Onasemnogene Abeparvovec in Patients With <scp>SMA</scp> : Interim Results of the <scp>RESTORE</scp> Registry in Japan

Kayoko Saito, Kamal Benguerba, Ken Tsuchida, Kazushige Yazawa, Isao Tsumiyama, Hiromitsu Kayama, Sandra P. Reyna, Farid Khan, Richard S. Finkel

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DOI: 10.1002/acn3.70437
Published: 2026-06-09
Container: Annals of Clinical and Translational Neurology
Publisher: Wiley
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.1002/acn3.70437,
  title = {Onasemnogene Abeparvovec in Patients With
                    <scp>SMA</scp>
                    : Interim Results of the
                    <scp>RESTORE</scp>
                    Registry in Japan},
  author = {Kayoko Saito and Kamal Benguerba and Ken Tsuchida and Kazushige Yazawa and Isao Tsumiyama and Hiromitsu Kayama and Sandra P. Reyna and Farid Khan and Richard S. Finkel},
  year = {2026},
  journal = {Annals of Clinical and Translational Neurology},
  doi = {10.1002/acn3.70437},
  url = {https://doi.org/10.1002/acn3.70437}
}

RIS

TY  - JOUR
TI  - Onasemnogene Abeparvovec in Patients With
                    <scp>SMA</scp>
                    : Interim Results of the
                    <scp>RESTORE</scp>
                    Registry in Japan
AU  - Kayoko Saito
AU  - Kamal Benguerba
AU  - Ken Tsuchida
AU  - Kazushige Yazawa
AU  - Isao Tsumiyama
AU  - Hiromitsu Kayama
AU  - Sandra P. Reyna
AU  - Farid Khan
AU  - Richard S. Finkel
PY  - 2026
JO  - Annals of Clinical and Translational Neurology
DO  - 10.1002/acn3.70437
UR  - https://doi.org/10.1002/acn3.70437
ER  -

APA

Saito, K., Benguerba, K., Tsuchida, K., Yazawa, K., Tsumiyama, I., Kayama, H., Reyna, S. P., Khan, F., & Finkel, R. S. (2026). Onasemnogene Abeparvovec in Patients With <scp>SMA</scp> : Interim Results of the <scp>RESTORE</scp> Registry in Japan. Annals of Clinical and Translational Neurology. https://doi.org/10.1002/acn3.70437

Source records

crossref · retrieved 2026-09-26T08:31:22.716Z