Precise hepatic base editing of ASGR1 enables robust and durable LDLR-independent lipid lowering in vivo

Yaofeng Hou, Yaxin Luo, Jiabei Chen, Xindi Shang, Yan Chang, Xianfang Zhang, Yan Ding, Wenwen Zhao, Chengfeng Ding, Xuan Feng, Jia Chen, Jianfeng Li, Bei Yang

Open source

DOI
10.1016/j.ymthe.2026.07.036
Published
2026-07
Container
Molecular Therapy
Publisher
Elsevier BV
Open access
unknown

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BibTeX

@article{allodium:10.1016/j.ymthe.2026.07.036,
  title = {Precise hepatic base editing of ASGR1 enables robust and durable LDLR-independent lipid lowering in vivo},
  author = {Yaofeng Hou and Yaxin Luo and Jiabei Chen and Xindi Shang and Yan Chang and Xianfang Zhang and Yan Ding and Wenwen Zhao and Chengfeng Ding and Xuan Feng and Jia Chen and Jianfeng Li and Bei Yang},
  year = {2026},
  journal = {Molecular Therapy},
  doi = {10.1016/j.ymthe.2026.07.036},
  url = {https://doi.org/10.1016/j.ymthe.2026.07.036}
}

RIS

TY  - JOUR
TI  - Precise hepatic base editing of ASGR1 enables robust and durable LDLR-independent lipid lowering in vivo
AU  - Yaofeng Hou
AU  - Yaxin Luo
AU  - Jiabei Chen
AU  - Xindi Shang
AU  - Yan Chang
AU  - Xianfang Zhang
AU  - Yan Ding
AU  - Wenwen Zhao
AU  - Chengfeng Ding
AU  - Xuan Feng
AU  - Jia Chen
AU  - Jianfeng Li
AU  - Bei Yang
PY  - 2026
JO  - Molecular Therapy
DO  - 10.1016/j.ymthe.2026.07.036
UR  - https://doi.org/10.1016/j.ymthe.2026.07.036
ER  - 

APA

Hou, Y., Luo, Y., Chen, J., Shang, X., Chang, Y., Zhang, X., Ding, Y., Zhao, W., Ding, C., Feng, X., Chen, J., Li, J., & Yang, B. (2026). Precise hepatic base editing of ASGR1 enables robust and durable LDLR-independent lipid lowering in vivo. Molecular Therapy. https://doi.org/10.1016/j.ymthe.2026.07.036

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