Hepatic gene replacement improves energy metabolism and survival in a mouse model of neonatal mitochondrial disease GRACILE syndrome.

Banerjee R, Purhonen J, Sultana N, Ros O, Nieminen AI, Kietz C, Fellman V, Kallijärvi J

Open source

DOI
10.1016/j.ymthe.2026.04.044
Published
2026 Aug 5
Container
Molecular therapy : the journal of the American Society of Gene Therapy
Publisher
Not recorded
Open access
yes

Credibility signals

limited evidence Score 45/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.

Show all credibility signals

Cite this work

BibTeX

@article{allodium:10.1016/j.ymthe.2026.04.044,
  title = {Hepatic gene replacement improves energy metabolism and survival in a mouse model of neonatal mitochondrial disease GRACILE syndrome.},
  author = {Banerjee R and Purhonen J and Sultana N and Ros O and Nieminen AI and Kietz C and Fellman V and Kallijärvi J},
  year = {2026},
  journal = {Molecular therapy : the journal of the American Society of Gene Therapy},
  doi = {10.1016/j.ymthe.2026.04.044},
  url = {https://doi.org/10.1016/j.ymthe.2026.04.044}
}

RIS

TY  - JOUR
TI  - Hepatic gene replacement improves energy metabolism and survival in a mouse model of neonatal mitochondrial disease GRACILE syndrome.
AU  - Banerjee R
AU  - Purhonen J
AU  - Sultana N
AU  - Ros O
AU  - Nieminen AI
AU  - Kietz C
AU  - Fellman V
AU  - Kallijärvi J
PY  - 2026
JO  - Molecular therapy : the journal of the American Society of Gene Therapy
DO  - 10.1016/j.ymthe.2026.04.044
UR  - https://doi.org/10.1016/j.ymthe.2026.04.044
ER  - 

APA

R, B., J, P., N, S., O, R., AI, N., C, K., V, F., & J, K. (2026). Hepatic gene replacement improves energy metabolism and survival in a mouse model of neonatal mitochondrial disease GRACILE syndrome.. Molecular therapy : the journal of the American Society of Gene Therapy. https://doi.org/10.1016/j.ymthe.2026.04.044

Source records