Changes in motor function, quality of life, and clinical manifestations in patients with Alpha-mannosidosis treated with Velmanase Alfa: Data from the French Étoile Alpha registry.

Guffon N, Mention-Mulliez K, Gaches F, Garavaglia D, Salomone F, Héron B

Open source

DOI
10.1016/j.ymgmr.2026.101351
Published
2026 Sep
Container
Molecular genetics and metabolism reports
Publisher
Not recorded
Open access
yes

Credibility signals

limited evidence Score 45/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.

Show all credibility signals

Cite this work

BibTeX

@article{allodium:10.1016/j.ymgmr.2026.101351,
  title = {Changes in motor function, quality of life, and clinical manifestations in patients with Alpha-mannosidosis treated with Velmanase Alfa: Data from the French Étoile Alpha registry.},
  author = {Guffon N and Mention-Mulliez K and Gaches F and Garavaglia D and Salomone F and Héron B},
  year = {2026},
  journal = {Molecular genetics and metabolism reports},
  doi = {10.1016/j.ymgmr.2026.101351},
  url = {https://doi.org/10.1016/j.ymgmr.2026.101351}
}

RIS

TY  - JOUR
TI  - Changes in motor function, quality of life, and clinical manifestations in patients with Alpha-mannosidosis treated with Velmanase Alfa: Data from the French Étoile Alpha registry.
AU  - Guffon N
AU  - Mention-Mulliez K
AU  - Gaches F
AU  - Garavaglia D
AU  - Salomone F
AU  - Héron B
PY  - 2026
JO  - Molecular genetics and metabolism reports
DO  - 10.1016/j.ymgmr.2026.101351
UR  - https://doi.org/10.1016/j.ymgmr.2026.101351
ER  - 

APA

N, G., K, M., F, G., D, G., F, S., & B, H. (2026). Changes in motor function, quality of life, and clinical manifestations in patients with Alpha-mannosidosis treated with Velmanase Alfa: Data from the French Étoile Alpha registry.. Molecular genetics and metabolism reports. https://doi.org/10.1016/j.ymgmr.2026.101351

Source records