Home Infusion With Recombinant Human α-Glucosidase in Children With Pompe Disease: The Dutch Experience Over 20 Years Across the Spectrum From Classic Infantile to Late-Onset Phenotypes.
- DOI
- 10.1007/s40259-026-00773-1
- Published
- 2026 Sep
- Container
- BioDrugs : clinical immunotherapeutics, biopharmaceuticals and gene therapy
- Publisher
- Not recorded
- Open access
- yes
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Cite this work
BibTeX
@article{allodium:10.1007/s40259-026-00773-1,
title = {Home Infusion With Recombinant Human α-Glucosidase in Children With Pompe Disease: The Dutch Experience Over 20 Years Across the Spectrum From Classic Infantile to Late-Onset Phenotypes.},
author = {Ditters IAM and Huidekoper HH and Hardon JF and Kruijshaar ME and van der Ploeg AT and van den Hout JMP},
year = {2026},
journal = {BioDrugs : clinical immunotherapeutics, biopharmaceuticals and gene therapy},
doi = {10.1007/s40259-026-00773-1},
url = {https://doi.org/10.1007/s40259-026-00773-1}
}RIS
TY - JOUR TI - Home Infusion With Recombinant Human α-Glucosidase in Children With Pompe Disease: The Dutch Experience Over 20 Years Across the Spectrum From Classic Infantile to Late-Onset Phenotypes. AU - Ditters IAM AU - Huidekoper HH AU - Hardon JF AU - Kruijshaar ME AU - van der Ploeg AT AU - van den Hout JMP PY - 2026 JO - BioDrugs : clinical immunotherapeutics, biopharmaceuticals and gene therapy DO - 10.1007/s40259-026-00773-1 UR - https://doi.org/10.1007/s40259-026-00773-1 ER -
APA
IAM, D., HH, H., JF, H., ME, K., AT, V. D. P., & JMP, V. D. H. (2026). Home Infusion With Recombinant Human α-Glucosidase in Children With Pompe Disease: The Dutch Experience Over 20 Years Across the Spectrum From Classic Infantile to Late-Onset Phenotypes.. BioDrugs : clinical immunotherapeutics, biopharmaceuticals and gene therapy. https://doi.org/10.1007/s40259-026-00773-1
Source records
- pubmed · retrieved 2026-09-26T00:32:40.932Z