A novel technology-driven enzyme replacement therapy for Pompe disease.

Meena NK, Gray K, Roberts J, DiGruccio M, Weaver V, Liu L, Do H, Gotschall RR, Raben N

Open source

DOI
10.1016/j.omta.2026.201867
Published
2026 Dec 10
Container
Molecular therapy. Advances
Publisher
Not recorded
Open access
yes

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BibTeX

@article{allodium:10.1016/j.omta.2026.201867,
  title = {A novel technology-driven enzyme replacement therapy for Pompe disease.},
  author = {Meena NK and Gray K and Roberts J and DiGruccio M and Weaver V and Liu L and Do H and Gotschall RR and Raben N},
  year = {2026},
  journal = {Molecular therapy. Advances},
  doi = {10.1016/j.omta.2026.201867},
  url = {https://doi.org/10.1016/j.omta.2026.201867}
}

RIS

TY  - JOUR
TI  - A novel technology-driven enzyme replacement therapy for Pompe disease.
AU  - Meena NK
AU  - Gray K
AU  - Roberts J
AU  - DiGruccio M
AU  - Weaver V
AU  - Liu L
AU  - Do H
AU  - Gotschall RR
AU  - Raben N
PY  - 2026
JO  - Molecular therapy. Advances
DO  - 10.1016/j.omta.2026.201867
UR  - https://doi.org/10.1016/j.omta.2026.201867
ER  - 

APA

NK, M., K, G., J, R., M, D., V, W., L, L., H, D., RR, G., & N, R. (2026). A novel technology-driven enzyme replacement therapy for Pompe disease.. Molecular therapy. Advances. https://doi.org/10.1016/j.omta.2026.201867

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