Liver-Targeted AAV8 Gene Therapy Ameliorates Skeletal and Cardiovascular Pathology in a Mucopolysaccharidosis IVA Murine Model

Kazuki Sawamoto, Subha Karumuthil-Melethil, Shaukat Khan, Molly Stapleton, Joseph T. Bruder, Olivier Danos, Shunji Tomatsu

Open source

DOI
10.1016/j.omtm.2020.05.015
Published
2020-09
Container
Molecular Therapy - Methods & Clinical Development
Publisher
Elsevier BV
Open access
unknown

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BibTeX

@article{allodium:10.1016/j.omtm.2020.05.015,
  title = {Liver-Targeted AAV8 Gene Therapy Ameliorates Skeletal and Cardiovascular Pathology in a Mucopolysaccharidosis IVA Murine Model},
  author = {Kazuki Sawamoto and Subha Karumuthil-Melethil and Shaukat Khan and Molly Stapleton and Joseph T. Bruder and Olivier Danos and Shunji Tomatsu},
  year = {2020},
  journal = {Molecular Therapy - Methods \& Clinical Development},
  doi = {10.1016/j.omtm.2020.05.015},
  url = {https://doi.org/10.1016/j.omtm.2020.05.015}
}

RIS

TY  - JOUR
TI  - Liver-Targeted AAV8 Gene Therapy Ameliorates Skeletal and Cardiovascular Pathology in a Mucopolysaccharidosis IVA Murine Model
AU  - Kazuki Sawamoto
AU  - Subha Karumuthil-Melethil
AU  - Shaukat Khan
AU  - Molly Stapleton
AU  - Joseph T. Bruder
AU  - Olivier Danos
AU  - Shunji Tomatsu
PY  - 2020
JO  - Molecular Therapy - Methods & Clinical Development
DO  - 10.1016/j.omtm.2020.05.015
UR  - https://doi.org/10.1016/j.omtm.2020.05.015
ER  - 

APA

Sawamoto, K., Karumuthil-Melethil, S., Khan, S., Stapleton, M., Bruder, J. T., Danos, O., & Tomatsu, S. (2020). Liver-Targeted AAV8 Gene Therapy Ameliorates Skeletal and Cardiovascular Pathology in a Mucopolysaccharidosis IVA Murine Model. Molecular Therapy - Methods & Clinical Development. https://doi.org/10.1016/j.omtm.2020.05.015

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