Outcome strategies for clinical trials in Neuropaediatric rare diseases.

Acosta MT, Aibar JÁ, Arango C, Cirauqui EA, Baeza C, Berry-Kravis E, Bishop KI, Busner J, Chapman C, Chaumette B, Del Cerro I, Diaz JC, Dorffner G, Edgar CJ, Giorgi S, Hölter SM, Kittel-Schneider S, Latzman RD, Moreno C, Pallanti S, Colzi C, Plasencia C, Radtke F, Rockwood K, Santuccione Chadha A, Sevinc G, Singh MK, Smith SH, Tandon PK, Tinoco D, Broggi E, Morgan SF, Magaraggia I, Zaragoza Domingo S

Open source

DOI: 10.1016/j.nsa.2026.107021
Published: 2026
Container: Neuroscience applied
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1016/j.nsa.2026.107021,
  title = {Outcome strategies for clinical trials in Neuropaediatric rare diseases.},
  author = {Acosta MT and Aibar JÁ and Arango C and Cirauqui EA and Baeza C and Berry-Kravis E and Bishop KI and Busner J and Chapman C and Chaumette B and Del Cerro I and Diaz JC and Dorffner G and Edgar CJ and Giorgi S and Hölter SM and Kittel-Schneider S and Latzman RD and Moreno C and Pallanti S and Colzi C and Plasencia C and Radtke F and Rockwood K and Santuccione Chadha A and Sevinc G and Singh MK and Smith SH and Tandon PK and Tinoco D and Broggi E and Morgan SF and Magaraggia I and Zaragoza Domingo S},
  year = {2026},
  journal = {Neuroscience applied},
  doi = {10.1016/j.nsa.2026.107021},
  url = {https://doi.org/10.1016/j.nsa.2026.107021}
}

RIS

TY  - JOUR
TI  - Outcome strategies for clinical trials in Neuropaediatric rare diseases.
AU  - Acosta MT
AU  - Aibar JÁ
AU  - Arango C
AU  - Cirauqui EA
AU  - Baeza C
AU  - Berry-Kravis E
AU  - Bishop KI
AU  - Busner J
AU  - Chapman C
AU  - Chaumette B
AU  - Del Cerro I
AU  - Diaz JC
AU  - Dorffner G
AU  - Edgar CJ
AU  - Giorgi S
AU  - Hölter SM
AU  - Kittel-Schneider S
AU  - Latzman RD
AU  - Moreno C
AU  - Pallanti S
AU  - Colzi C
AU  - Plasencia C
AU  - Radtke F
AU  - Rockwood K
AU  - Santuccione Chadha A
AU  - Sevinc G
AU  - Singh MK
AU  - Smith SH
AU  - Tandon PK
AU  - Tinoco D
AU  - Broggi E
AU  - Morgan SF
AU  - Magaraggia I
AU  - Zaragoza Domingo S
PY  - 2026
JO  - Neuroscience applied
DO  - 10.1016/j.nsa.2026.107021
UR  - https://doi.org/10.1016/j.nsa.2026.107021
ER  -

APA

MT, A., JÁ, A., C, A., EA, C., C, B., E, B., KI, B., J, B., C, C., B, C., I, D. C., JC, D., G, D., CJ, E., S, G., SM, H., S, K., RD, L., C, M., S, P., C, C., C, P., F, R., K, R., A, S. C., G, S., MK, S., SH, S., PK, T., D, T., E, B., SF, M., I, M., & S, Z. D. (2026). Outcome strategies for clinical trials in Neuropaediatric rare diseases.. Neuroscience applied. https://doi.org/10.1016/j.nsa.2026.107021

Source records

pubmed · retrieved 2026-09-25T11:56:16.984Z