Vision Outcomes in Children Treated With Voretigene Neparvovec for RPE65-Associated Retinopathy.

Thompson DA, De Smit E, Tan W, Handley SE, Marmoy OR, Henderson RH

DOI: 10.1001/jamaophthalmol.2025.5505
Published: 2026 Feb 1
Container: JAMA ophthalmology
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1001/jamaophthalmol.2025.5505,
  title = {Vision Outcomes in Children Treated With Voretigene Neparvovec for RPE65-Associated Retinopathy.},
  author = {Thompson DA and De Smit E and Tan W and Handley SE and Marmoy OR and Henderson RH},
  year = {2026},
  journal = {JAMA ophthalmology},
  doi = {10.1001/jamaophthalmol.2025.5505},
  url = {https://doi.org/10.1001/jamaophthalmol.2025.5505}
}

RIS

TY  - JOUR
TI  - Vision Outcomes in Children Treated With Voretigene Neparvovec for RPE65-Associated Retinopathy.
AU  - Thompson DA
AU  - De Smit E
AU  - Tan W
AU  - Handley SE
AU  - Marmoy OR
AU  - Henderson RH
PY  - 2026
JO  - JAMA ophthalmology
DO  - 10.1001/jamaophthalmol.2025.5505
UR  - https://doi.org/10.1001/jamaophthalmol.2025.5505
ER  -

APA

DA, T., E, D. S., W, T., SE, H., OR, M., & RH, H. (2026). Vision Outcomes in Children Treated With Voretigene Neparvovec for RPE65-Associated Retinopathy.. JAMA ophthalmology. https://doi.org/10.1001/jamaophthalmol.2025.5505

Source records

pubmed · retrieved 2026-09-27T13:12:14.177Z
europe-pmc · retrieved 2026-09-27T13:12:14.193Z