Pharmacodynamics, Efficacy, and Safety of Intraputaminal Eladocagene Exuparvovec Administered to Pediatric Patients With Aromatic L-Amino Acid Decarboxylase Deficiency Using an MR-Compatible Cannula: 48 Weeks of Follow-Up.

Curry DJ, Pearl PL, Stone SSD, Gilbert DL, Vadivelu S, Ben-Zeev B, Vestal M, Zafar M, Tai CH, Chou SC, Zibly Z, Ungar L, Parnes M, Hull M, Emrick L, Werner C, Krolick A, Penematsa V, Wang A, Rahman R, Golden L, Chien YH, Hwu PW

Open source

DOI: 10.1002/jimd.70151
Published: 2026 Mar
Container: Journal of inherited metabolic disease
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1002/jimd.70151,
  title = {Pharmacodynamics, Efficacy, and Safety of Intraputaminal Eladocagene Exuparvovec Administered to Pediatric Patients With Aromatic L-Amino Acid Decarboxylase Deficiency Using an MR-Compatible Cannula: 48 Weeks of Follow-Up.},
  author = {Curry DJ and Pearl PL and Stone SSD and Gilbert DL and Vadivelu S and Ben-Zeev B and Vestal M and Zafar M and Tai CH and Chou SC and Zibly Z and Ungar L and Parnes M and Hull M and Emrick L and Werner C and Krolick A and Penematsa V and Wang A and Rahman R and Golden L and Chien YH and Hwu PW},
  year = {2026},
  journal = {Journal of inherited metabolic disease},
  doi = {10.1002/jimd.70151},
  url = {https://doi.org/10.1002/jimd.70151}
}

RIS

TY  - JOUR
TI  - Pharmacodynamics, Efficacy, and Safety of Intraputaminal Eladocagene Exuparvovec Administered to Pediatric Patients With Aromatic L-Amino Acid Decarboxylase Deficiency Using an MR-Compatible Cannula: 48 Weeks of Follow-Up.
AU  - Curry DJ
AU  - Pearl PL
AU  - Stone SSD
AU  - Gilbert DL
AU  - Vadivelu S
AU  - Ben-Zeev B
AU  - Vestal M
AU  - Zafar M
AU  - Tai CH
AU  - Chou SC
AU  - Zibly Z
AU  - Ungar L
AU  - Parnes M
AU  - Hull M
AU  - Emrick L
AU  - Werner C
AU  - Krolick A
AU  - Penematsa V
AU  - Wang A
AU  - Rahman R
AU  - Golden L
AU  - Chien YH
AU  - Hwu PW
PY  - 2026
JO  - Journal of inherited metabolic disease
DO  - 10.1002/jimd.70151
UR  - https://doi.org/10.1002/jimd.70151
ER  -

APA

DJ, C., PL, P., SSD, S., DL, G., S, V., B, B., M, V., M, Z., CH, T., SC, C., Z, Z., L, U., M, P., M, H., L, E., C, W., A, K., V, P., A, W., R, R., L, G., YH, C., & PW, H. (2026). Pharmacodynamics, Efficacy, and Safety of Intraputaminal Eladocagene Exuparvovec Administered to Pediatric Patients With Aromatic L-Amino Acid Decarboxylase Deficiency Using an MR-Compatible Cannula: 48 Weeks of Follow-Up.. Journal of inherited metabolic disease. https://doi.org/10.1002/jimd.70151

Source records

pubmed · retrieved 2026-09-27T07:46:26.933Z