Efficacy and Safety of Vamorolone vs Placebo and Prednisone Among Boys With Duchenne Muscular Dystrophy

Michela Guglieri, Paula R. Clemens, Seth J. Perlman, Edward C. Smith, Iain Horrocks, Richard S. Finkel, Jean K. Mah, Nicolas Deconinck, Nathalie Goemans, Jana Haberlova, Volker Straub, Laurel J. Mengle-Gaw, Benjamin D. Schwartz, Amy D. Harper, Perry B. Shieh, Liesbeth De Waele, Diana Castro, Michelle L. Yang, Monique M. Ryan, Craig M. McDonald, Mar Tulinius, Richard Webster, Hugh J. McMillan, Nancy L. Kuntz, Vashmi K. Rao, Giovanni Baranello, Stefan Spinty, Anne-Marie Childs, Annie M. Sbrocchi, Kathryn A. Selby, Migvis Monduy, Yoram Nevo, Juan J. Vilchez-Padilla, Andres Nascimento-Osorio, Erik H. Niks, Imelda J.M. de Groot, Marina Katsalouli, Meredith K. James, Johannes van den Anker, Jesse M. Damsker, Alexandra Ahmet, Leanne M. Ward, Mark Jaros, Phil Shale, Utkarsh J. Dang, Eric P. Hoffman

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DOI: 10.1001/jamaneurol.2022.2480
Published: 2022-10-01
Container: JAMA Neurology
Publisher: American Medical Association (AMA)
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.1001/jamaneurol.2022.2480,
  title = {Efficacy and Safety of Vamorolone vs Placebo and Prednisone Among Boys With Duchenne Muscular Dystrophy},
  author = {Michela Guglieri and Paula R. Clemens and Seth J. Perlman and Edward C. Smith and Iain Horrocks and Richard S. Finkel and Jean K. Mah and Nicolas Deconinck and Nathalie Goemans and Jana Haberlova and Volker Straub and Laurel J. Mengle-Gaw and Benjamin D. Schwartz and Amy D. Harper and Perry B. Shieh and Liesbeth De Waele and Diana Castro and Michelle L. Yang and Monique M. Ryan and Craig M. McDonald and Mar Tulinius and Richard Webster and Hugh J. McMillan and Nancy L. Kuntz and Vashmi K. Rao and Giovanni Baranello and Stefan Spinty and Anne-Marie Childs and Annie M. Sbrocchi and Kathryn A. Selby and Migvis Monduy and Yoram Nevo and Juan J. Vilchez-Padilla and Andres Nascimento-Osorio and Erik H. Niks and Imelda J.M. de Groot and Marina Katsalouli and Meredith K. James and Johannes van den Anker and Jesse M. Damsker and Alexandra Ahmet and Leanne M. Ward and Mark Jaros and Phil Shale and Utkarsh J. Dang and Eric P. Hoffman},
  year = {2022},
  journal = {JAMA Neurology},
  doi = {10.1001/jamaneurol.2022.2480},
  url = {https://doi.org/10.1001/jamaneurol.2022.2480}
}

RIS

TY  - JOUR
TI  - Efficacy and Safety of Vamorolone vs Placebo and Prednisone Among Boys With Duchenne Muscular Dystrophy
AU  - Michela Guglieri
AU  - Paula R. Clemens
AU  - Seth J. Perlman
AU  - Edward C. Smith
AU  - Iain Horrocks
AU  - Richard S. Finkel
AU  - Jean K. Mah
AU  - Nicolas Deconinck
AU  - Nathalie Goemans
AU  - Jana Haberlova
AU  - Volker Straub
AU  - Laurel J. Mengle-Gaw
AU  - Benjamin D. Schwartz
AU  - Amy D. Harper
AU  - Perry B. Shieh
AU  - Liesbeth De Waele
AU  - Diana Castro
AU  - Michelle L. Yang
AU  - Monique M. Ryan
AU  - Craig M. McDonald
AU  - Mar Tulinius
AU  - Richard Webster
AU  - Hugh J. McMillan
AU  - Nancy L. Kuntz
AU  - Vashmi K. Rao
AU  - Giovanni Baranello
AU  - Stefan Spinty
AU  - Anne-Marie Childs
AU  - Annie M. Sbrocchi
AU  - Kathryn A. Selby
AU  - Migvis Monduy
AU  - Yoram Nevo
AU  - Juan J. Vilchez-Padilla
AU  - Andres Nascimento-Osorio
AU  - Erik H. Niks
AU  - Imelda J.M. de Groot
AU  - Marina Katsalouli
AU  - Meredith K. James
AU  - Johannes van den Anker
AU  - Jesse M. Damsker
AU  - Alexandra Ahmet
AU  - Leanne M. Ward
AU  - Mark Jaros
AU  - Phil Shale
AU  - Utkarsh J. Dang
AU  - Eric P. Hoffman
PY  - 2022
JO  - JAMA Neurology
DO  - 10.1001/jamaneurol.2022.2480
UR  - https://doi.org/10.1001/jamaneurol.2022.2480
ER  -

APA

Guglieri, M., Clemens, P. R., Perlman, S. J., Smith, E. C., Horrocks, I., Finkel, R. S., Mah, J. K., Deconinck, N., Goemans, N., Haberlova, J., Straub, V., Mengle-Gaw, L. J., Schwartz, B. D., Harper, A. D., Shieh, P. B., Waele, L. D., Castro, D., Yang, M. L., Ryan, M. M., McDonald, C. M., Tulinius, M., Webster, R., McMillan, H. J., Kuntz, N. L., Rao, V. K., Baranello, G., Spinty, S., Childs, A., Sbrocchi, A. M., Selby, K. A., Monduy, M., Nevo, Y., Vilchez-Padilla, J. J., Nascimento-Osorio, A., Niks, E. H., Groot, I. J. D., Katsalouli, M., James, M. K., Anker, J. V. D., Damsker, J. M., Ahmet, A., Ward, L. M., Jaros, M., Shale, P., Dang, U. J., & Hoffman, E. P. (2022). Efficacy and Safety of Vamorolone vs Placebo and Prednisone Among Boys With Duchenne Muscular Dystrophy. JAMA Neurology. https://doi.org/10.1001/jamaneurol.2022.2480

Source records

crossref · retrieved 2026-09-25T18:16:31.202Z