Long-term safety and efficacy of pegunigalsidase alfa: A multicenter 6-year study in adult patients with Fabry disease.
- DOI
- 10.1016/j.gim.2023.100968
- Published
- 2023 Dec
- Container
- Genetics in medicine : official journal of the American College of Medical Genetics
- Publisher
- Not recorded
- Open access
- unknown
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limited evidence Score 43/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.
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Cite this work
BibTeX
@article{allodium:10.1016/j.gim.2023.100968,
title = {Long-term safety and efficacy of pegunigalsidase alfa: A multicenter 6-year study in adult patients with Fabry disease.},
author = {Hughes D and Gonzalez D and Maegawa G and Bernat JA and Holida M and Giraldo P and Atta MG and Chertkoff R and Alon S and Almon EB and Rocco R and Goker-Alpan O},
year = {2023},
journal = {Genetics in medicine : official journal of the American College of Medical Genetics},
doi = {10.1016/j.gim.2023.100968},
url = {https://doi.org/10.1016/j.gim.2023.100968}
}RIS
TY - JOUR TI - Long-term safety and efficacy of pegunigalsidase alfa: A multicenter 6-year study in adult patients with Fabry disease. AU - Hughes D AU - Gonzalez D AU - Maegawa G AU - Bernat JA AU - Holida M AU - Giraldo P AU - Atta MG AU - Chertkoff R AU - Alon S AU - Almon EB AU - Rocco R AU - Goker-Alpan O PY - 2023 JO - Genetics in medicine : official journal of the American College of Medical Genetics DO - 10.1016/j.gim.2023.100968 UR - https://doi.org/10.1016/j.gim.2023.100968 ER -
APA
D, H., D, G., G, M., JA, B., M, H., P, G., MG, A., R, C., S, A., EB, A., R, R., & O, G. (2023). Long-term safety and efficacy of pegunigalsidase alfa: A multicenter 6-year study in adult patients with Fabry disease.. Genetics in medicine : official journal of the American College of Medical Genetics. https://doi.org/10.1016/j.gim.2023.100968
Source records
- pubmed · retrieved 2026-09-26T00:32:39.787Z