Long-Term Evaluation of Givinostat in Duchenne Muscular Dystrophy, and Natural History Comparisons.

McDonald CM, Guglieri M, Vučinić D, Acsadi G, Brandsema JF, Bruno C, Finanger EL, Harper A, Lobato ML, Masson R, Muelas N, Munell F, Nevo Y, Péréon Y, Phan H, Sansone VA, Scoto M, Willis T, Finkel RS, Vandenborne K, Cazzaniga S, Montrasio S, Alessi F, Bettica P, Mercuri E, Givinostat Study 51 Investigators, Cooperative International Neuromuscular Research Group (CINRG) Duchenne Natural History Study (DNHS) Investigators, ImagingDMD Investigators

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DOI: 10.1002/acn3.70165
Published: 2025 Nov
Container: Annals of clinical and translational neurology
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1002/acn3.70165,
  title = {Long-Term Evaluation of Givinostat in Duchenne Muscular Dystrophy, and Natural History Comparisons.},
  author = {McDonald CM and Guglieri M and Vučinić D and Acsadi G and Brandsema JF and Bruno C and Finanger EL and Harper A and Lobato ML and Masson R and Muelas N and Munell F and Nevo Y and Péréon Y and Phan H and Sansone VA and Scoto M and Willis T and Finkel RS and Vandenborne K and Cazzaniga S and Montrasio S and Alessi F and Bettica P and Mercuri E and Givinostat Study 51 Investigators and Cooperative International Neuromuscular Research Group (CINRG) Duchenne Natural History Study (DNHS) Investigators and ImagingDMD Investigators},
  year = {2025},
  journal = {Annals of clinical and translational neurology},
  doi = {10.1002/acn3.70165},
  url = {https://doi.org/10.1002/acn3.70165}
}

RIS

TY  - JOUR
TI  - Long-Term Evaluation of Givinostat in Duchenne Muscular Dystrophy, and Natural History Comparisons.
AU  - McDonald CM
AU  - Guglieri M
AU  - Vučinić D
AU  - Acsadi G
AU  - Brandsema JF
AU  - Bruno C
AU  - Finanger EL
AU  - Harper A
AU  - Lobato ML
AU  - Masson R
AU  - Muelas N
AU  - Munell F
AU  - Nevo Y
AU  - Péréon Y
AU  - Phan H
AU  - Sansone VA
AU  - Scoto M
AU  - Willis T
AU  - Finkel RS
AU  - Vandenborne K
AU  - Cazzaniga S
AU  - Montrasio S
AU  - Alessi F
AU  - Bettica P
AU  - Mercuri E
AU  - Givinostat Study 51 Investigators
AU  - Cooperative International Neuromuscular Research Group (CINRG) Duchenne Natural History Study (DNHS) Investigators
AU  - ImagingDMD Investigators
PY  - 2025
JO  - Annals of clinical and translational neurology
DO  - 10.1002/acn3.70165
UR  - https://doi.org/10.1002/acn3.70165
ER  -

APA

CM, M., M, G., D, V., G, A., JF, B., C, B., EL, F., A, H., ML, L., R, M., N, M., F, M., Y, N., Y, P., H, P., VA, S., M, S., T, W., RS, F., K, V., S, C., S, M., F, A., P, B., E, M., Investigators, G. S. 5., Investigators, C. I. N. R. G. (. D. N. H. S. (., & Investigators, I. (2025). Long-Term Evaluation of Givinostat in Duchenne Muscular Dystrophy, and Natural History Comparisons.. Annals of clinical and translational neurology. https://doi.org/10.1002/acn3.70165

Source records

pubmed · retrieved 2026-09-27T01:07:48.915Z