Small Molecules to Elevate Rab7-GTPase Activity and Lower Cholesterol Accumulation in Niemann-Pick Type C Disease.

Nguyen MKL, Nikenich MR, Seifert K, Pinkenburg C, Lai F, Walther HL, Hartmann M, Szulc A, Sparkes E, Chen S, Wikramanayake R, Bernaus-Esqué M, Liu Y, Tebar F, Serwetnyk M, Wenninger A, Patzke C, Blagg BSJ, Ashfeld BL, Groundwater PW, Hibbs DE, Hoy AJ, Rentero C, Enrich C, Cho AN, Du JJ, Grewal T

Open source

DOI: 10.1007/s11095-026-04058-8
Published: 2026 Apr
Container: Pharmaceutical research
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1007/s11095-026-04058-8,
  title = {Small Molecules to Elevate Rab7-GTPase Activity and Lower Cholesterol Accumulation in Niemann-Pick Type C Disease.},
  author = {Nguyen MKL and Nikenich MR and Seifert K and Pinkenburg C and Lai F and Walther HL and Hartmann M and Szulc A and Sparkes E and Chen S and Wikramanayake R and Bernaus-Esqué M and Liu Y and Tebar F and Serwetnyk M and Wenninger A and Patzke C and Blagg BSJ and Ashfeld BL and Groundwater PW and Hibbs DE and Hoy AJ and Rentero C and Enrich C and Cho AN and Du JJ and Grewal T},
  year = {2026},
  journal = {Pharmaceutical research},
  doi = {10.1007/s11095-026-04058-8},
  url = {https://doi.org/10.1007/s11095-026-04058-8}
}

RIS

TY  - JOUR
TI  - Small Molecules to Elevate Rab7-GTPase Activity and Lower Cholesterol Accumulation in Niemann-Pick Type C Disease.
AU  - Nguyen MKL
AU  - Nikenich MR
AU  - Seifert K
AU  - Pinkenburg C
AU  - Lai F
AU  - Walther HL
AU  - Hartmann M
AU  - Szulc A
AU  - Sparkes E
AU  - Chen S
AU  - Wikramanayake R
AU  - Bernaus-Esqué M
AU  - Liu Y
AU  - Tebar F
AU  - Serwetnyk M
AU  - Wenninger A
AU  - Patzke C
AU  - Blagg BSJ
AU  - Ashfeld BL
AU  - Groundwater PW
AU  - Hibbs DE
AU  - Hoy AJ
AU  - Rentero C
AU  - Enrich C
AU  - Cho AN
AU  - Du JJ
AU  - Grewal T
PY  - 2026
JO  - Pharmaceutical research
DO  - 10.1007/s11095-026-04058-8
UR  - https://doi.org/10.1007/s11095-026-04058-8
ER  -

APA

MKL, N., MR, N., K, S., C, P., F, L., HL, W., M, H., A, S., E, S., S, C., R, W., M, B., Y, L., F, T., M, S., A, W., C, P., BSJ, B., BL, A., PW, G., DE, H., AJ, H., C, R., C, E., AN, C., JJ, D., & T, G. (2026). Small Molecules to Elevate Rab7-GTPase Activity and Lower Cholesterol Accumulation in Niemann-Pick Type C Disease.. Pharmaceutical research. https://doi.org/10.1007/s11095-026-04058-8

Source records

pubmed · retrieved 2026-09-26T10:29:55.748Z