Functional characterization of 42 GAA missense variants using a validated in vitro cellular functional assay

Shelly Goomber, Erin Huggins, Catherine W. Rehder, Gregory E. Crawford, Seung-Hye Jung, Jessica Doxey, Apoorva K. Iyengar, Erica B. Nading, Priya S. Kishnani, Deeksha S. Bali

Open source

DOI
10.1016/j.ymgme.2026.110237
Published
2026-09
Container
Molecular Genetics and Metabolism
Publisher
Elsevier BV
Open access
unknown

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BibTeX

@article{allodium:10.1016/j.ymgme.2026.110237,
  title = {Functional characterization of 42 GAA missense variants using a validated in vitro cellular functional assay},
  author = {Shelly Goomber and Erin Huggins and Catherine W. Rehder and Gregory E. Crawford and Seung-Hye Jung and Jessica Doxey and Apoorva K. Iyengar and Erica B. Nading and Priya S. Kishnani and Deeksha S. Bali},
  year = {2026},
  journal = {Molecular Genetics and Metabolism},
  doi = {10.1016/j.ymgme.2026.110237},
  url = {https://doi.org/10.1016/j.ymgme.2026.110237}
}

RIS

TY  - JOUR
TI  - Functional characterization of 42 GAA missense variants using a validated in vitro cellular functional assay
AU  - Shelly Goomber
AU  - Erin Huggins
AU  - Catherine W. Rehder
AU  - Gregory E. Crawford
AU  - Seung-Hye Jung
AU  - Jessica Doxey
AU  - Apoorva K. Iyengar
AU  - Erica B. Nading
AU  - Priya S. Kishnani
AU  - Deeksha S. Bali
PY  - 2026
JO  - Molecular Genetics and Metabolism
DO  - 10.1016/j.ymgme.2026.110237
UR  - https://doi.org/10.1016/j.ymgme.2026.110237
ER  - 

APA

Goomber, S., Huggins, E., Rehder, C. W., Crawford, G. E., Jung, S., Doxey, J., Iyengar, A. K., Nading, E. B., Kishnani, P. S., & Bali, D. S. (2026). Functional characterization of 42 GAA missense variants using a validated in vitro cellular functional assay. Molecular Genetics and Metabolism. https://doi.org/10.1016/j.ymgme.2026.110237

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