AAV-mediated CBLN1 replacement rescues hereditary ataxia caused by bi-allelic CBLN1 variants.

Yamasaki T, Kakegawa W, Hayashi A, Ogawa N, Takano T, Matsuda K, Takatsuto K, Abdel-Hamid MS, Zaki MS, Gleeson JG, Yuzaki M

Open source

DOI
10.1016/j.ymthe.2026.09.003
Published
2026 Sep 2
Container
Molecular therapy : the journal of the American Society of Gene Therapy
Publisher
Not recorded
Open access
unknown

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BibTeX

@article{allodium:10.1016/j.ymthe.2026.09.003,
  title = {AAV-mediated CBLN1 replacement rescues hereditary ataxia caused by bi-allelic CBLN1 variants.},
  author = {Yamasaki T and Kakegawa W and Hayashi A and Ogawa N and Takano T and Matsuda K and Takatsuto K and Abdel-Hamid MS and Zaki MS and Gleeson JG and Yuzaki M},
  year = {2026},
  journal = {Molecular therapy : the journal of the American Society of Gene Therapy},
  doi = {10.1016/j.ymthe.2026.09.003},
  url = {https://doi.org/10.1016/j.ymthe.2026.09.003}
}

RIS

TY  - JOUR
TI  - AAV-mediated CBLN1 replacement rescues hereditary ataxia caused by bi-allelic CBLN1 variants.
AU  - Yamasaki T
AU  - Kakegawa W
AU  - Hayashi A
AU  - Ogawa N
AU  - Takano T
AU  - Matsuda K
AU  - Takatsuto K
AU  - Abdel-Hamid MS
AU  - Zaki MS
AU  - Gleeson JG
AU  - Yuzaki M
PY  - 2026
JO  - Molecular therapy : the journal of the American Society of Gene Therapy
DO  - 10.1016/j.ymthe.2026.09.003
UR  - https://doi.org/10.1016/j.ymthe.2026.09.003
ER  - 

APA

T, Y., W, K., A, H., N, O., T, T., K, M., K, T., MS, A., MS, Z., JG, G., & M, Y. (2026). AAV-mediated CBLN1 replacement rescues hereditary ataxia caused by bi-allelic CBLN1 variants.. Molecular therapy : the journal of the American Society of Gene Therapy. https://doi.org/10.1016/j.ymthe.2026.09.003

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