Hematopoietic stem cell gene therapy improves outcomes in a clinically relevant mouse model of multiple sulfatase deficiency.

Pham V, Tricoli L, Hong X, Wongkittichote P, Castruccio Castracani C, Guerra A, Schlotawa L, Adang LA, Kuhs A, Cassidy MM, Kane O, Tsai E, Presa M, Lutz C, Rivella SB, Ahrens-Nicklas RC

Open source

DOI
10.1016/j.ymthe.2024.08.015
Published
2024 Nov 6
Container
Molecular therapy : the journal of the American Society of Gene Therapy
Publisher
Not recorded
Open access
yes

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BibTeX

@article{allodium:10.1016/j.ymthe.2024.08.015,
  title = {Hematopoietic stem cell gene therapy improves outcomes in a clinically relevant mouse model of multiple sulfatase deficiency.},
  author = {Pham V and Tricoli L and Hong X and Wongkittichote P and Castruccio Castracani C and Guerra A and Schlotawa L and Adang LA and Kuhs A and Cassidy MM and Kane O and Tsai E and Presa M and Lutz C and Rivella SB and Ahrens-Nicklas RC},
  year = {2024},
  journal = {Molecular therapy : the journal of the American Society of Gene Therapy},
  doi = {10.1016/j.ymthe.2024.08.015},
  url = {https://doi.org/10.1016/j.ymthe.2024.08.015}
}

RIS

TY  - JOUR
TI  - Hematopoietic stem cell gene therapy improves outcomes in a clinically relevant mouse model of multiple sulfatase deficiency.
AU  - Pham V
AU  - Tricoli L
AU  - Hong X
AU  - Wongkittichote P
AU  - Castruccio Castracani C
AU  - Guerra A
AU  - Schlotawa L
AU  - Adang LA
AU  - Kuhs A
AU  - Cassidy MM
AU  - Kane O
AU  - Tsai E
AU  - Presa M
AU  - Lutz C
AU  - Rivella SB
AU  - Ahrens-Nicklas RC
PY  - 2024
JO  - Molecular therapy : the journal of the American Society of Gene Therapy
DO  - 10.1016/j.ymthe.2024.08.015
UR  - https://doi.org/10.1016/j.ymthe.2024.08.015
ER  - 

APA

V, P., L, T., X, H., P, W., C, C. C., A, G., L, S., LA, A., A, K., MM, C., O, K., E, T., M, P., C, L., SB, R., & RC, A. (2024). Hematopoietic stem cell gene therapy improves outcomes in a clinically relevant mouse model of multiple sulfatase deficiency.. Molecular therapy : the journal of the American Society of Gene Therapy. https://doi.org/10.1016/j.ymthe.2024.08.015

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