Real-world use of complement inhibitors for haemolytic uraemic syndrome: an analysis of the European Rare Kidney Disease Registry cohort

Aleksandra Vujović, Anne-Laure Sellier-Leclerc, Maria Cristina Mancuso, Olivia Boyer, Atif Awan, Antonio Gargiulo, Sebastian Loos, Marc Fila, Augustina Jankauskiene, Gema Ariceta, Nele Kanzelmeyer, Enrico Vidal, Maria Van Dyck, Tanja Kersnik Levart, Naděžda Šimánková, Stephane Decramer, Jonas Hofstetter, Marina Vivarelli, Savino Sciascia, Nicole C.A.J. van de Kar, Franz Schaefer, Nicole C.A.J. van de Kar, Marina Vivarelli, Savino Sciascia, David Kavanagh, René Andersen, Mia Faerch, Soren Rittig, Miquel Blasco, Pedro Arango Sancho, Alvaro Madrid, Gema Ariceta, Loreto Gesualdo, Camillo Carrara, Piero Ruggenenti, Kai-Uwe Eckardt, Jan Halbritter, Dominik Müller, Adrian Schreiber, Evelyn Seelow, Yahsou Delmas, Jerome Harambat, Brigitte Llanas, Nathalie Godefroid, Eric Goffin, Johann Morelle, Adrian Catalin Lungu, George Reusz, Péter Sallay, Attila Szabo, Kalman Tory, Jan Ulrich Becker, Kathrin Burgmaier, Volker Burst, Sandra Habbig, Max Liebau, Roman-Ulrich Mueller, Lutz Weber, Mette Damholt, Anne-Lise Kamper, Karl Emil Nelveg-Kristensen, Hanne Nørgaard, Ida Maria Schmidt, Soeren Soerensen, Wladimir Szpirt, Agnieszka Jaskólska, Monika Miklaszewska, Anna Moczulska, Elżbieta Szczęsny-Choruz, Katarzyna Zachwieja, Peter Conlon, Atif Awan, Michael Wiesener, Anja Büscher, Rainer Büscher, Lars Pape, Francesca Becherucci, Paola Romagnani, Ann Raes, Thomas Renson, Evelien Snauwaert, Johan Vande Walle, Jill Vanmassenhove, Mark Eijgelsheim, Casper Franssen, Coen Stegeman, Florian Grahammer, Thomas Henne, Tobias Huber, Christian Krebs, Sebastian Loos, Anne Mühlig, Jun Oh, Ulf Panzer, Raphael Schild, Jessica Kaufeld, Stefanie Haeberle, Franz Schaefer, Tanja Wlodkowski, Juuso Tainio, Elisa Ylinen, Obbo Bredewold, Wieneke Michels, Dorien Peters, Antonius Rabelink, Arghya Ray, Joris Rotmans, Siebe Spijker, Y.K. Onno Teng, Kathleen Claes, Noel Knops, Tanja Kersnik Levart, Anamarija Meglič, Gregor Novljan, Agnieszka Gach, Monika Pawlak-Bratkowska, Małgorzata Stańczyk, Marcin Tkaczyk, Pierre Cochat, Anne-Laure Sellier-Leclerc, Teresa Cavero, Eduardo Guiterrez, Joaquin Martinez, Enrique Morales, Hernando Trujillo, Gianluigi Ardissino, Valentina Capone, Sara Testa, Denis Morin, Martin Konrad, Ilaria Luongo, Gabriele Malgieri, Luigi Annicchiarico Petruzzelli, Wilbert van der Meijden, Jack Wetzels, Mattia Parolin, Enrico Vidal, Thérésa Kwon, Olivia Boyer, Aude Servais, Laurent Mesnard, Alena Parikova, Silvie Rajnochova-Bloudickova, Janka Slatinska, Ondrej Viklicky, Martin Bezdicka, Nadezda Simankova, Dana Thomasova, Jakub Zieg, Francesco Emma, Rocco Baccaro, Giuseppe Grandaliano, Alessandro Naticchia, Francesco Pesce, Margherita Baldassarri, Andrea Guarnieri, Anna Maria Pinto, Alessandra Renieri, Stephane Decramer, Stanislas Faguer, David Ribes, Thomas Simon, Stephanie Tellier, Daniel Gale, Christoph Licht, Michal Malina, Candice Roufosse, Neil Sheerin, Susana Carvajal Arjona, Renée de Wildt, Uwe Korst, Christiane Mockenhaupt, Francisco Monfort, Mireya Vicenta Rios Carratala

