Challenging the more-is-better dogma: A precision-optimized AAV gene therapy for SMA

Chunjuan Song, Jingbo Liu, Qingzeng Wang, Peixin Zhu, Jiayi Xu, Ying Zhou, Zhucheng Lin, Xin Xin, Wei Hu, Zhongwan Li, Shuyuan Chen, Ye Zhang, Shaoyong Li, Junhui Li, Yigang Wang, Jingjing Luo, Xiaoyuan Jia, Ni Yuan, Lijun Wang, Guo-jie Ye, Yi Wang, Zhenhua Wu

Open source

DOI
10.1016/j.ymthe.2026.04.027
Published
2026-07
Container
Molecular Therapy
Publisher
Elsevier BV
Open access
unknown

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BibTeX

@article{allodium:10.1016/j.ymthe.2026.04.027,
  title = {Challenging the more-is-better dogma: A precision-optimized AAV gene therapy for SMA},
  author = {Chunjuan Song and Jingbo Liu and Qingzeng Wang and Peixin Zhu and Jiayi Xu and Ying Zhou and Zhucheng Lin and Xin Xin and Wei Hu and Zhongwan Li and Shuyuan Chen and Ye Zhang and Shaoyong Li and Junhui Li and Yigang Wang and Jingjing Luo and Xiaoyuan Jia and Ni Yuan and Lijun Wang and Guo-jie Ye and Yi Wang and Zhenhua Wu},
  year = {2026},
  journal = {Molecular Therapy},
  doi = {10.1016/j.ymthe.2026.04.027},
  url = {https://doi.org/10.1016/j.ymthe.2026.04.027}
}

RIS

TY  - JOUR
TI  - Challenging the more-is-better dogma: A precision-optimized AAV gene therapy for SMA
AU  - Chunjuan Song
AU  - Jingbo Liu
AU  - Qingzeng Wang
AU  - Peixin Zhu
AU  - Jiayi Xu
AU  - Ying Zhou
AU  - Zhucheng Lin
AU  - Xin Xin
AU  - Wei Hu
AU  - Zhongwan Li
AU  - Shuyuan Chen
AU  - Ye Zhang
AU  - Shaoyong Li
AU  - Junhui Li
AU  - Yigang Wang
AU  - Jingjing Luo
AU  - Xiaoyuan Jia
AU  - Ni Yuan
AU  - Lijun Wang
AU  - Guo-jie Ye
AU  - Yi Wang
AU  - Zhenhua Wu
PY  - 2026
JO  - Molecular Therapy
DO  - 10.1016/j.ymthe.2026.04.027
UR  - https://doi.org/10.1016/j.ymthe.2026.04.027
ER  - 

APA

Song, C., Liu, J., Wang, Q., Zhu, P., Xu, J., Zhou, Y., Lin, Z., Xin, X., Hu, W., Li, Z., Chen, S., Zhang, Y., Li, S., Li, J., Wang, Y., Luo, J., Jia, X., Yuan, N., Wang, L., Ye, G., Wang, Y., & Wu, Z. (2026). Challenging the more-is-better dogma: A precision-optimized AAV gene therapy for SMA. Molecular Therapy. https://doi.org/10.1016/j.ymthe.2026.04.027

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