Potential ASO-based personalized treatment for Charcot-Marie-Tooth disease type 2S.

Smieszek S, Przychodzen B, Tyner C, Johnson C, Bai H, Kwon JM, Hagan DW, Niccum C, Brighton R, Hawkins K, Aiken R, Nawaz A, Guo X, Hickman J, Polymeropoulos CM, Birznieks G, Polymeropoulos MH

Open source

DOI: 10.1016/j.omtn.2025.102479
Published: 2025 Mar 11
Container: Molecular therapy. Nucleic acids
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1016/j.omtn.2025.102479,
  title = {Potential ASO-based personalized treatment for Charcot-Marie-Tooth disease type 2S.},
  author = {Smieszek S and Przychodzen B and Tyner C and Johnson C and Bai H and Kwon JM and Hagan DW and Niccum C and Brighton R and Hawkins K and Aiken R and Nawaz A and Guo X and Hickman J and Polymeropoulos CM and Birznieks G and Polymeropoulos MH},
  year = {2025},
  journal = {Molecular therapy. Nucleic acids},
  doi = {10.1016/j.omtn.2025.102479},
  url = {https://doi.org/10.1016/j.omtn.2025.102479}
}

RIS

TY  - JOUR
TI  - Potential ASO-based personalized treatment for Charcot-Marie-Tooth disease type 2S.
AU  - Smieszek S
AU  - Przychodzen B
AU  - Tyner C
AU  - Johnson C
AU  - Bai H
AU  - Kwon JM
AU  - Hagan DW
AU  - Niccum C
AU  - Brighton R
AU  - Hawkins K
AU  - Aiken R
AU  - Nawaz A
AU  - Guo X
AU  - Hickman J
AU  - Polymeropoulos CM
AU  - Birznieks G
AU  - Polymeropoulos MH
PY  - 2025
JO  - Molecular therapy. Nucleic acids
DO  - 10.1016/j.omtn.2025.102479
UR  - https://doi.org/10.1016/j.omtn.2025.102479
ER  -

APA

S, S., B, P., C, T., C, J., H, B., JM, K., DW, H., C, N., R, B., K, H., R, A., A, N., X, G., J, H., CM, P., G, B., & MH, P. (2025). Potential ASO-based personalized treatment for Charcot-Marie-Tooth disease type 2S.. Molecular therapy. Nucleic acids. https://doi.org/10.1016/j.omtn.2025.102479

Source records

pubmed · retrieved 2026-09-27T07:00:51.746Z
europe-pmc · retrieved 2026-09-27T07:00:51.742Z
doaj · retrieved 2026-09-27T07:00:51.759Z