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DOI
10.1016/j.eclinm.2025.103159
Published
2025-04
Container
eClinicalMedicine
Publisher
Elsevier BV
Open access
unknown

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BibTeX

@article{allodium:10.1016/j.eclinm.2025.103159,
  title = {Real-world use of complement inhibitors for haemolytic uraemic syndrome: an analysis of the European Rare Kidney Disease Registry cohort},
  author = {Aleksandra Vujović and Anne-Laure Sellier-Leclerc and Maria Cristina Mancuso and Olivia Boyer and Atif Awan and Antonio Gargiulo and Sebastian Loos and Marc Fila and Augustina Jankauskiene and Gema Ariceta and Nele Kanzelmeyer and Enrico Vidal and Maria Van Dyck and Tanja Kersnik Levart and Naděžda Šimánková and Stephane Decramer and Jonas Hofstetter and Marina Vivarelli and Savino Sciascia and Nicole C.A.J. van de Kar and Franz Schaefer and Nicole C.A.J. van de Kar and Marina Vivarelli and Savino Sciascia and David Kavanagh and René Andersen and Mia Faerch and Soren Rittig and Miquel Blasco and Pedro Arango Sancho and Alvaro Madrid and Gema Ariceta and Loreto Gesualdo and Camillo Carrara and Piero Ruggenenti and Kai-Uwe Eckardt and Jan Halbritter and Dominik Müller and Adrian Schreiber and Evelyn Seelow and Yahsou Delmas and Jerome Harambat and Brigitte Llanas and Nathalie Godefroid and Eric Goffin and Johann Morelle and Adrian Catalin Lungu and George Reusz and Péter Sallay and Attila Szabo and Kalman Tory and Jan Ulrich Becker and Kathrin Burgmaier and Volker Burst and Sandra Habbig and Max Liebau and Roman-Ulrich Mueller and Lutz Weber and Mette Damholt and Anne-Lise Kamper and Karl Emil Nelveg-Kristensen and Hanne Nørgaard and Ida Maria Schmidt and Soeren Soerensen and Wladimir Szpirt and Agnieszka Jaskólska and Monika Miklaszewska and Anna Moczulska and Elżbieta Szczęsny-Choruz and Katarzyna Zachwieja and Peter Conlon and Atif Awan and Michael Wiesener and Anja Büscher and Rainer Büscher and Lars Pape and Francesca Becherucci and Paola Romagnani and Ann Raes and Thomas Renson and Evelien Snauwaert and Johan Vande Walle and Jill Vanmassenhove and Mark Eijgelsheim and Casper Franssen and Coen Stegeman and Florian Grahammer and Thomas Henne and Tobias Huber and Christian Krebs and Sebastian Loos and Anne Mühlig and Jun Oh and Ulf Panzer and Raphael Schild and Jessica Kaufeld and Stefanie Haeberle and Franz Schaefer and Tanja Wlodkowski and Juuso Tainio and Elisa Ylinen and Obbo Bredewold and Wieneke Michels and Dorien Peters and Antonius Rabelink and Arghya Ray and Joris Rotmans and Siebe Spijker and Y.K. Onno Teng and Kathleen Claes and Noel Knops and Tanja Kersnik Levart and Anamarija Meglič and Gregor Novljan and Agnieszka Gach and Monika Pawlak-Bratkowska and Małgorzata Stańczyk and Marcin Tkaczyk and Pierre Cochat and Anne-Laure Sellier-Leclerc and Teresa Cavero and Eduardo Guiterrez and Joaquin Martinez and Enrique Morales and Hernando Trujillo and Gianluigi Ardissino and Valentina Capone and Sara Testa and Denis Morin and Martin Konrad and Ilaria Luongo and Gabriele Malgieri and Luigi Annicchiarico Petruzzelli and Wilbert van der Meijden and Jack Wetzels and Mattia Parolin and Enrico Vidal and Thérésa Kwon and Olivia Boyer and Aude Servais and Laurent Mesnard and Alena Parikova and Silvie Rajnochova-Bloudickova and Janka Slatinska and Ondrej Viklicky and Martin Bezdicka and Nadezda Simankova and Dana Thomasova and Jakub Zieg and Francesco Emma and Rocco Baccaro and Giuseppe Grandaliano and Alessandro Naticchia and Francesco Pesce and Margherita Baldassarri and Andrea Guarnieri and Anna Maria Pinto and Alessandra Renieri and Stephane Decramer and Stanislas Faguer and David Ribes and Thomas Simon and Stephanie Tellier and Daniel Gale and Christoph Licht and Michal Malina and Candice Roufosse and Neil Sheerin and Susana Carvajal Arjona and Renée de Wildt and Uwe Korst and Christiane Mockenhaupt and Francisco Monfort and Mireya Vicenta Rios Carratala},
  year = {2025},
  journal = {eClinicalMedicine},
  doi = {10.1016/j.eclinm.2025.103159},
  url = {https://doi.org/10.1016/j.eclinm.2025.103159}
}

