Hematopoietic stem cell gene therapy improves outcomes in a clinically relevant mouse model of multiple sulfatase deficiency.
- DOI
- 10.1016/j.ymthe.2024.08.015
- Published
- 2024 Nov 6
- Container
- Molecular therapy : the journal of the American Society of Gene Therapy
- Publisher
- Not recorded
- Open access
- yes
Credibility signals
limited evidence Score 45/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.
Show all credibility signals
- cautionDOI registered: No matching Crossref record was present in this response.
- cautionDOI resolves: No matching Crossref record was present in this response.
- not scoredDirectory of Open Access Journals: No matching DOAJ record was present in this response. No allow-list match; this is not evidence of low credibility.
- not scoredMEDLINE indexed: Not checked or no result supplied; no credibility inference made.
- not scoredOpenAlex core source: Not checked or no result supplied; no credibility inference made.
- not scoredKnown publisher allow-list: Not checked or no result supplied; no credibility inference made.
- not scoredROR affiliation: Not checked or no result supplied; no credibility inference made.
- not scoredRetraction Watch retraction: No retraction notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch expression of concern: No expression of concern notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch correction: No correction notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch reinstatement: No reinstatement notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- supportingOpen access status: Normalized open-access status: open.
- not scoredPublication license: Not checked or no result supplied; no credibility inference made.
- not scoredPublication version: A publication version was supplied but is not scored.
- cautionMetadata completeness: 5 of 6 scored descriptive metadata groups are present; missing fields increase uncertainty.
Cite this work
BibTeX
@article{allodium:10.1016/j.ymthe.2024.08.015,
title = {Hematopoietic stem cell gene therapy improves outcomes in a clinically relevant mouse model of multiple sulfatase deficiency.},
author = {Pham V and Tricoli L and Hong X and Wongkittichote P and Castruccio Castracani C and Guerra A and Schlotawa L and Adang LA and Kuhs A and Cassidy MM and Kane O and Tsai E and Presa M and Lutz C and Rivella SB and Ahrens-Nicklas RC},
year = {2024},
journal = {Molecular therapy : the journal of the American Society of Gene Therapy},
doi = {10.1016/j.ymthe.2024.08.015},
url = {https://doi.org/10.1016/j.ymthe.2024.08.015}
}RIS
TY - JOUR TI - Hematopoietic stem cell gene therapy improves outcomes in a clinically relevant mouse model of multiple sulfatase deficiency. AU - Pham V AU - Tricoli L AU - Hong X AU - Wongkittichote P AU - Castruccio Castracani C AU - Guerra A AU - Schlotawa L AU - Adang LA AU - Kuhs A AU - Cassidy MM AU - Kane O AU - Tsai E AU - Presa M AU - Lutz C AU - Rivella SB AU - Ahrens-Nicklas RC PY - 2024 JO - Molecular therapy : the journal of the American Society of Gene Therapy DO - 10.1016/j.ymthe.2024.08.015 UR - https://doi.org/10.1016/j.ymthe.2024.08.015 ER -
APA
V, P., L, T., X, H., P, W., C, C. C., A, G., L, S., LA, A., A, K., MM, C., O, K., E, T., M, P., C, L., SB, R., & RC, A. (2024). Hematopoietic stem cell gene therapy improves outcomes in a clinically relevant mouse model of multiple sulfatase deficiency.. Molecular therapy : the journal of the American Society of Gene Therapy. https://doi.org/10.1016/j.ymthe.2024.08.015
Source records
- pubmed · retrieved 2026-09-26T12:52:51.938Z