Navigating Drug Discovery for Myhre Syndrome: The Complexity of a Multisystemic Rare Disease.

Pindon A, Brunetti-Pierri N, Young KH, Young MK, Macias MJ, Mo X.

DOI: 10.1002/ajmg.c.32156
Published: 2025-11-03
Container: Am J Med Genet C Semin Med Genet
Publisher: Not recorded
Open access: no

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Cite this work

BibTeX

@article{allodium:10.1002/ajmg.c.32156,
  title = {Navigating Drug Discovery for Myhre Syndrome: The Complexity of a Multisystemic Rare Disease.},
  author = {Pindon A and  Brunetti-Pierri N and  Young KH and  Young MK and  Macias MJ and  Mo X.},
  year = {2025},
  journal = {Am J Med Genet C Semin Med Genet},
  doi = {10.1002/ajmg.c.32156},
  url = {https://doi.org/10.1002/ajmg.c.32156}
}

RIS

TY  - JOUR
TI  - Navigating Drug Discovery for Myhre Syndrome: The Complexity of a Multisystemic Rare Disease.
AU  - Pindon A
AU  -  Brunetti-Pierri N
AU  -  Young KH
AU  -  Young MK
AU  -  Macias MJ
AU  -  Mo X.
PY  - 2025
JO  - Am J Med Genet C Semin Med Genet
DO  - 10.1002/ajmg.c.32156
UR  - https://doi.org/10.1002/ajmg.c.32156
ER  -

APA

A, P., N, B., KH, Y., MK, Y., MJ, M., & X., M. (2025). Navigating Drug Discovery for Myhre Syndrome: The Complexity of a Multisystemic Rare Disease.. Am J Med Genet C Semin Med Genet. https://doi.org/10.1002/ajmg.c.32156

Source records

europe-pmc · retrieved 2026-09-24T19:51:06.313Z