Lipid nanoparticle-based non-viral in situ gene editing of congenital ichthyosis-causing mutations in human skin models

Dilem Ceren Apaydin, Gaurav Sadhnani, Tiffany Carlaw, Jan Renziehausen, Elena Lizunova, Viviane Filor, Anna Hiller, Sophia Brumhard, Vincent Halim, Ulrike Brüning, Johannes Bischof, Rafaela Horbach Marodin, Daniel Z. Kurek, Manuel Rhiel, Sandra Ammann, Tatjana I. Cornu, Toni Cathomen, Leif Erik Sander, Benedikt Obermayer, Fabian Coscia, Jennifer Kirwan, Ulrich Koller, Achim D. Gruber, Wolfgang Bäumer, Sarah Hedtrich

Open source

DOI: 10.1016/j.stem.2026.01.001
Published: 2026-02
Container: Cell Stem Cell
Publisher: Elsevier BV
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.1016/j.stem.2026.01.001,
  title = {Lipid nanoparticle-based non-viral in situ gene editing of congenital ichthyosis-causing mutations in human skin models},
  author = {Dilem Ceren Apaydin and Gaurav Sadhnani and Tiffany Carlaw and Jan Renziehausen and Elena Lizunova and Viviane Filor and Anna Hiller and Sophia Brumhard and Vincent Halim and Ulrike Brüning and Johannes Bischof and Rafaela Horbach Marodin and Daniel Z. Kurek and Manuel Rhiel and Sandra Ammann and Tatjana I. Cornu and Toni Cathomen and Leif Erik Sander and Benedikt Obermayer and Fabian Coscia and Jennifer Kirwan and Ulrich Koller and Achim D. Gruber and Wolfgang Bäumer and Sarah Hedtrich},
  year = {2026},
  journal = {Cell Stem Cell},
  doi = {10.1016/j.stem.2026.01.001},
  url = {https://doi.org/10.1016/j.stem.2026.01.001}
}

RIS

TY  - JOUR
TI  - Lipid nanoparticle-based non-viral in situ gene editing of congenital ichthyosis-causing mutations in human skin models
AU  - Dilem Ceren Apaydin
AU  - Gaurav Sadhnani
AU  - Tiffany Carlaw
AU  - Jan Renziehausen
AU  - Elena Lizunova
AU  - Viviane Filor
AU  - Anna Hiller
AU  - Sophia Brumhard
AU  - Vincent Halim
AU  - Ulrike Brüning
AU  - Johannes Bischof
AU  - Rafaela Horbach Marodin
AU  - Daniel Z. Kurek
AU  - Manuel Rhiel
AU  - Sandra Ammann
AU  - Tatjana I. Cornu
AU  - Toni Cathomen
AU  - Leif Erik Sander
AU  - Benedikt Obermayer
AU  - Fabian Coscia
AU  - Jennifer Kirwan
AU  - Ulrich Koller
AU  - Achim D. Gruber
AU  - Wolfgang Bäumer
AU  - Sarah Hedtrich
PY  - 2026
JO  - Cell Stem Cell
DO  - 10.1016/j.stem.2026.01.001
UR  - https://doi.org/10.1016/j.stem.2026.01.001
ER  -

APA

Apaydin, D. C., Sadhnani, G., Carlaw, T., Renziehausen, J., Lizunova, E., Filor, V., Hiller, A., Brumhard, S., Halim, V., Brüning, U., Bischof, J., Marodin, R. H., Kurek, D. Z., Rhiel, M., Ammann, S., Cornu, T. I., Cathomen, T., Sander, L. E., Obermayer, B., Coscia, F., Kirwan, J., Koller, U., Gruber, A. D., Bäumer, W., & Hedtrich, S. (2026). Lipid nanoparticle-based non-viral in situ gene editing of congenital ichthyosis-causing mutations in human skin models. Cell Stem Cell. https://doi.org/10.1016/j.stem.2026.01.001

Source records

crossref · retrieved 2026-09-27T08:31:29.321Z