Nucleoside-Modified mRNA Encoding Alpha-Galactosidase A Ameliorates Fabry Disease Phenotypes in Human IPSC-Derived Cardiomyocytes.

Juchem M, Oehlsen L, Ersoy S, Ye JL, Weber N, Mohr E, Agyapong W, Liu J, Fuchs M, Xiao K, Jahn C, Eggenschwiler R, Cantz T, Beimdiek J, Buettner FFR, Kraft T, Hegermann J, Knorr IJ, Ernst L, Feldbrügge L, Puffert R, Schmidt K, Bär C, Hoepfner J, Thum T

Open source

DOI: 10.1002/advs.77151
Published: 2026 Aug 13
Container: Advanced science (Weinheim, Baden-Wurttemberg, Germany)
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1002/advs.77151,
  title = {Nucleoside-Modified mRNA Encoding Alpha-Galactosidase A Ameliorates Fabry Disease Phenotypes in Human IPSC-Derived Cardiomyocytes.},
  author = {Juchem M and Oehlsen L and Ersoy S and Ye JL and Weber N and Mohr E and Agyapong W and Liu J and Fuchs M and Xiao K and Jahn C and Eggenschwiler R and Cantz T and Beimdiek J and Buettner FFR and Kraft T and Hegermann J and Knorr IJ and Ernst L and Feldbrügge L and Puffert R and Schmidt K and Bär C and Hoepfner J and Thum T},
  year = {2026},
  journal = {Advanced science (Weinheim, Baden-Wurttemberg, Germany)},
  doi = {10.1002/advs.77151},
  url = {https://doi.org/10.1002/advs.77151}
}

RIS

TY  - JOUR
TI  - Nucleoside-Modified mRNA Encoding Alpha-Galactosidase A Ameliorates Fabry Disease Phenotypes in Human IPSC-Derived Cardiomyocytes.
AU  - Juchem M
AU  - Oehlsen L
AU  - Ersoy S
AU  - Ye JL
AU  - Weber N
AU  - Mohr E
AU  - Agyapong W
AU  - Liu J
AU  - Fuchs M
AU  - Xiao K
AU  - Jahn C
AU  - Eggenschwiler R
AU  - Cantz T
AU  - Beimdiek J
AU  - Buettner FFR
AU  - Kraft T
AU  - Hegermann J
AU  - Knorr IJ
AU  - Ernst L
AU  - Feldbrügge L
AU  - Puffert R
AU  - Schmidt K
AU  - Bär C
AU  - Hoepfner J
AU  - Thum T
PY  - 2026
JO  - Advanced science (Weinheim, Baden-Wurttemberg, Germany)
DO  - 10.1002/advs.77151
UR  - https://doi.org/10.1002/advs.77151
ER  -

APA

M, J., L, O., S, E., JL, Y., N, W., E, M., W, A., J, L., M, F., K, X., C, J., R, E., T, C., J, B., FFR, B., T, K., J, H., IJ, K., L, E., L, F., R, P., K, S., C, B., J, H., & T, T. (2026). Nucleoside-Modified mRNA Encoding Alpha-Galactosidase A Ameliorates Fabry Disease Phenotypes in Human IPSC-Derived Cardiomyocytes.. Advanced science (Weinheim, Baden-Wurttemberg, Germany). https://doi.org/10.1002/advs.77151

Source records

pubmed · retrieved 2026-09-27T15:00:02.071Z
europe-pmc · retrieved 2026-09-27T15:00:02.084Z