A Pharmacological Chaperone Therapy for Acute Intermittent Porphyria.
- DOI
- 10.1016/j.ymthe.2019.11.010
- Published
- 2020 Feb 5
- Container
- Molecular therapy : the journal of the American Society of Gene Therapy
- Publisher
- Not recorded
- Open access
- yes
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Cite this work
BibTeX
@article{allodium:10.1016/j.ymthe.2019.11.010,
title = {A Pharmacological Chaperone Therapy for Acute Intermittent Porphyria.},
author = {Bustad HJ and Toska K and Schmitt C and Vorland M and Skjærven L and Kallio JP and Simonin S and Letteron P and Underhaug J and Sandberg S and Martinez A},
year = {2020},
journal = {Molecular therapy : the journal of the American Society of Gene Therapy},
doi = {10.1016/j.ymthe.2019.11.010},
url = {https://doi.org/10.1016/j.ymthe.2019.11.010}
}RIS
TY - JOUR TI - A Pharmacological Chaperone Therapy for Acute Intermittent Porphyria. AU - Bustad HJ AU - Toska K AU - Schmitt C AU - Vorland M AU - Skjærven L AU - Kallio JP AU - Simonin S AU - Letteron P AU - Underhaug J AU - Sandberg S AU - Martinez A PY - 2020 JO - Molecular therapy : the journal of the American Society of Gene Therapy DO - 10.1016/j.ymthe.2019.11.010 UR - https://doi.org/10.1016/j.ymthe.2019.11.010 ER -
APA
HJ, B., K, T., C, S., M, V., L, S., JP, K., S, S., P, L., J, U., S, S., & A, M. (2020). A Pharmacological Chaperone Therapy for Acute Intermittent Porphyria.. Molecular therapy : the journal of the American Society of Gene Therapy. https://doi.org/10.1016/j.ymthe.2019.11.010
Source records
- pubmed · retrieved 2026-09-27T11:47:38.203Z