Systemic delivery of phagocytosis-shielded retroviral vectors enables in vivo HSC gene therapy for sickle cell disease

Denise Klatt, Adele Mucci, Boya Liu, Marie Peschers, Giulia Schiroli, Axel Schambach, John Manis, Myriam Armant, David T. Scadden, Els Verhoeyen, Danilo Pellin, David A. Williams, Christian Brendel

Open source

DOI
10.1016/j.stem.2026.09.001
Published
2026-09
Container
Cell Stem Cell
Publisher
Elsevier BV
Open access
unknown

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BibTeX

@article{allodium:10.1016/j.stem.2026.09.001,
  title = {Systemic delivery of phagocytosis-shielded retroviral vectors enables in vivo HSC gene therapy for sickle cell disease},
  author = {Denise Klatt and Adele Mucci and Boya Liu and Marie Peschers and Giulia Schiroli and Axel Schambach and John Manis and Myriam Armant and David T. Scadden and Els Verhoeyen and Danilo Pellin and David A. Williams and Christian Brendel},
  year = {2026},
  journal = {Cell Stem Cell},
  doi = {10.1016/j.stem.2026.09.001},
  url = {https://doi.org/10.1016/j.stem.2026.09.001}
}

RIS

TY  - JOUR
TI  - Systemic delivery of phagocytosis-shielded retroviral vectors enables in vivo HSC gene therapy for sickle cell disease
AU  - Denise Klatt
AU  - Adele Mucci
AU  - Boya Liu
AU  - Marie Peschers
AU  - Giulia Schiroli
AU  - Axel Schambach
AU  - John Manis
AU  - Myriam Armant
AU  - David T. Scadden
AU  - Els Verhoeyen
AU  - Danilo Pellin
AU  - David A. Williams
AU  - Christian Brendel
PY  - 2026
JO  - Cell Stem Cell
DO  - 10.1016/j.stem.2026.09.001
UR  - https://doi.org/10.1016/j.stem.2026.09.001
ER  - 

APA

Klatt, D., Mucci, A., Liu, B., Peschers, M., Schiroli, G., Schambach, A., Manis, J., Armant, M., Scadden, D. T., Verhoeyen, E., Pellin, D., Williams, D. A., & Brendel, C. (2026). Systemic delivery of phagocytosis-shielded retroviral vectors enables in vivo HSC gene therapy for sickle cell disease. Cell Stem Cell. https://doi.org/10.1016/j.stem.2026.09.001

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