Olipudase alfa for acid sphingomyelinase deficiency: Evidence of efficacy from a compassionate use program
- DOI
- 10.1016/j.ymgmr.2026.101372
- Published
- 2026-12
- Container
- Molecular Genetics and Metabolism Reports
- Publisher
- Elsevier BV
- Open access
- unknown
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Cite this work
BibTeX
@article{allodium:10.1016/j.ymgmr.2026.101372,
title = {Olipudase alfa for acid sphingomyelinase deficiency: Evidence of efficacy from a compassionate use program},
author = {Vincenza Gragnaniello and Veronica Maria Tagi and Francesca Carubbi and Antonio Barbato and Michelina Sibilio and Simona Fecarotta and Maria Grazia Pappalardo and Irene Motta and Annalisa Sechi and Maurizio Scarpa and Andrea Pession and Laura Fiori},
year = {2026},
journal = {Molecular Genetics and Metabolism Reports},
doi = {10.1016/j.ymgmr.2026.101372},
url = {https://doi.org/10.1016/j.ymgmr.2026.101372}
}RIS
TY - JOUR TI - Olipudase alfa for acid sphingomyelinase deficiency: Evidence of efficacy from a compassionate use program AU - Vincenza Gragnaniello AU - Veronica Maria Tagi AU - Francesca Carubbi AU - Antonio Barbato AU - Michelina Sibilio AU - Simona Fecarotta AU - Maria Grazia Pappalardo AU - Irene Motta AU - Annalisa Sechi AU - Maurizio Scarpa AU - Andrea Pession AU - Laura Fiori PY - 2026 JO - Molecular Genetics and Metabolism Reports DO - 10.1016/j.ymgmr.2026.101372 UR - https://doi.org/10.1016/j.ymgmr.2026.101372 ER -
APA
Gragnaniello, V., Tagi, V. M., Carubbi, F., Barbato, A., Sibilio, M., Fecarotta, S., Pappalardo, M. G., Motta, I., Sechi, A., Scarpa, M., Pession, A., & Fiori, L. (2026). Olipudase alfa for acid sphingomyelinase deficiency: Evidence of efficacy from a compassionate use program. Molecular Genetics and Metabolism Reports. https://doi.org/10.1016/j.ymgmr.2026.101372
Source records
- crossref · retrieved 2026-11-10T20:41:27.849Z