N-of-1 investigational study of a novel antisense oligonucleotide drug in CHCHD10-related ALS shows early signs of efficacy
- DOI
- 10.1016/j.medj.2026.101295
- Published
- 2026-09
- Container
- Med
- Publisher
- Elsevier BV
- Open access
- unknown
Credibility signals
uncertain Score 64/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.
Show all credibility signals
- supportingDOI registered: A matching record was returned by Crossref.
- supportingDOI resolves: A matching record was returned by Crossref.
- not scoredDirectory of Open Access Journals: No matching DOAJ record was present in this response. No allow-list match; this is not evidence of low credibility.
- not scoredMEDLINE indexed: Not checked or no result supplied; no credibility inference made.
- not scoredOpenAlex core source: Not checked or no result supplied; no credibility inference made.
- not scoredKnown publisher allow-list: Not checked or no result supplied; no credibility inference made.
- not scoredROR affiliation: Not checked or no result supplied; no credibility inference made.
- not scoredRetraction Watch retraction: No retraction notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch expression of concern: No expression of concern notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch correction: No correction notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch reinstatement: No reinstatement notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredOpen access status: Not checked or no result supplied; no credibility inference made.
- not scoredPublication license: Not checked or no result supplied; no credibility inference made.
- not scoredPublication version: A publication version was supplied but is not scored.
- supportingMetadata completeness: All 6 scored descriptive metadata groups are present.
Cite this work
BibTeX
@article{allodium:10.1016/j.medj.2026.101295,
title = {N-of-1 investigational study of a novel antisense oligonucleotide drug in CHCHD10-related ALS shows early signs of efficacy},
author = {Margot A. Cousin and Aditi I. Dagli and Laurence Mignon and Jaimin S. Shah and Mercedes Prudencio and Tania F. Gendron and Angita Jain and Evan Udine and Marka van Blitterswijk and Erik H. Middlebrooks and Megan H. Donahue and Jany E. Dagher and Jens O. Watzlawik and Wolfdieter Springer and Tejal Parekh and Zachary T. McEachin and Leonard Petrucelli and Björn Oskarsson},
year = {2026},
journal = {Med},
doi = {10.1016/j.medj.2026.101295},
url = {https://doi.org/10.1016/j.medj.2026.101295}
}RIS
TY - JOUR TI - N-of-1 investigational study of a novel antisense oligonucleotide drug in CHCHD10-related ALS shows early signs of efficacy AU - Margot A. Cousin AU - Aditi I. Dagli AU - Laurence Mignon AU - Jaimin S. Shah AU - Mercedes Prudencio AU - Tania F. Gendron AU - Angita Jain AU - Evan Udine AU - Marka van Blitterswijk AU - Erik H. Middlebrooks AU - Megan H. Donahue AU - Jany E. Dagher AU - Jens O. Watzlawik AU - Wolfdieter Springer AU - Tejal Parekh AU - Zachary T. McEachin AU - Leonard Petrucelli AU - Björn Oskarsson PY - 2026 JO - Med DO - 10.1016/j.medj.2026.101295 UR - https://doi.org/10.1016/j.medj.2026.101295 ER -
APA
Cousin, M. A., Dagli, A. I., Mignon, L., Shah, J. S., Prudencio, M., Gendron, T. F., Jain, A., Udine, E., Blitterswijk, M. V., Middlebrooks, E. H., Donahue, M. H., Dagher, J. E., Watzlawik, J. O., Springer, W., Parekh, T., McEachin, Z. T., Petrucelli, L., & Oskarsson, B. (2026). N-of-1 investigational study of a novel antisense oligonucleotide drug in CHCHD10-related ALS shows early signs of efficacy. Med. https://doi.org/10.1016/j.medj.2026.101295
Source records
- crossref · retrieved 2026-09-25T21:46:23.271Z