Impact of Enzyme Replacement Therapy on Patients with Late Onset Pompe Disease – Real World Data from a Developing Country

Swasti Pal, Sunita Bijarnia-Mahay, Sheela Nampoothiri, Mamta Muranjan, Neerja Gupta, Sankar VH, Sujatha Jagadeesh, Meenakshi Bhat, Sanjeeva GN, Dhanya Yesodharan, Prerana Modani, Madhulika Kabra, Priya S. Kishnani, Ratna Dua Puri

Open source

DOI
10.1007/s12098-026-06205-w
Published
2026-07-06
Container
Indian Journal of Pediatrics
Publisher
Springer Science and Business Media LLC
Open access
unknown

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BibTeX

@article{allodium:10.1007/s12098-026-06205-w,
  title = {Impact of Enzyme Replacement Therapy on Patients with Late Onset Pompe Disease – Real World Data from a Developing Country},
  author = {Swasti Pal and Sunita Bijarnia-Mahay and Sheela Nampoothiri and Mamta Muranjan and Neerja Gupta and Sankar VH and Sujatha Jagadeesh and Meenakshi Bhat and Sanjeeva GN and Dhanya Yesodharan and Prerana Modani and Madhulika Kabra and Priya S. Kishnani and Ratna Dua Puri},
  year = {2026},
  journal = {Indian Journal of Pediatrics},
  doi = {10.1007/s12098-026-06205-w},
  url = {https://doi.org/10.1007/s12098-026-06205-w}
}

RIS

TY  - JOUR
TI  - Impact of Enzyme Replacement Therapy on Patients with Late Onset Pompe Disease – Real World Data from a Developing Country
AU  - Swasti Pal
AU  - Sunita Bijarnia-Mahay
AU  - Sheela Nampoothiri
AU  - Mamta Muranjan
AU  - Neerja Gupta
AU  - Sankar VH
AU  - Sujatha Jagadeesh
AU  - Meenakshi Bhat
AU  - Sanjeeva GN
AU  - Dhanya Yesodharan
AU  - Prerana Modani
AU  - Madhulika Kabra
AU  - Priya S. Kishnani
AU  - Ratna Dua Puri
PY  - 2026
JO  - Indian Journal of Pediatrics
DO  - 10.1007/s12098-026-06205-w
UR  - https://doi.org/10.1007/s12098-026-06205-w
ER  - 

APA

Pal, S., Bijarnia-Mahay, S., Nampoothiri, S., Muranjan, M., Gupta, N., VH, S., Jagadeesh, S., Bhat, M., GN, S., Yesodharan, D., Modani, P., Kabra, M., Kishnani, P. S., & Puri, R. D. (2026). Impact of Enzyme Replacement Therapy on Patients with Late Onset Pompe Disease – Real World Data from a Developing Country. Indian Journal of Pediatrics. https://doi.org/10.1007/s12098-026-06205-w

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