Atrophin-1 antisense oligonucleotide provides robust protection from pathology in a fully humanized DRPLA model

Velvet L. Smith, Bereket Z. Gidi, Robert M. Bragg, Jeffrey P. Cantle, Aliza Ben-Varon, Briana Noble, Silvia Prades, Andrea Compton, Julie Greenfield, Joanna A. Korecka, Anya Gemos, Timothy Yu, Vikram Khurana, Holly B. Kordasiewicz, Hien T. Zhao, Melissa Barker-Haliski, Daniel D. Child, Jeffrey B. Carroll

Open source

DOI
10.1016/j.omtn.2025.102815
Published
2026-03
Container
Molecular Therapy Nucleic Acids
Publisher
Elsevier BV
Open access
unknown

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BibTeX

@article{allodium:10.1016/j.omtn.2025.102815,
  title = {Atrophin-1 antisense oligonucleotide provides robust protection from pathology in a fully humanized DRPLA model},
  author = {Velvet L. Smith and Bereket Z. Gidi and Robert M. Bragg and Jeffrey P. Cantle and Aliza Ben-Varon and Briana Noble and Silvia Prades and Andrea Compton and Julie Greenfield and Joanna A. Korecka and Anya Gemos and Timothy Yu and Vikram Khurana and Holly B. Kordasiewicz and Hien T. Zhao and Melissa Barker-Haliski and Daniel D. Child and Jeffrey B. Carroll},
  year = {2026},
  journal = {Molecular Therapy Nucleic Acids},
  doi = {10.1016/j.omtn.2025.102815},
  url = {https://doi.org/10.1016/j.omtn.2025.102815}
}

RIS

TY  - JOUR
TI  - Atrophin-1 antisense oligonucleotide provides robust protection from pathology in a fully humanized DRPLA model
AU  - Velvet L. Smith
AU  - Bereket Z. Gidi
AU  - Robert M. Bragg
AU  - Jeffrey P. Cantle
AU  - Aliza Ben-Varon
AU  - Briana Noble
AU  - Silvia Prades
AU  - Andrea Compton
AU  - Julie Greenfield
AU  - Joanna A. Korecka
AU  - Anya Gemos
AU  - Timothy Yu
AU  - Vikram Khurana
AU  - Holly B. Kordasiewicz
AU  - Hien T. Zhao
AU  - Melissa Barker-Haliski
AU  - Daniel D. Child
AU  - Jeffrey B. Carroll
PY  - 2026
JO  - Molecular Therapy Nucleic Acids
DO  - 10.1016/j.omtn.2025.102815
UR  - https://doi.org/10.1016/j.omtn.2025.102815
ER  - 

APA

Smith, V. L., Gidi, B. Z., Bragg, R. M., Cantle, J. P., Ben-Varon, A., Noble, B., Prades, S., Compton, A., Greenfield, J., Korecka, J. A., Gemos, A., Yu, T., Khurana, V., Kordasiewicz, H. B., Zhao, H. T., Barker-Haliski, M., Child, D. D., & Carroll, J. B. (2026). Atrophin-1 antisense oligonucleotide provides robust protection from pathology in a fully humanized DRPLA model. Molecular Therapy Nucleic Acids. https://doi.org/10.1016/j.omtn.2025.102815

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