RIS

TY  - JOUR
TI  - Real-world use of complement inhibitors for haemolytic uraemic syndrome: an analysis of the European Rare Kidney Disease Registry cohort
AU  - Aleksandra Vujović
AU  - Anne-Laure Sellier-Leclerc
AU  - Maria Cristina Mancuso
AU  - Olivia Boyer
AU  - Atif Awan
AU  - Antonio Gargiulo
AU  - Sebastian Loos
AU  - Marc Fila
AU  - Augustina Jankauskiene
AU  - Gema Ariceta
AU  - Nele Kanzelmeyer
AU  - Enrico Vidal
AU  - Maria Van Dyck
AU  - Tanja Kersnik Levart
AU  - Naděžda Šimánková
AU  - Stephane Decramer
AU  - Jonas Hofstetter
AU  - Marina Vivarelli
AU  - Savino Sciascia
AU  - Nicole C.A.J. van de Kar
AU  - Franz Schaefer
AU  - Nicole C.A.J. van de Kar
AU  - Marina Vivarelli
AU  - Savino Sciascia
AU  - David Kavanagh
AU  - René Andersen
AU  - Mia Faerch
AU  - Soren Rittig
AU  - Miquel Blasco
AU  - Pedro Arango Sancho
AU  - Alvaro Madrid
AU  - Gema Ariceta
AU  - Loreto Gesualdo
AU  - Camillo Carrara
AU  - Piero Ruggenenti
AU  - Kai-Uwe Eckardt
AU  - Jan Halbritter
AU  - Dominik Müller
AU  - Adrian Schreiber
AU  - Evelyn Seelow
AU  - Yahsou Delmas
AU  - Jerome Harambat
AU  - Brigitte Llanas
AU  - Nathalie Godefroid
AU  - Eric Goffin
AU  - Johann Morelle
AU  - Adrian Catalin Lungu
AU  - George Reusz
AU  - Péter Sallay
AU  - Attila Szabo
AU  - Kalman Tory
AU  - Jan Ulrich Becker
AU  - Kathrin Burgmaier
AU  - Volker Burst
AU  - Sandra Habbig
AU  - Max Liebau
AU  - Roman-Ulrich Mueller
AU  - Lutz Weber
AU  - Mette Damholt
AU  - Anne-Lise Kamper
AU  - Karl Emil Nelveg-Kristensen
AU  - Hanne Nørgaard
AU  - Ida Maria Schmidt
AU  - Soeren Soerensen
AU  - Wladimir Szpirt
AU  - Agnieszka Jaskólska
AU  - Monika Miklaszewska
AU  - Anna Moczulska
AU  - Elżbieta Szczęsny-Choruz
AU  - Katarzyna Zachwieja
AU  - Peter Conlon
AU  - Atif Awan
AU  - Michael Wiesener
AU  - Anja Büscher
AU  - Rainer Büscher
AU  - Lars Pape
AU  - Francesca Becherucci
AU  - Paola Romagnani
AU  - Ann Raes
AU  - Thomas Renson
AU  - Evelien Snauwaert
AU  - Johan Vande Walle
AU  - Jill Vanmassenhove
AU  - Mark Eijgelsheim
AU  - Casper Franssen
AU  - Coen Stegeman
