Interim analysis of post-marketing surveillance study of intracerebroventricular idursulfase therapy for neuronopathic mucopolysaccharidosis type II: Safety and effectiveness in clinical practice in Japan

Motomichi Kosuga, Tetsumin So, Yasutsugu Chinen, Shungo Okamoto, Tokiko Fukuda, Eiichi Yamamoto, Azuma Ikari, Tadayuki Kumagai, Ikuma Musha, Yasunori Wada, Toshihiko Kakiuchi, Yuki Ueda, Kiyoshi Egawa, Yuki Yamada, Mahoko Furujo, Sumito Dateki, Yoko Nakajima, Naoko Ozawa, Torayuki Okuyama

Open source

DOI: 10.1016/j.ymgme.2026.110243
Published: 2026-09
Container: Molecular Genetics and Metabolism
Publisher: Elsevier BV
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.1016/j.ymgme.2026.110243,
  title = {Interim analysis of post-marketing surveillance study of intracerebroventricular idursulfase therapy for neuronopathic mucopolysaccharidosis type II: Safety and effectiveness in clinical practice in Japan},
  author = {Motomichi Kosuga and Tetsumin So and Yasutsugu Chinen and Shungo Okamoto and Tokiko Fukuda and Eiichi Yamamoto and Azuma Ikari and Tadayuki Kumagai and Ikuma Musha and Yasunori Wada and Toshihiko Kakiuchi and Yuki Ueda and Kiyoshi Egawa and Yuki Yamada and Mahoko Furujo and Sumito Dateki and Yoko Nakajima and Naoko Ozawa and Torayuki Okuyama},
  year = {2026},
  journal = {Molecular Genetics and Metabolism},
  doi = {10.1016/j.ymgme.2026.110243},
  url = {https://doi.org/10.1016/j.ymgme.2026.110243}
}

RIS

TY  - JOUR
TI  - Interim analysis of post-marketing surveillance study of intracerebroventricular idursulfase therapy for neuronopathic mucopolysaccharidosis type II: Safety and effectiveness in clinical practice in Japan
AU  - Motomichi Kosuga
AU  - Tetsumin So
AU  - Yasutsugu Chinen
AU  - Shungo Okamoto
AU  - Tokiko Fukuda
AU  - Eiichi Yamamoto
AU  - Azuma Ikari
AU  - Tadayuki Kumagai
AU  - Ikuma Musha
AU  - Yasunori Wada
AU  - Toshihiko Kakiuchi
AU  - Yuki Ueda
AU  - Kiyoshi Egawa
AU  - Yuki Yamada
AU  - Mahoko Furujo
AU  - Sumito Dateki
AU  - Yoko Nakajima
AU  - Naoko Ozawa
AU  - Torayuki Okuyama
PY  - 2026
JO  - Molecular Genetics and Metabolism
DO  - 10.1016/j.ymgme.2026.110243
UR  - https://doi.org/10.1016/j.ymgme.2026.110243
ER  -

APA

Kosuga, M., So, T., Chinen, Y., Okamoto, S., Fukuda, T., Yamamoto, E., Ikari, A., Kumagai, T., Musha, I., Wada, Y., Kakiuchi, T., Ueda, Y., Egawa, K., Yamada, Y., Furujo, M., Dateki, S., Nakajima, Y., Ozawa, N., & Okuyama, T. (2026). Interim analysis of post-marketing surveillance study of intracerebroventricular idursulfase therapy for neuronopathic mucopolysaccharidosis type II: Safety and effectiveness in clinical practice in Japan. Molecular Genetics and Metabolism. https://doi.org/10.1016/j.ymgme.2026.110243

Source records

crossref · retrieved 2026-09-25T21:03:04.106Z