Base editing rescues a hereditary motor neuron disease in mouse and patient-derived iPSC organoid models

Keiko Imamura, Shin Yoshioka, Kota Kamizato, Ryosuke Oki, Hiroyuki Hioki, Kayoko Tsukita, Ikuyo Inoue, Rina Shimizu, Mako Takiguchi, Tomoki Sakasai, Aya Okusa, Ran Shibukawa, Takeshi Niki, Satoko Sakurai, Taro Okunomiya, Takayuki Kondo, Tomohisa Kato, Atsushi Miyanohara, Manabu Kakinohana, Takuya Yamamoto, Martin Marsala, Keiji Nishida, Yuishin Izumi, Haruhisa Inoue

Open source

DOI: 10.1016/j.omta.2026.201835
Published: 2026-12
Container: Molecular Therapy Advances
Publisher: Elsevier BV
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.1016/j.omta.2026.201835,
  title = {Base editing rescues a hereditary motor neuron disease in mouse and patient-derived iPSC organoid models},
  author = {Keiko Imamura and Shin Yoshioka and Kota Kamizato and Ryosuke Oki and Hiroyuki Hioki and Kayoko Tsukita and Ikuyo Inoue and Rina Shimizu and Mako Takiguchi and Tomoki Sakasai and Aya Okusa and Ran Shibukawa and Takeshi Niki and Satoko Sakurai and Taro Okunomiya and Takayuki Kondo and Tomohisa Kato and Atsushi Miyanohara and Manabu Kakinohana and Takuya Yamamoto and Martin Marsala and Keiji Nishida and Yuishin Izumi and Haruhisa Inoue},
  year = {2026},
  journal = {Molecular Therapy Advances},
  doi = {10.1016/j.omta.2026.201835},
  url = {https://doi.org/10.1016/j.omta.2026.201835}
}

RIS

TY  - JOUR
TI  - Base editing rescues a hereditary motor neuron disease in mouse and patient-derived iPSC organoid models
AU  - Keiko Imamura
AU  - Shin Yoshioka
AU  - Kota Kamizato
AU  - Ryosuke Oki
AU  - Hiroyuki Hioki
AU  - Kayoko Tsukita
AU  - Ikuyo Inoue
AU  - Rina Shimizu
AU  - Mako Takiguchi
AU  - Tomoki Sakasai
AU  - Aya Okusa
AU  - Ran Shibukawa
AU  - Takeshi Niki
AU  - Satoko Sakurai
AU  - Taro Okunomiya
AU  - Takayuki Kondo
AU  - Tomohisa Kato
AU  - Atsushi Miyanohara
AU  - Manabu Kakinohana
AU  - Takuya Yamamoto
AU  - Martin Marsala
AU  - Keiji Nishida
AU  - Yuishin Izumi
AU  - Haruhisa Inoue
PY  - 2026
JO  - Molecular Therapy Advances
DO  - 10.1016/j.omta.2026.201835
UR  - https://doi.org/10.1016/j.omta.2026.201835
ER  -

APA

Imamura, K., Yoshioka, S., Kamizato, K., Oki, R., Hioki, H., Tsukita, K., Inoue, I., Shimizu, R., Takiguchi, M., Sakasai, T., Okusa, A., Shibukawa, R., Niki, T., Sakurai, S., Okunomiya, T., Kondo, T., Kato, T., Miyanohara, A., Kakinohana, M., Yamamoto, T., Marsala, M., Nishida, K., Izumi, Y., & Inoue, H. (2026). Base editing rescues a hereditary motor neuron disease in mouse and patient-derived iPSC organoid models. Molecular Therapy Advances. https://doi.org/10.1016/j.omta.2026.201835

Source records

crossref · retrieved 2026-09-25T05:27:30.739Z