Intrathecal idursulfase-IT in patients with neuronopathic mucopolysaccharidosis II: Results from a phase 2/3 randomized study
- DOI
- 10.1016/j.ymgme.2022.07.017
- Published
- 2022-09
- Container
- Molecular Genetics and Metabolism
- Publisher
- Elsevier BV
- Open access
- unknown
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Cite this work
BibTeX
@article{allodium:10.1016/j.ymgme.2022.07.017,
title = {Intrathecal idursulfase-IT in patients with neuronopathic mucopolysaccharidosis II: Results from a phase 2/3 randomized study},
author = {Joseph Muenzer and Barbara K. Burton and Paul Harmatz and Luis González Gutiérrez-Solana and Matilde Ruiz-Garcia and Simon A. Jones and Nathalie Guffon and Michal Inbar-Feigenberg and Drago Bratkovic and Michael Hale and Yuna Wu and Karen S. Yee and David A.H. Whiteman and David Alexanderian},
year = {2022},
journal = {Molecular Genetics and Metabolism},
doi = {10.1016/j.ymgme.2022.07.017},
url = {https://doi.org/10.1016/j.ymgme.2022.07.017}
}RIS
TY - JOUR TI - Intrathecal idursulfase-IT in patients with neuronopathic mucopolysaccharidosis II: Results from a phase 2/3 randomized study AU - Joseph Muenzer AU - Barbara K. Burton AU - Paul Harmatz AU - Luis González Gutiérrez-Solana AU - Matilde Ruiz-Garcia AU - Simon A. Jones AU - Nathalie Guffon AU - Michal Inbar-Feigenberg AU - Drago Bratkovic AU - Michael Hale AU - Yuna Wu AU - Karen S. Yee AU - David A.H. Whiteman AU - David Alexanderian PY - 2022 JO - Molecular Genetics and Metabolism DO - 10.1016/j.ymgme.2022.07.017 UR - https://doi.org/10.1016/j.ymgme.2022.07.017 ER -
APA
Muenzer, J., Burton, B. K., Harmatz, P., Gutiérrez-Solana, L. G., Ruiz-Garcia, M., Jones, S. A., Guffon, N., Inbar-Feigenberg, M., Bratkovic, D., Hale, M., Wu, Y., Yee, K. S., Whiteman, D. A., & Alexanderian, D. (2022). Intrathecal idursulfase-IT in patients with neuronopathic mucopolysaccharidosis II: Results from a phase 2/3 randomized study. Molecular Genetics and Metabolism. https://doi.org/10.1016/j.ymgme.2022.07.017
Source records
- crossref · retrieved 2026-09-27T06:00:10.561Z