Lentivirus-mediated gene therapy for Fabry disease: 5-year End-of-Study results from the Canadian FACTs trial.

Khan A, Barber DL, McKillop WM, Rupar CA, Auray-Blais C, Fraser G, Fowler DH, Berger A, Foley R, Keating A, West ML, Medin JA

Open source

DOI: 10.1002/ctm2.70073
Published: 2025 Jan
Container: Clinical and translational medicine
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1002/ctm2.70073,
  title = {Lentivirus-mediated gene therapy for Fabry disease: 5-year End-of-Study results from the Canadian FACTs trial.},
  author = {Khan A and Barber DL and McKillop WM and Rupar CA and Auray-Blais C and Fraser G and Fowler DH and Berger A and Foley R and Keating A and West ML and Medin JA},
  year = {2025},
  journal = {Clinical and translational medicine},
  doi = {10.1002/ctm2.70073},
  url = {https://doi.org/10.1002/ctm2.70073}
}

RIS

TY  - JOUR
TI  - Lentivirus-mediated gene therapy for Fabry disease: 5-year End-of-Study results from the Canadian FACTs trial.
AU  - Khan A
AU  - Barber DL
AU  - McKillop WM
AU  - Rupar CA
AU  - Auray-Blais C
AU  - Fraser G
AU  - Fowler DH
AU  - Berger A
AU  - Foley R
AU  - Keating A
AU  - West ML
AU  - Medin JA
PY  - 2025
JO  - Clinical and translational medicine
DO  - 10.1002/ctm2.70073
UR  - https://doi.org/10.1002/ctm2.70073
ER  -

APA

A, K., DL, B., WM, M., CA, R., C, A., G, F., DH, F., A, B., R, F., A, K., ML, W., & JA, M. (2025). Lentivirus-mediated gene therapy for Fabry disease: 5-year End-of-Study results from the Canadian FACTs trial.. Clinical and translational medicine. https://doi.org/10.1002/ctm2.70073

Source records

pubmed · retrieved 2026-09-26T23:51:55.279Z