Challenges and Possible Strategies to Address Them in Rare Disease Drug Development: A Statistical Perspective.
- DOI
- 10.1002/cpt.3631
- Published
- 2025 Jul
- Container
- Clinical pharmacology and therapeutics
- Publisher
- Not recorded
- Open access
- unknown
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Cite this work
BibTeX
@article{allodium:10.1002/cpt.3631,
title = {Challenges and Possible Strategies to Address Them in Rare Disease Drug Development: A Statistical Perspective.},
author = {Chen J and Nie L and Lee S and Chu H and Tian H and Wang Y and He W and Jemielita T and Gruber S and Song Y and Tamura R and Tian L and Zhao Y and Chen Y and van der Laan M and Lee H},
year = {2025},
journal = {Clinical pharmacology and therapeutics},
doi = {10.1002/cpt.3631},
url = {https://doi.org/10.1002/cpt.3631}
}RIS
TY - JOUR TI - Challenges and Possible Strategies to Address Them in Rare Disease Drug Development: A Statistical Perspective. AU - Chen J AU - Nie L AU - Lee S AU - Chu H AU - Tian H AU - Wang Y AU - He W AU - Jemielita T AU - Gruber S AU - Song Y AU - Tamura R AU - Tian L AU - Zhao Y AU - Chen Y AU - van der Laan M AU - Lee H PY - 2025 JO - Clinical pharmacology and therapeutics DO - 10.1002/cpt.3631 UR - https://doi.org/10.1002/cpt.3631 ER -
APA
J, C., L, N., S, L., H, C., H, T., Y, W., W, H., T, J., S, G., Y, S., R, T., L, T., Y, Z., Y, C., M, V. D. L., & H, L. (2025). Challenges and Possible Strategies to Address Them in Rare Disease Drug Development: A Statistical Perspective.. Clinical pharmacology and therapeutics. https://doi.org/10.1002/cpt.3631
Source records
- pubmed · retrieved 2026-09-26T23:30:09.793Z