Sadan AU - Isaac Whitworth AU - Kathy Wong AU - Spencer Wright AU - Mariah Connolly AU - Adrian Felix AU - Karly Garrett AU - Ashley Stepler AU - Abigail De La Rosa Garcia AU - Kamran Khan AU - Ivy McGlaughlin AU - Grace Ghali AU - Oyinkansola Lawal AU - Linda Nelson AU - Marissa Pabon AU - Diana Rede AU - Heather Sporn AU - Victor Bill AU - Kirsten Clark AU - Cornelia Kamp AU - Julie Kennedy AU - Eileen Fannon AU - Christopher Mark AU - Arian Horbovetz AU - Andrew McGarry AU - Margherita Torti PY - 2026 JO - JAMA Network Open DO - 10.1001/jamanetworkopen.2026.34809 UR - https://doi.org/10.1001/jamanetworkopen.2026.34809 ER -
APA
Paganoni, S., Chibnik, L. B., Quintana, M., Macklin, E. A., Detry, M. A., Vestrucci, M., Paulon, G., McGlothlin, A., Wang, J., Walk, D., Elman, L., Chase, M., Heyd, L., Harkey, B., Sherman, A. V., Shefner, J., Berry, J. D., Scirocco, E., Giacomelli, E., Yu, H., Kittle, G., Hall, M., Ho, D., Jawdat, O., Ladha, S., Locatelli, E., Rivner, M., Felice, K., Katz, J., Ajroud-Driss, S., Fee, D., Miller, T., Rosow, L., Quick, A., Heitzman, D., Foster, L. A., Maragakis, N. J., Goutman, S. A., Rosenfeld, J., Benatar, M., Swenson, A., Connors, R. D., Shroff, S., Bedlack, R., McIlduff, C. E., Chen, I. A., Fernandes, J. A. M., Walsh, A., Peltier, A., Ilieva, H., Diaz, F., Kushlaf, H., Beydoun, S. R., Myers, B., Arcila-Londono, X., Heiman-Patterson, T., Elliott, M., Whitesell, J., Al-Lahham, T., Elliott, M., Olney, N., Baer, M., Jackson, C., Young, E., Caress, J., Weiss, M. D., Kuenzler, R., Nayar, S., Kasarskis, E. J., Simmons, Z., Gibson, S., Owegi, M. A., Goyal, N. A., Wymer, J. P., Gwathmey, K. G., Erickson, A., Gursoy, N., Alameda, G., Bodkin, C., Wu, A., Martinez-Thompson, J., Twydell, P. T., Andrews, J., Bayat, E., Rezania, K., Usman, U., McCluskey, L., Kovvuru, S., Jennings, D., Garza-Meilandt, A., Maciuca, R., Cohen, I. V., Tamuly, D., Eren, E., Cudkowicz, M. E., Babu, S., Unknown, Donahue, R. A., Chen, H., Kantor, A., Caporaletti, J., McCaffrey, A., Scalia, J., Cohen, J. A., Shah, J., Hayat, G., Pattee, G. L., Chaudhry, V., Zilliox, L., Johnson, S., Farmakidis, C., Milliard, J., Bowser, R., Lopes, G., Barnes, B., Jenkins, L., Sufit, R., Szymanski, A., Shrilla, D., Malcolm, A., Lomen-Hoerth, C., Goslinga, J., Kang, M., Tugizova, M., Sampognaro, P., Kolb, S., Heintzman, S., Martin, A., Clawson, L. L., Uchil, A., Riley, K., Arneklev, J., Feldman, E. L., Quigley, S., Kaur, J., Carberry, N., Nance, C., Thomas, F. P., Li, X., Rutkove, S., Farias, J., Vu, T., Murray, K., Hernandez, C. G., Piccione, E., Thaisetthawatkul, P., Romano, A., Davis, D. L., Pasinelli, P., Lewis, R., Janecek, J., Darki, L., Rodrigue, R., Rojas, L., Steijlen, K., Zaman, I., Deboo, A., Ivanick, D., Guthrie, B., Lacomis, D., Jones, S., Hadler, M., Brown, L., Bazan, T., Quinn, C., Maiser, S., Bhavaraju-Sanka, R., Meyer, J. A., Cartwright, M. S., Rad, N., Thakore, N., Mahuwala, Z., Kumaraswamy, V. (. M., Grogan, J., Su, X., Mamarabadi, M., Bromberg, M., Jr., R. H. B., Daniello, K., Mullen, J., McNeely, W., Fan, Q., Treidler, S., Staff, N. P., Yasek, J., Roos, R., Renkl, E., Oskarsson, B., Diaz-Abad, M., Arroyave, L., Barlow, V., Changkuon, G., Cirino, M., Coleman, M., Dagostino, D., Deignan, C., Deirmendjian, E., Mattos, A. D., DiStefano, S., Drake, K., Estes, M., Figueroa-Szostek, P., Ford, A. M., Garozzo, T., Hasenoehrl, M., Henrique, J., Henrique, N., Hurwitz, S., Igne, C., Irwin, L., Jentoft, K., Jordan, B., Katsovskiy, I., Kharakozova, O., Kolvek, T., Korin, A., La, T., Li, H., Mazina, L., Ostrow, J., Pagliaro, J., Palillo, J., Patel, P., Patterson, J., Phan, M., Popel, N., Rosenthal, J., Sanjana, A., Small, C., Stimpson, T., Tamburello, L. M., Tarasenko, N., Thomas, M., Tustison, E., Udo, E., Vigneswaran, P., Wahab, Y., Sadan, A. W., Whitworth, I., Wong, K., Wright, S., Connolly, M., Felix, A., Garrett, K., Stepler, A., Garcia, A. D. L. R., Khan, K., McGlaughlin, I., Ghali, G., Lawal, O., Nelson, L., Pabon, M., Rede, D., Sporn, H., Bill, V., Clark, K., Kamp, C., Kennedy, J., Fannon, E., Mark, C., Horbovetz, A., McGarry, A., & Torti, M. (2026). DNL343 and Disease Progression in Amyotrophic Lateral Sclerosis. JAMA Network Open. https://doi.org/10.1001/jamanetworkopen.2026.34809
Source records
- crossref · retrieved 2026-09-25T02:19:34.992Z