Nucleic Acid Therapeutics in Rare Disease: From Precision Medicine to Programmable Platforms

Tomasz Z. Tomkiewicz, Siyamini Sivananthan, Paul Gissen, Haiyan Zhou

Open source

DOI: 10.1002/jimd.70262
Published: 2026-11
Container: Journal of Inherited Metabolic Disease
Publisher: Wiley
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.1002/jimd.70262,
  title = {Nucleic Acid Therapeutics in Rare Disease: From Precision Medicine to Programmable Platforms},
  author = {Tomasz Z. Tomkiewicz and Siyamini Sivananthan and Paul Gissen and Haiyan Zhou},
  year = {2026},
  journal = {Journal of Inherited Metabolic Disease},
  doi = {10.1002/jimd.70262},
  url = {https://doi.org/10.1002/jimd.70262}
}

RIS

TY  - JOUR
TI  - Nucleic Acid Therapeutics in Rare Disease: From Precision Medicine to Programmable Platforms
AU  - Tomasz Z. Tomkiewicz
AU  - Siyamini Sivananthan
AU  - Paul Gissen
AU  - Haiyan Zhou
PY  - 2026
JO  - Journal of Inherited Metabolic Disease
DO  - 10.1002/jimd.70262
UR  - https://doi.org/10.1002/jimd.70262
ER  -

APA

Tomkiewicz, T. Z., Sivananthan, S., Gissen, P., & Zhou, H. (2026). Nucleic Acid Therapeutics in Rare Disease: From Precision Medicine to Programmable Platforms. Journal of Inherited Metabolic Disease. https://doi.org/10.1002/jimd.70262

Source records

crossref · retrieved 2026-11-05T05:01:11.776Z