Efficacy and safety of risdiplam in adults with 5q-associated spinal muscular atrophy: a nationwide observational cohort study in Austria.

Keritam O, Erdler M, Fasching B, Zulehner G, Rath J, Krenn M, Waldhör T, Gruber VA, Langweil N, Kiss C, Griedl TA, Gold V, Wanschitz J, Hotter A, Kleinveld VEA, Horlings CGC, Erber A, Schernhammer E, Troger J, Grinzinger S, Müller P, Langenscheidt D, Rappold M, Wiesenhofer A, Gosk-Tomek M, Knipp F, Mahal S, Bernert G, Baumann M, Zimprich F, Topakian R, Eggers C, Quasthoff S, Löscher W, Cetin H

Open source

DOI: 10.1016/j.eclinm.2025.103536
Published: 2025 Oct
Container: EClinicalMedicine
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1016/j.eclinm.2025.103536,
  title = {Efficacy and safety of risdiplam in adults with 5q-associated spinal muscular atrophy: a nationwide observational cohort study in Austria.},
  author = {Keritam O and Erdler M and Fasching B and Zulehner G and Rath J and Krenn M and Waldhör T and Gruber VA and Langweil N and Kiss C and Griedl TA and Gold V and Wanschitz J and Hotter A and Kleinveld VEA and Horlings CGC and Erber A and Schernhammer E and Troger J and Grinzinger S and Müller P and Langenscheidt D and Rappold M and Wiesenhofer A and Gosk-Tomek M and Knipp F and Mahal S and Bernert G and Baumann M and Zimprich F and Topakian R and Eggers C and Quasthoff S and Löscher W and Cetin H},
  year = {2025},
  journal = {EClinicalMedicine},
  doi = {10.1016/j.eclinm.2025.103536},
  url = {https://doi.org/10.1016/j.eclinm.2025.103536}
}

RIS

TY  - JOUR
TI  - Efficacy and safety of risdiplam in adults with 5q-associated spinal muscular atrophy: a nationwide observational cohort study in Austria.
AU  - Keritam O
AU  - Erdler M
AU  - Fasching B
AU  - Zulehner G
AU  - Rath J
AU  - Krenn M
AU  - Waldhör T
AU  - Gruber VA
AU  - Langweil N
AU  - Kiss C
AU  - Griedl TA
AU  - Gold V
AU  - Wanschitz J
AU  - Hotter A
AU  - Kleinveld VEA
AU  - Horlings CGC
AU  - Erber A
AU  - Schernhammer E
AU  - Troger J
AU  - Grinzinger S
AU  - Müller P
AU  - Langenscheidt D
AU  - Rappold M
AU  - Wiesenhofer A
AU  - Gosk-Tomek M
AU  - Knipp F
AU  - Mahal S
AU  - Bernert G
AU  - Baumann M
AU  - Zimprich F
AU  - Topakian R
AU  - Eggers C
AU  - Quasthoff S
AU  - Löscher W
AU  - Cetin H
PY  - 2025
JO  - EClinicalMedicine
DO  - 10.1016/j.eclinm.2025.103536
UR  - https://doi.org/10.1016/j.eclinm.2025.103536
ER  -

APA

O, K., M, E., B, F., G, Z., J, R., M, K., T, W., VA, G., N, L., C, K., TA, G., V, G., J, W., A, H., VEA, K., CGC, H., A, E., E, S., J, T., S, G., P, M., D, L., M, R., A, W., M, G., F, K., S, M., G, B., M, B., F, Z., R, T., C, E., S, Q., W, L., & H, C. (2025). Efficacy and safety of risdiplam in adults with 5q-associated spinal muscular atrophy: a nationwide observational cohort study in Austria.. EClinicalMedicine. https://doi.org/10.1016/j.eclinm.2025.103536

Source records

pubmed · retrieved 2026-09-26T05:23:04.670Z