Challenges and Possible Strategies to Address Them in Rare Disease Drug Development: A Statistical Perspective.

Chen J, Nie L, Lee S, Chu H, Tian H, Wang Y, He W, Jemielita T, Gruber S, Song Y, Tamura R, Tian L, Zhao Y, Chen Y, van der Laan M, Lee H

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DOI
10.1002/cpt.3631
Published
2025 Jul
Container
Clinical pharmacology and therapeutics
Publisher
Not recorded
Open access
unknown

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BibTeX

@article{allodium:10.1002/cpt.3631,
  title = {Challenges and Possible Strategies to Address Them in Rare Disease Drug Development: A Statistical Perspective.},
  author = {Chen J and Nie L and Lee S and Chu H and Tian H and Wang Y and He W and Jemielita T and Gruber S and Song Y and Tamura R and Tian L and Zhao Y and Chen Y and van der Laan M and Lee H},
  year = {2025},
  journal = {Clinical pharmacology and therapeutics},
  doi = {10.1002/cpt.3631},
  url = {https://doi.org/10.1002/cpt.3631}
}

RIS

TY  - JOUR
TI  - Challenges and Possible Strategies to Address Them in Rare Disease Drug Development: A Statistical Perspective.
AU  - Chen J
AU  - Nie L
AU  - Lee S
AU  - Chu H
AU  - Tian H
AU  - Wang Y
AU  - He W
AU  - Jemielita T
AU  - Gruber S
AU  - Song Y
AU  - Tamura R
AU  - Tian L
AU  - Zhao Y
AU  - Chen Y
AU  - van der Laan M
AU  - Lee H
PY  - 2025
JO  - Clinical pharmacology and therapeutics
DO  - 10.1002/cpt.3631
UR  - https://doi.org/10.1002/cpt.3631
ER  - 

APA

J, C., L, N., S, L., H, C., H, T., Y, W., W, H., T, J., S, G., Y, S., R, T., L, T., Y, Z., Y, C., M, V. D. L., & H, L. (2025). Challenges and Possible Strategies to Address Them in Rare Disease Drug Development: A Statistical Perspective.. Clinical pharmacology and therapeutics. https://doi.org/10.1002/cpt.3631

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