Gene therapy benefits in a small cohort of symptomatic 5q spinal muscular atrophy patients and real world pediatric outcomes
- DOI
- 10.1016/j.jped.2026.101597
- Published
- 2026-11
- Container
- Jornal de Pediatria
- Publisher
- Elsevier BV
- Open access
- unknown
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Cite this work
BibTeX
@article{allodium:10.1016/j.jped.2026.101597,
title = {Gene therapy benefits in a small cohort of symptomatic 5q spinal muscular atrophy patients and real world pediatric outcomes},
author = {Andresa R.B.V. Santos and Lisiane S. Ferreira and Tamires S. Santos and Juliana F. Mazzeu and Ney C.A. Boa Sorte},
year = {2026},
journal = {Jornal de Pediatria},
doi = {10.1016/j.jped.2026.101597},
url = {https://doi.org/10.1016/j.jped.2026.101597}
}RIS
TY - JOUR TI - Gene therapy benefits in a small cohort of symptomatic 5q spinal muscular atrophy patients and real world pediatric outcomes AU - Andresa R.B.V. Santos AU - Lisiane S. Ferreira AU - Tamires S. Santos AU - Juliana F. Mazzeu AU - Ney C.A. Boa Sorte PY - 2026 JO - Jornal de Pediatria DO - 10.1016/j.jped.2026.101597 UR - https://doi.org/10.1016/j.jped.2026.101597 ER -
APA
Santos, A. R., Ferreira, L. S., Santos, T. S., Mazzeu, J. F., & Sorte, N. C. B. (2026). Gene therapy benefits in a small cohort of symptomatic 5q spinal muscular atrophy patients and real world pediatric outcomes. Jornal de Pediatria. https://doi.org/10.1016/j.jped.2026.101597
Source records
- crossref · retrieved 2026-09-25T19:30:50.384Z