AU  - Florian Grahammer
AU  - Thomas Henne
AU  - Tobias Huber
AU  - Christian Krebs
AU  - Sebastian Loos
AU  - Anne Mühlig
AU  - Jun Oh
AU  - Ulf Panzer
AU  - Raphael Schild
AU  - Jessica Kaufeld
AU  - Stefanie Haeberle
AU  - Franz Schaefer
AU  - Tanja Wlodkowski
AU  - Juuso Tainio
AU  - Elisa Ylinen
AU  - Obbo Bredewold
AU  - Wieneke Michels
AU  - Dorien Peters
AU  - Antonius Rabelink
AU  - Arghya Ray
AU  - Joris Rotmans
AU  - Siebe Spijker
AU  - Y.K. Onno Teng
AU  - Kathleen Claes
AU  - Noel Knops
AU  - Tanja Kersnik Levart
AU  - Anamarija Meglič
AU  - Gregor Novljan
AU  - Agnieszka Gach
AU  - Monika Pawlak-Bratkowska
AU  - Małgorzata Stańczyk
AU  - Marcin Tkaczyk
AU  - Pierre Cochat
AU  - Anne-Laure Sellier-Leclerc
AU  - Teresa Cavero
AU  - Eduardo Guiterrez
AU  - Joaquin Martinez
AU  - Enrique Morales
AU  - Hernando Trujillo
AU  - Gianluigi Ardissino
AU  - Valentina Capone
AU  - Sara Testa
AU  - Denis Morin
AU  - Martin Konrad
AU  - Ilaria Luongo
AU  - Gabriele Malgieri
AU  - Luigi Annicchiarico Petruzzelli
AU  - Wilbert van der Meijden
AU  - Jack Wetzels
AU  - Mattia Parolin
AU  - Enrico Vidal
AU  - Thérésa Kwon
AU  - Olivia Boyer
AU  - Aude Servais
AU  - Laurent Mesnard
AU  - Alena Parikova
AU  - Silvie Rajnochova-Bloudickova
AU  - Janka Slatinska
AU  - Ondrej Viklicky
AU  - Martin Bezdicka
AU  - Nadezda Simankova
AU  - Dana Thomasova
AU  - Jakub Zieg
AU  - Francesco Emma
AU  - Rocco Baccaro
AU  - Giuseppe Grandaliano
AU  - Alessandro Naticchia
AU  - Francesco Pesce
AU  - Margherita Baldassarri
AU  - Andrea Guarnieri
AU  - Anna Maria Pinto
AU  - Alessandra Renieri
AU  - Stephane Decramer
AU  - Stanislas Faguer
AU  - David Ribes
AU  - Thomas Simon
AU  - Stephanie Tellier
AU  - Daniel Gale
AU  - Christoph Licht
AU  - Michal Malina
AU  - Candice Roufosse
AU  - Neil Sheerin
AU  - Susana Carvajal Arjona
AU  - Renée de Wildt
AU  - Uwe Korst
AU  - Christiane Mockenhaupt
AU  - Francisco Monfort
AU  - Mireya Vicenta Rios Carratala
PY  - 2025
JO  - eClinicalMedicine
DO  - 10.1016/j.eclinm.2025.103159
UR  - https://doi.org/10.1016/j.eclinm.2025.103159
ER  - 

