Antisense Oligonucleotide Tofersen Distribution in the Central Nervous System of SOD1-ALS Autopsy Tissue Donors.

Guise AJ, Sellon MT, Roemer SF, Monine M, Comfort Harris NT, Bartlett D, David E, Xu S, Jandreski L, Malek S, Garafalo S, Nestorov I, Ireland MD, King A, Bowser RP, Korben VA, Ravits J, Shaw PJ, Highley JR, Ferguson TA, Fradette S, Graham DL, Sorenson EJ, Oskarsson B, Reichard RR, Dickson DW, Paganoni S, Babu S, Oakley DH, Frosch MP, Miller TM, Bucelli RC, Perrin RJ, Ly CV, Plowey ED

Open source

DOI: 10.1001/jamaneurol.2026.2195
Published: 2026 Sep 1
Container: JAMA neurology
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1001/jamaneurol.2026.2195,
  title = {Antisense Oligonucleotide Tofersen Distribution in the Central Nervous System of SOD1-ALS Autopsy Tissue Donors.},
  author = {Guise AJ and Sellon MT and Roemer SF and Monine M and Comfort Harris NT and Bartlett D and David E and Xu S and Jandreski L and Malek S and Garafalo S and Nestorov I and Ireland MD and King A and Bowser RP and Korben VA and Ravits J and Shaw PJ and Highley JR and Ferguson TA and Fradette S and Graham DL and Sorenson EJ and Oskarsson B and Reichard RR and Dickson DW and Paganoni S and Babu S and Oakley DH and Frosch MP and Miller TM and Bucelli RC and Perrin RJ and Ly CV and Plowey ED},
  year = {2026},
  journal = {JAMA neurology},
  doi = {10.1001/jamaneurol.2026.2195},
  url = {https://doi.org/10.1001/jamaneurol.2026.2195}
}

RIS

TY  - JOUR
TI  - Antisense Oligonucleotide Tofersen Distribution in the Central Nervous System of SOD1-ALS Autopsy Tissue Donors.
AU  - Guise AJ
AU  - Sellon MT
AU  - Roemer SF
AU  - Monine M
AU  - Comfort Harris NT
AU  - Bartlett D
AU  - David E
AU  - Xu S
AU  - Jandreski L
AU  - Malek S
AU  - Garafalo S
AU  - Nestorov I
AU  - Ireland MD
AU  - King A
AU  - Bowser RP
AU  - Korben VA
AU  - Ravits J
AU  - Shaw PJ
AU  - Highley JR
AU  - Ferguson TA
AU  - Fradette S
AU  - Graham DL
AU  - Sorenson EJ
AU  - Oskarsson B
AU  - Reichard RR
AU  - Dickson DW
AU  - Paganoni S
AU  - Babu S
AU  - Oakley DH
AU  - Frosch MP
AU  - Miller TM
AU  - Bucelli RC
AU  - Perrin RJ
AU  - Ly CV
AU  - Plowey ED
PY  - 2026
JO  - JAMA neurology
DO  - 10.1001/jamaneurol.2026.2195
UR  - https://doi.org/10.1001/jamaneurol.2026.2195
ER  -

APA

AJ, G., MT, S., SF, R., M, M., NT, C. H., D, B., E, D., S, X., L, J., S, M., S, G., I, N., MD, I., A, K., RP, B., VA, K., J, R., PJ, S., JR, H., TA, F., S, F., DL, G., EJ, S., B, O., RR, R., DW, D., S, P., S, B., DH, O., MP, F., TM, M., RC, B., RJ, P., CV, L., & ED, P. (2026). Antisense Oligonucleotide Tofersen Distribution in the Central Nervous System of SOD1-ALS Autopsy Tissue Donors.. JAMA neurology. https://doi.org/10.1001/jamaneurol.2026.2195

Source records

pubmed · retrieved 2026-09-26T06:56:24.402Z