Lipid nanoparticle delivery of antisense gapmers attenuates pathology in a mouse model of facioscapulohumeral muscular dystrophy.
- DOI
- 10.1016/j.ymthe.2026.05.010
- Published
- 2026 Aug 5
- Container
- Molecular therapy : the journal of the American Society of Gene Therapy
- Publisher
- Not recorded
- Open access
- yes
Credibility signals
limited evidence Score 45/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.
Show all credibility signals
- cautionDOI registered: No matching Crossref record was present in this response.
- cautionDOI resolves: No matching Crossref record was present in this response.
- not scoredDirectory of Open Access Journals: No matching DOAJ record was present in this response. No allow-list match; this is not evidence of low credibility.
- not scoredMEDLINE indexed: Not checked or no result supplied; no credibility inference made.
- not scoredOpenAlex core source: Not checked or no result supplied; no credibility inference made.
- not scoredKnown publisher allow-list: Not checked or no result supplied; no credibility inference made.
- not scoredROR affiliation: Not checked or no result supplied; no credibility inference made.
- not scoredRetraction Watch retraction: No retraction notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch expression of concern: No expression of concern notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch correction: No correction notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch reinstatement: No reinstatement notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- supportingOpen access status: Normalized open-access status: open.
- not scoredPublication license: Not checked or no result supplied; no credibility inference made.
- not scoredPublication version: A publication version was supplied but is not scored.
- cautionMetadata completeness: 5 of 6 scored descriptive metadata groups are present; missing fields increase uncertainty.
Cite this work
BibTeX
@article{allodium:10.1016/j.ymthe.2026.05.010,
title = {Lipid nanoparticle delivery of antisense gapmers attenuates pathology in a mouse model of facioscapulohumeral muscular dystrophy.},
author = {Anwar S and Chan KYT and Zia A and Beck SL and Moriyama H and Lim KRQ and Shah MNA and Haque US and Maruyama R and Witzigmann D and Echigoya Y and Bosnakovski D and Kyba M and Cullis PR and Yokota T},
year = {2026},
journal = {Molecular therapy : the journal of the American Society of Gene Therapy},
doi = {10.1016/j.ymthe.2026.05.010},
url = {https://doi.org/10.1016/j.ymthe.2026.05.010}
}RIS
TY - JOUR TI - Lipid nanoparticle delivery of antisense gapmers attenuates pathology in a mouse model of facioscapulohumeral muscular dystrophy. AU - Anwar S AU - Chan KYT AU - Zia A AU - Beck SL AU - Moriyama H AU - Lim KRQ AU - Shah MNA AU - Haque US AU - Maruyama R AU - Witzigmann D AU - Echigoya Y AU - Bosnakovski D AU - Kyba M AU - Cullis PR AU - Yokota T PY - 2026 JO - Molecular therapy : the journal of the American Society of Gene Therapy DO - 10.1016/j.ymthe.2026.05.010 UR - https://doi.org/10.1016/j.ymthe.2026.05.010 ER -
APA
S, A., KYT, C., A, Z., SL, B., H, M., KRQ, L., MNA, S., US, H., R, M., D, W., Y, E., D, B., M, K., PR, C., & T, Y. (2026). Lipid nanoparticle delivery of antisense gapmers attenuates pathology in a mouse model of facioscapulohumeral muscular dystrophy.. Molecular therapy : the journal of the American Society of Gene Therapy. https://doi.org/10.1016/j.ymthe.2026.05.010
Source records
- pubmed · retrieved 2026-09-27T14:16:04.339Z
- europe-pmc · retrieved 2026-09-27T14:16:04.359Z