Migalastat Versus Enzyme Replacement Therapy in Treatment-Naïve Fabry Disease: Real-World Evidence From the followME Fabry Pathfinders Registry.
- DOI
- 10.1002/jimd.70261
- Published
- 2026 Nov
- Container
- Journal of inherited metabolic disease
- Publisher
- Not recorded
- Open access
- unknown
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limited evidence Score 43/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.
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Cite this work
BibTeX
@article{allodium:10.1002/jimd.70261,
title = {Migalastat Versus Enzyme Replacement Therapy in Treatment-Naïve Fabry Disease: Real-World Evidence From the followME Fabry Pathfinders Registry.},
author = {Nordbeck P and Kopiec A and Hummel N and Gielen V and Veleva-Rotse BO and MacCulloch A},
year = {2026},
journal = {Journal of inherited metabolic disease},
doi = {10.1002/jimd.70261},
url = {https://doi.org/10.1002/jimd.70261}
}RIS
TY - JOUR TI - Migalastat Versus Enzyme Replacement Therapy in Treatment-Naïve Fabry Disease: Real-World Evidence From the followME Fabry Pathfinders Registry. AU - Nordbeck P AU - Kopiec A AU - Hummel N AU - Gielen V AU - Veleva-Rotse BO AU - MacCulloch A PY - 2026 JO - Journal of inherited metabolic disease DO - 10.1002/jimd.70261 UR - https://doi.org/10.1002/jimd.70261 ER -
APA
P, N., A, K., N, H., V, G., BO, V., & A, M. (2026). Migalastat Versus Enzyme Replacement Therapy in Treatment-Naïve Fabry Disease: Real-World Evidence From the followME Fabry Pathfinders Registry.. Journal of inherited metabolic disease. https://doi.org/10.1002/jimd.70261
Source records
- pubmed · retrieved 2026-11-10T05:50:28.534Z