Intraputaminal AAV9 co-delivery of AADC and GDNF in severe AADC deficiency: first-in-human pediatric dose-escalation study

Feng Han, Pingping Gao, Youfeng Zhou, Tongtong Cui, Yichao Xu, Xi Fang, Min Shen, Suzhen Dong, Yumin Zhong, Yingyan Wang, Lijun Bu, Li Chen, Yuanyin Xia, Ruen Yao, Nan Bao, Bin Xue, Yingying Tao, Jingjie Ge, Zizhao Ju, Yuhua Zhu, Yihui Guan, Chuantao Zuo, Xinyan Sun, Shan Ding, Gui Cao, Xianfeng Wang, Li Feng, Hongxia Mao, Hua Lv, Xiaoping Zhao, Wei Li, Jiwen Wang, Yunhai Song

Open source

DOI: 10.1007/s11427-026-3407-8
Published: 2026-09-21
Container: Science China Life Sciences
Publisher: Springer Science and Business Media LLC
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.1007/s11427-026-3407-8,
  title = {Intraputaminal AAV9 co-delivery of AADC and GDNF in severe AADC deficiency: first-in-human pediatric dose-escalation study},
  author = {Feng Han and Pingping Gao and Youfeng Zhou and Tongtong Cui and Yichao Xu and Xi Fang and Min Shen and Suzhen Dong and Yumin Zhong and Yingyan Wang and Lijun Bu and Li Chen and Yuanyin Xia and Ruen Yao and Nan Bao and Bin Xue and Yingying Tao and Jingjie Ge and Zizhao Ju and Yuhua Zhu and Yihui Guan and Chuantao Zuo and Xinyan Sun and Shan Ding and Gui Cao and Xianfeng Wang and Li Feng and Hongxia Mao and Hua Lv and Xiaoping Zhao and Wei Li and Jiwen Wang and Yunhai Song},
  year = {2026},
  journal = {Science China Life Sciences},
  doi = {10.1007/s11427-026-3407-8},
  url = {https://doi.org/10.1007/s11427-026-3407-8}
}

RIS

TY  - JOUR
TI  - Intraputaminal AAV9 co-delivery of AADC and GDNF in severe AADC deficiency: first-in-human pediatric dose-escalation study
AU  - Feng Han
AU  - Pingping Gao
AU  - Youfeng Zhou
AU  - Tongtong Cui
AU  - Yichao Xu
AU  - Xi Fang
AU  - Min Shen
AU  - Suzhen Dong
AU  - Yumin Zhong
AU  - Yingyan Wang
AU  - Lijun Bu
AU  - Li Chen
AU  - Yuanyin Xia
AU  - Ruen Yao
AU  - Nan Bao
AU  - Bin Xue
AU  - Yingying Tao
AU  - Jingjie Ge
AU  - Zizhao Ju
AU  - Yuhua Zhu
AU  - Yihui Guan
AU  - Chuantao Zuo
AU  - Xinyan Sun
AU  - Shan Ding
AU  - Gui Cao
AU  - Xianfeng Wang
AU  - Li Feng
AU  - Hongxia Mao
AU  - Hua Lv
AU  - Xiaoping Zhao
AU  - Wei Li
AU  - Jiwen Wang
AU  - Yunhai Song
PY  - 2026
JO  - Science China Life Sciences
DO  - 10.1007/s11427-026-3407-8
UR  - https://doi.org/10.1007/s11427-026-3407-8
ER  -

APA

Han, F., Gao, P., Zhou, Y., Cui, T., Xu, Y., Fang, X., Shen, M., Dong, S., Zhong, Y., Wang, Y., Bu, L., Chen, L., Xia, Y., Yao, R., Bao, N., Xue, B., Tao, Y., Ge, J., Ju, Z., Zhu, Y., Guan, Y., Zuo, C., Sun, X., Ding, S., Cao, G., Wang, X., Feng, L., Mao, H., Lv, H., Zhao, X., Li, W., Wang, J., & Song, Y. (2026). Intraputaminal AAV9 co-delivery of AADC and GDNF in severe AADC deficiency: first-in-human pediatric dose-escalation study. Science China Life Sciences. https://doi.org/10.1007/s11427-026-3407-8

Source records

crossref · retrieved 2026-09-25T06:07:12.442Z