Targeting white matter astrocytes with a Gfap-disruptive Cas9 nuclease benefits a murine model of Alexander disease

Anne E.J. Hillen, Irene Capuano, Barbara Gega, Rossana Norata, Margaux Mombled, Ilaria Laface, Giada Zambonini, Andrea Lomagno, Marine Rouillon, Serena G. Giannelli, Fabrizio Benedicenti, Francesco Gazzo, Sergio Arévalo, Giulio Spinozzi, Francesca Sanvito, Mario Amendola, Vania Broccoli, Eugenio Montini, Angela Gritti, Vasco Meneghini

Open source

DOI
10.1016/j.ymthe.2026.09.019
Published
2026-09
Container
Molecular Therapy
Publisher
Elsevier BV
Open access
unknown

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BibTeX

@article{allodium:10.1016/j.ymthe.2026.09.019,
  title = {Targeting white matter astrocytes with a Gfap-disruptive Cas9 nuclease benefits a murine model of Alexander disease},
  author = {Anne E.J. Hillen and Irene Capuano and Barbara Gega and Rossana Norata and Margaux Mombled and Ilaria Laface and Giada Zambonini and Andrea Lomagno and Marine Rouillon and Serena G. Giannelli and Fabrizio Benedicenti and Francesco Gazzo and Sergio Arévalo and Giulio Spinozzi and Francesca Sanvito and Mario Amendola and Vania Broccoli and Eugenio Montini and Angela Gritti and Vasco Meneghini},
  year = {2026},
  journal = {Molecular Therapy},
  doi = {10.1016/j.ymthe.2026.09.019},
  url = {https://doi.org/10.1016/j.ymthe.2026.09.019}
}

RIS

TY  - JOUR
TI  - Targeting white matter astrocytes with a Gfap-disruptive Cas9 nuclease benefits a murine model of Alexander disease
AU  - Anne E.J. Hillen
AU  - Irene Capuano
AU  - Barbara Gega
AU  - Rossana Norata
AU  - Margaux Mombled
AU  - Ilaria Laface
AU  - Giada Zambonini
AU  - Andrea Lomagno
AU  - Marine Rouillon
AU  - Serena G. Giannelli
AU  - Fabrizio Benedicenti
AU  - Francesco Gazzo
AU  - Sergio Arévalo
AU  - Giulio Spinozzi
AU  - Francesca Sanvito
AU  - Mario Amendola
AU  - Vania Broccoli
AU  - Eugenio Montini
AU  - Angela Gritti
AU  - Vasco Meneghini
PY  - 2026
JO  - Molecular Therapy
DO  - 10.1016/j.ymthe.2026.09.019
UR  - https://doi.org/10.1016/j.ymthe.2026.09.019
ER  - 

APA

Hillen, A. E., Capuano, I., Gega, B., Norata, R., Mombled, M., Laface, I., Zambonini, G., Lomagno, A., Rouillon, M., Giannelli, S. G., Benedicenti, F., Gazzo, F., Arévalo, S., Spinozzi, G., Sanvito, F., Amendola, M., Broccoli, V., Montini, E., Gritti, A., & Meneghini, V. (2026). Targeting white matter astrocytes with a Gfap-disruptive Cas9 nuclease benefits a murine model of Alexander disease. Molecular Therapy. https://doi.org/10.1016/j.ymthe.2026.09.019

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