APA

Vujović, A., Sellier-Leclerc, A., Mancuso, M. C., Boyer, O., Awan, A., Gargiulo, A., Loos, S., Fila, M., Jankauskiene, A., Ariceta, G., Kanzelmeyer, N., Vidal, E., Dyck, M. V., Levart, T. K., Šimánková, N., Decramer, S., Hofstetter, J., Vivarelli, M., Sciascia, S., Kar, N. C. V. D., Schaefer, F., Kar, N. C. V. D., Vivarelli, M., Sciascia, S., Kavanagh, D., Andersen, R., Faerch, M., Rittig, S., Blasco, M., Sancho, P. A., Madrid, A., Ariceta, G., Gesualdo, L., Carrara, C., Ruggenenti, P., Eckardt, K., Halbritter, J., Müller, D., Schreiber, A., Seelow, E., Delmas, Y., Harambat, J., Llanas, B., Godefroid, N., Goffin, E., Morelle, J., Lungu, A. C., Reusz, G., Sallay, P., Szabo, A., Tory, K., Becker, J. U., Burgmaier, K., Burst, V., Habbig, S., Liebau, M., Mueller, R., Weber, L., Damholt, M., Kamper, A., Nelveg-Kristensen, K. E., Nørgaard, H., Schmidt, I. M., Soerensen, S., Szpirt, W., Jaskólska, A., Miklaszewska, M., Moczulska, A., Szczęsny-Choruz, E., Zachwieja, K., Conlon, P., Awan, A., Wiesener, M., Büscher, A., Büscher, R., Pape, L., Becherucci, F., Romagnani, P., Raes, A., Renson, T., Snauwaert, E., Walle, J. V., Vanmassenhove, J., Eijgelsheim, M., Franssen, C., Stegeman, C., Grahammer, F., Henne, T., Huber, T., Krebs, C., Loos, S., Mühlig, A., Oh, J., Panzer, U., Schild, R., Kaufeld, J., Haeberle, S., Schaefer, F., Wlodkowski, T., Tainio, J., Ylinen, E., Bredewold, O., Michels, W., Peters, D., Rabelink, A., Ray, A., Rotmans, J., Spijker, S., Teng, Y. O., Claes, K., Knops, N., Levart, T. K., Meglič, A., Novljan, G., Gach, A., Pawlak-Bratkowska, M., Stańczyk, M., Tkaczyk, M., Cochat, P., Sellier-Leclerc, A., Cavero, T., Guiterrez, E., Martinez, J., Morales, E., Trujillo, H., Ardissino, G., Capone, V., Testa, S., Morin, D., Konrad, M., Luongo, I., Malgieri, G., Petruzzelli, L. A., Meijden, W. V. D., Wetzels, J., Parolin, M., Vidal, E., Kwon, T., Boyer, O., Servais, A., Mesnard, L., Parikova, A., Rajnochova-Bloudickova, S., Slatinska, J., Viklicky, O., Bezdicka, M., Simankova, N., Thomasova, D., Zieg, J., Emma, F., Baccaro, R., Grandaliano, G., Naticchia, A., Pesce, F., Baldassarri, M., Guarnieri, A., Pinto, A. M., Renieri, A., Decramer, S., Faguer, S., Ribes, D., Simon, T., Tellier, S., Gale, D., Licht, C., Malina, M., Roufosse, C., Sheerin, N., Arjona, S. C., Wildt, R. D., Korst, U., Mockenhaupt, C., Monfort, F., & Carratala, M. V. R. (2025). Real-world use of complement inhibitors for haemolytic uraemic syndrome: an analysis of the European Rare Kidney Disease Registry cohort. eClinicalMedicine. https://doi.org/10.1016/j.eclinm.2025.103159

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