AAV-mediated CBLN1 replacement rescues hereditary ataxia caused by bi-allelic CBLN1 variants.
- DOI
- 10.1016/j.ymthe.2026.09.003
- Published
- 2026 Sep 2
- Container
- Molecular therapy : the journal of the American Society of Gene Therapy
- Publisher
- Not recorded
- Open access
- unknown
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Cite this work
BibTeX
@article{allodium:10.1016/j.ymthe.2026.09.003,
title = {AAV-mediated CBLN1 replacement rescues hereditary ataxia caused by bi-allelic CBLN1 variants.},
author = {Yamasaki T and Kakegawa W and Hayashi A and Ogawa N and Takano T and Matsuda K and Takatsuto K and Abdel-Hamid MS and Zaki MS and Gleeson JG and Yuzaki M},
year = {2026},
journal = {Molecular therapy : the journal of the American Society of Gene Therapy},
doi = {10.1016/j.ymthe.2026.09.003},
url = {https://doi.org/10.1016/j.ymthe.2026.09.003}
}RIS
TY - JOUR TI - AAV-mediated CBLN1 replacement rescues hereditary ataxia caused by bi-allelic CBLN1 variants. AU - Yamasaki T AU - Kakegawa W AU - Hayashi A AU - Ogawa N AU - Takano T AU - Matsuda K AU - Takatsuto K AU - Abdel-Hamid MS AU - Zaki MS AU - Gleeson JG AU - Yuzaki M PY - 2026 JO - Molecular therapy : the journal of the American Society of Gene Therapy DO - 10.1016/j.ymthe.2026.09.003 UR - https://doi.org/10.1016/j.ymthe.2026.09.003 ER -
APA
T, Y., W, K., A, H., N, O., T, T., K, M., K, T., MS, A., MS, Z., JG, G., & M, Y. (2026). AAV-mediated CBLN1 replacement rescues hereditary ataxia caused by bi-allelic CBLN1 variants.. Molecular therapy : the journal of the American Society of Gene Therapy. https://doi.org/10.1016/j.ymthe.2026.09.003
Source records
- pubmed · retrieved 2026-09-26T04:14:57.876Z