Current clinical applications of AAV-mediated gene therapy.

Byrne BJ, Flanigan KM, Matesanz SE, Finkel RS, Waldrop MA, D'Ambrosio ES, Johnson NE, Smith BK, Bönnemann C, Carrig S, Rossano JW, Greenberg B, Lalaguna L, Lara-Pezzi E, Subramony S, Corti M, Mercado-Rodriguez C, Leon-Astudillo C, Ahrens-Nicklas R, Bharucha-Goebel D, Gao G, Gessler DJ, Hwu WL, Chien YH, Lee NC, Boye SL, Boye SE, George LA

Open source

DOI: 10.1016/j.ymthe.2025.04.045
Published: 2025 Jun 4
Container: Molecular therapy : the journal of the American Society of Gene Therapy
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1016/j.ymthe.2025.04.045,
  title = {Current clinical applications of AAV-mediated gene therapy.},
  author = {Byrne BJ and Flanigan KM and Matesanz SE and Finkel RS and Waldrop MA and D'Ambrosio ES and Johnson NE and Smith BK and Bönnemann C and Carrig S and Rossano JW and Greenberg B and Lalaguna L and Lara-Pezzi E and Subramony S and Corti M and Mercado-Rodriguez C and Leon-Astudillo C and Ahrens-Nicklas R and Bharucha-Goebel D and Gao G and Gessler DJ and Hwu WL and Chien YH and Lee NC and Boye SL and Boye SE and George LA},
  year = {2025},
  journal = {Molecular therapy : the journal of the American Society of Gene Therapy},
  doi = {10.1016/j.ymthe.2025.04.045},
  url = {https://doi.org/10.1016/j.ymthe.2025.04.045}
}

RIS

TY  - JOUR
TI  - Current clinical applications of AAV-mediated gene therapy.
AU  - Byrne BJ
AU  - Flanigan KM
AU  - Matesanz SE
AU  - Finkel RS
AU  - Waldrop MA
AU  - D'Ambrosio ES
AU  - Johnson NE
AU  - Smith BK
AU  - Bönnemann C
AU  - Carrig S
AU  - Rossano JW
AU  - Greenberg B
AU  - Lalaguna L
AU  - Lara-Pezzi E
AU  - Subramony S
AU  - Corti M
AU  - Mercado-Rodriguez C
AU  - Leon-Astudillo C
AU  - Ahrens-Nicklas R
AU  - Bharucha-Goebel D
AU  - Gao G
AU  - Gessler DJ
AU  - Hwu WL
AU  - Chien YH
AU  - Lee NC
AU  - Boye SL
AU  - Boye SE
AU  - George LA
PY  - 2025
JO  - Molecular therapy : the journal of the American Society of Gene Therapy
DO  - 10.1016/j.ymthe.2025.04.045
UR  - https://doi.org/10.1016/j.ymthe.2025.04.045
ER  -

APA

BJ, B., KM, F., SE, M., RS, F., MA, W., ES, D., NE, J., BK, S., C, B., S, C., JW, R., B, G., L, L., E, L., S, S., M, C., C, M., C, L., R, A., D, B., G, G., DJ, G., WL, H., YH, C., NC, L., SL, B., SE, B., & LA, G. (2025). Current clinical applications of AAV-mediated gene therapy.. Molecular therapy : the journal of the American Society of Gene Therapy. https://doi.org/10.1016/j.ymthe.2025.04.045

Source records

pubmed · retrieved 2026-09-26T09:14:27.354Z