A functional comparison of readthrough agent ELX-02 across a wide range of nonsense CFTR variants

Marlies Destoop, Anabela S. Ramalho, Iris A.L. Silva, Annelotte M. Vonk, Sylvia Suen, Marlou C. Bierlaagh, Sylvia F. Boj, Robert G.J. Vries, Jeffrey M. Beekman, Kris De Boeck, Cornelis K. van der Ent, Margarida D. Amaral, Francois Vermeulen, Sacha Spelier

Open source

DOI
10.1016/j.jcf.2026.09.004
Published
2026-09
Container
Journal of Cystic Fibrosis
Publisher
Elsevier BV
Open access
unknown

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BibTeX

@article{allodium:10.1016/j.jcf.2026.09.004,
  title = {A functional comparison of readthrough agent ELX-02 across a wide range of nonsense CFTR variants},
  author = {Marlies Destoop and Anabela S. Ramalho and Iris A.L. Silva and Annelotte M. Vonk and Sylvia Suen and Marlou C. Bierlaagh and Sylvia F. Boj and Robert G.J. Vries and Jeffrey M. Beekman and Kris De Boeck and Cornelis K. van der Ent and Margarida D. Amaral and Francois Vermeulen and Sacha Spelier},
  year = {2026},
  journal = {Journal of Cystic Fibrosis},
  doi = {10.1016/j.jcf.2026.09.004},
  url = {https://doi.org/10.1016/j.jcf.2026.09.004}
}

RIS

TY  - JOUR
TI  - A functional comparison of readthrough agent ELX-02 across a wide range of nonsense CFTR variants
AU  - Marlies Destoop
AU  - Anabela S. Ramalho
AU  - Iris A.L. Silva
AU  - Annelotte M. Vonk
AU  - Sylvia Suen
AU  - Marlou C. Bierlaagh
AU  - Sylvia F. Boj
AU  - Robert G.J. Vries
AU  - Jeffrey M. Beekman
AU  - Kris De Boeck
AU  - Cornelis K. van der Ent
AU  - Margarida D. Amaral
AU  - Francois Vermeulen
AU  - Sacha Spelier
PY  - 2026
JO  - Journal of Cystic Fibrosis
DO  - 10.1016/j.jcf.2026.09.004
UR  - https://doi.org/10.1016/j.jcf.2026.09.004
ER  - 

APA

Destoop, M., Ramalho, A. S., Silva, I. A., Vonk, A. M., Suen, S., Bierlaagh, M. C., Boj, S. F., Vries, R. G., Beekman, J. M., Boeck, K. D., Ent, C. K. V. D., Amaral, M. D., Vermeulen, F., & Spelier, S. (2026). A functional comparison of readthrough agent ELX-02 across a wide range of nonsense CFTR variants. Journal of Cystic Fibrosis. https://doi.org/10.1016/j.jcf.2026.09.004

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