Treatment of spinal injury muscle spasticity by spinal subpial AAV9-GAD65/VGAT delivery: An efficacy and safety study in rat, pig, and NHP.

Nguyen D, Yoshizumi T, Sawamura M, Agashkov K, Krotov V, Hruska-Plochan M, Tadokoro T, Kemthong T, Platoshyn O, Miyanohara A, Kamizato K, Juhas S, Juhasova J, Studenovska H, Polymenidou M, Skalnikova HK, Motlik J, Proks V, Teeravechyan S, Abraham ME, Vanicky I, Belan P, Ciacci J, Marsala M

Open source

DOI: 10.1016/j.ymthe.2026.06.008
Published: 2026 Sep 2
Container: Molecular therapy : the journal of the American Society of Gene Therapy
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1016/j.ymthe.2026.06.008,
  title = {Treatment of spinal injury muscle spasticity by spinal subpial AAV9-GAD65/VGAT delivery: An efficacy and safety study in rat, pig, and NHP.},
  author = {Nguyen D and Yoshizumi T and Sawamura M and Agashkov K and Krotov V and Hruska-Plochan M and Tadokoro T and Kemthong T and Platoshyn O and Miyanohara A and Kamizato K and Juhas S and Juhasova J and Studenovska H and Polymenidou M and Skalnikova HK and Motlik J and Proks V and Teeravechyan S and Abraham ME and Vanicky I and Belan P and Ciacci J and Marsala M},
  year = {2026},
  journal = {Molecular therapy : the journal of the American Society of Gene Therapy},
  doi = {10.1016/j.ymthe.2026.06.008},
  url = {https://doi.org/10.1016/j.ymthe.2026.06.008}
}

RIS

TY  - JOUR
TI  - Treatment of spinal injury muscle spasticity by spinal subpial AAV9-GAD65/VGAT delivery: An efficacy and safety study in rat, pig, and NHP.
AU  - Nguyen D
AU  - Yoshizumi T
AU  - Sawamura M
AU  - Agashkov K
AU  - Krotov V
AU  - Hruska-Plochan M
AU  - Tadokoro T
AU  - Kemthong T
AU  - Platoshyn O
AU  - Miyanohara A
AU  - Kamizato K
AU  - Juhas S
AU  - Juhasova J
AU  - Studenovska H
AU  - Polymenidou M
AU  - Skalnikova HK
AU  - Motlik J
AU  - Proks V
AU  - Teeravechyan S
AU  - Abraham ME
AU  - Vanicky I
AU  - Belan P
AU  - Ciacci J
AU  - Marsala M
PY  - 2026
JO  - Molecular therapy : the journal of the American Society of Gene Therapy
DO  - 10.1016/j.ymthe.2026.06.008
UR  - https://doi.org/10.1016/j.ymthe.2026.06.008
ER  -

APA

D, N., T, Y., M, S., K, A., V, K., M, H., T, T., T, K., O, P., A, M., K, K., S, J., J, J., H, S., M, P., HK, S., J, M., V, P., S, T., ME, A., I, V., P, B., J, C., & M, M. (2026). Treatment of spinal injury muscle spasticity by spinal subpial AAV9-GAD65/VGAT delivery: An efficacy and safety study in rat, pig, and NHP.. Molecular therapy : the journal of the American Society of Gene Therapy. https://doi.org/10.1016/j.ymthe.2026.06.008

Source records

pubmed · retrieved 2026-09-26T07:51:38.547Z