Genetic susceptibility to thrombotic microangiopathy in a 10-month-old patient with SMA type 1: a caveat for gene therapy eligibility.
- DOI
- 10.1016/j.nmd.2026.107376
- Published
- 2026 Sep
- Container
- Neuromuscular disorders : NMD
- Publisher
- Not recorded
- Open access
- no
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Cite this work
BibTeX
@article{allodium:10.1016/j.nmd.2026.107376,
title = {Genetic susceptibility to thrombotic microangiopathy in a 10-month-old patient with SMA type 1: a caveat for gene therapy eligibility.},
author = {D'Alessandro R and Somà A and Vacchetti M and Salvalaggio A and Guarnone E and Cavallina I and Rolle E and Rossi F and Montin D and Saglio F and Peruzzi L and Barberis M and Sbaiz L and Deaglio S and Fagioli F and Mongini TE and Ricci FS},
year = {2026},
journal = {Neuromuscular disorders : NMD},
doi = {10.1016/j.nmd.2026.107376},
url = {https://doi.org/10.1016/j.nmd.2026.107376}
}RIS
TY - JOUR TI - Genetic susceptibility to thrombotic microangiopathy in a 10-month-old patient with SMA type 1: a caveat for gene therapy eligibility. AU - D'Alessandro R AU - Somà A AU - Vacchetti M AU - Salvalaggio A AU - Guarnone E AU - Cavallina I AU - Rolle E AU - Rossi F AU - Montin D AU - Saglio F AU - Peruzzi L AU - Barberis M AU - Sbaiz L AU - Deaglio S AU - Fagioli F AU - Mongini TE AU - Ricci FS PY - 2026 JO - Neuromuscular disorders : NMD DO - 10.1016/j.nmd.2026.107376 UR - https://doi.org/10.1016/j.nmd.2026.107376 ER -
APA
R, D., A, S., M, V., A, S., E, G., I, C., E, R., F, R., D, M., F, S., L, P., M, B., L, S., S, D., F, F., TE, M., & FS, R. (2026). Genetic susceptibility to thrombotic microangiopathy in a 10-month-old patient with SMA type 1: a caveat for gene therapy eligibility.. Neuromuscular disorders : NMD. https://doi.org/10.1016/j.nmd.2026.107376
Source records
- pubmed · retrieved 2026-09-25T13:46:27.080Z
- europe-pmc · retrieved 2026-09-25T13:46:27.095Z