Bridging the translational gap in drug repurposing for rare diseases: clinical success versus regulatory conversion

Wael Khazen, Arnaud Valent, Samantha Parker, Solange Corriol-Rohou, Teresinha Evangelista, Xavier Nissan, Alexandre Mejat

Open source

DOI
10.1016/j.drudis.2026.104807
Published
2026-09
Container
Drug Discovery Today
Publisher
Elsevier BV
Open access
unknown

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BibTeX

@article{allodium:10.1016/j.drudis.2026.104807,
  title = {Bridging the translational gap in drug repurposing for rare diseases: clinical success versus regulatory conversion},
  author = {Wael Khazen and Arnaud Valent and Samantha Parker and Solange Corriol-Rohou and Teresinha Evangelista and Xavier Nissan and Alexandre Mejat},
  year = {2026},
  journal = {Drug Discovery Today},
  doi = {10.1016/j.drudis.2026.104807},
  url = {https://doi.org/10.1016/j.drudis.2026.104807}
}

RIS

TY  - JOUR
TI  - Bridging the translational gap in drug repurposing for rare diseases: clinical success versus regulatory conversion
AU  - Wael Khazen
AU  - Arnaud Valent
AU  - Samantha Parker
AU  - Solange Corriol-Rohou
AU  - Teresinha Evangelista
AU  - Xavier Nissan
AU  - Alexandre Mejat
PY  - 2026
JO  - Drug Discovery Today
DO  - 10.1016/j.drudis.2026.104807
UR  - https://doi.org/10.1016/j.drudis.2026.104807
ER  - 

APA

Khazen, W., Valent, A., Parker, S., Corriol-Rohou, S., Evangelista, T., Nissan, X., & Mejat, A. (2026). Bridging the translational gap in drug repurposing for rare diseases: clinical success versus regulatory conversion. Drug Discovery Today. https://doi.org/10.1016/j.drudis.2026.104807

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