Targeted insertion of partial CFTR cDNA replicates native CFTR expression with restored channel function in CF airway epithelium.

Barillà C, Suzuki S, Park SH, Nalluri D, Wen H, Hanafy MA, Betancourth D, Umrigar A, Leir SH, Lovrenert K, Sivachenko A, Tabak B, Liu Z, Zhao R, Valley HC, Rab A, Sorscher EJ, Solomon GM, Mense M, Carulli JP, Harris A, Bao G, Davis BR

Open source

DOI
10.1016/j.omtn.2026.103123
Published
2026 Dec 8
Container
Molecular therapy. Nucleic acids
Publisher
Not recorded
Open access
yes

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BibTeX

@article{allodium:10.1016/j.omtn.2026.103123,
  title = {Targeted insertion of partial CFTR cDNA replicates native CFTR expression with restored channel function in CF airway epithelium.},
  author = {Barillà C and Suzuki S and Park SH and Nalluri D and Wen H and Hanafy MA and Betancourth D and Umrigar A and Leir SH and Lovrenert K and Sivachenko A and Tabak B and Liu Z and Zhao R and Valley HC and Rab A and Sorscher EJ and Solomon GM and Mense M and Carulli JP and Harris A and Bao G and Davis BR},
  year = {2026},
  journal = {Molecular therapy. Nucleic acids},
  doi = {10.1016/j.omtn.2026.103123},
  url = {https://doi.org/10.1016/j.omtn.2026.103123}
}

RIS

TY  - JOUR
TI  - Targeted insertion of partial CFTR cDNA replicates native CFTR expression with restored channel function in CF airway epithelium.
AU  - Barillà C
AU  - Suzuki S
AU  - Park SH
AU  - Nalluri D
AU  - Wen H
AU  - Hanafy MA
AU  - Betancourth D
AU  - Umrigar A
AU  - Leir SH
AU  - Lovrenert K
AU  - Sivachenko A
AU  - Tabak B
AU  - Liu Z
AU  - Zhao R
AU  - Valley HC
AU  - Rab A
AU  - Sorscher EJ
AU  - Solomon GM
AU  - Mense M
AU  - Carulli JP
AU  - Harris A
AU  - Bao G
AU  - Davis BR
PY  - 2026
JO  - Molecular therapy. Nucleic acids
DO  - 10.1016/j.omtn.2026.103123
UR  - https://doi.org/10.1016/j.omtn.2026.103123
ER  - 

APA

C, B., S, S., SH, P., D, N., H, W., MA, H., D, B., A, U., SH, L., K, L., A, S., B, T., Z, L., R, Z., HC, V., A, R., EJ, S., GM, S., M, M., JP, C., A, H., G, B., & BR, D. (2026). Targeted insertion of partial CFTR cDNA replicates native CFTR expression with restored channel function in CF airway epithelium.. Molecular therapy. Nucleic acids. https://doi.org/10.1016/j.omtn.2026.103123

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